Clinical Trials

Numerous clinical trials evaluate the clinical utility, pharmacokinetics, and safety of mycophenolate mofetil from Phase 1 through Phase 4 across multiple therapeutic areas. These studies examine conditions including renal transplant complications, systemic lupus erythematosus, autoimmune hepatitis, and hematological malignancies, with statuses spanning completed, actively recruiting, withdrawn, and terminated. Sponsored by academic medical centers, university hospitals, and biopharmaceutical organizations such as Bristol-Myers Squibb, these investigations highlight the agent's broad applications in organ transplantation and autoimmune regulation.

NCT Number Recruitment Conditions Sponsor/Collaborators Start Date Phases
NCT06412497 RECRUITING
Severe Aplastic Anemia; Acquired Amegakaryocytic Thrombocytopenia; Acquired Pure Red Cell Aplasia; Paroxysmal Nocturnal Hemoglobinuria
Masonic Cancer Center, University of Minnesota
2024-06-05 PHASE2
NCT07524530 NOT_YET_RECRUITING
Core Binding Factor Alpha Subunits; Hematologic Neoplasms; Leukemia; Lymphoma
National Cancer Institute (NCI)
2026-09-09 PHASE2
NCT04877288 RECRUITING
Renal Allograft Recipients
Bristol-Myers Squibb
2021-07-21 PHASE3
NCT06013423 RECRUITING
Acute Leukemia of Ambiguous Lineage; Acute Lymphoblastic Leukemia; Acute Myeloid Leukemia; Blastic Plasmacytoid Dendritic Cell Neoplasm; Hematopoietic and Lymphatic System Neoplasm; Mixed Phenotype Acute Leukemia; Myelodysplastic Syndrome; Myeloproliferative Neoplasm; Non-Hodgkin Lymphoma; Chronic Myeloid Leukemia, BCR-ABL1 Positive
Fred Hutchinson Cancer Center
2024-07-23 PHASE2
NCT05027945 RECRUITING
Immunodeficiency; Hematopoietic Stem Cell Transplantation
National Cancer Institute (NCI)
2023-02-23 PHASE2
NCT06568549 RECRUITING
Kidney Transplantation; Mycophenolate Mofetil
Mayo Clinic
2025-06-13 PHASE4
NCT06942156 NOT_YET_RECRUITING
Heart Transplant
Chong Kun Dang Pharmaceutical
2025-08-14 PHASE4
NCT07162038 RECRUITING
Hematologic Malignancies; Hematologic Neoplasms
National Cancer Institute (NCI)
2025-11-14 PHASE1
NCT06872333 RECRUITING
Graft Failure; Sickle Cell Disease; Hemoglobinopathies
Masonic Cancer Center, University of Minnesota
2024-11-19 PHASE2
NCT07493538 RECRUITING
AML; MDS; Acute Leukemia; Acute Myeloid Leukemia; Myelodysplastic Syndromes
Masonic Cancer Center, University of Minnesota
2026-04-10 PHASE2
NCT07605364 NOT_YET_RECRUITING
Advanced Glioblastoma
Alliance for Clinical Trials in Oncology
2026-06-10 PHASE2; PHASE3
NCT07412470 RECRUITING
Kidney Transplant Rejection
Sanofi
2026-03-13 PHASE2; PHASE3
NCT03121001 RECRUITING
Sickle Cell Disease
University of Illinois at Chicago
2017-03-20 PHASE2
NCT07767188 NOT_YET_RECRUITING
Lupus Nephritis
Zhao Minghui
2026-09-10 PHASE3
NCT05236036 ACTIVE_NOT_RECRUITING
Astrocytoma; Glioblastoma; Glioblastoma, IDH-Wildtype; MGMT-Unmethylated Glioblastoma; Recurrent Glioblastoma
Northwestern University
2022-08-08 PHASE1
NCT07359859 RECRUITING
Hematologic Malignancies
Memorial Sloan Kettering Cancer Center
2026-01-20 PHASE2
NCT07675291 NOT_YET_RECRUITING
Lupus Nephritis
Nanfang Hospital, Southern Medical University
2026-06
NCT02954939 RECRUITING
Lupus Nephritis
The University of Hong Kong
2017-03-01
NCT06549231 RECRUITING
Interstitial Lung Disease With Systemic Sclerosis
University Hospital, Tours
2025-01-08 PHASE3
NCT05327023 RECRUITING
Hematologic Neoplasms
National Cancer Institute (NCI)
2022-05-23 PHASE1; PHASE2
NCT06055608 RECRUITING
Kidney Transplant
National Institute of Allergy and Infectious Diseases (NIAID)
2024-05-22 PHASE2
NCT05088356 ACTIVE_NOT_RECRUITING
Allogeneic Hematopoietic Cell Transplantation (HCT); Advanced Hematologic Malignancies; Acute Leukemia; Chronic Myelogenous Leukemia; Myelodysplastic Syndromes; Myeloproliferative Disorders
Stanford University
2021-09-07 PHASE1
NCT07663422 NOT_YET_RECRUITING
Immune-mediated Hepatitis; Immune-related Adverse Event
Fox Chase Cancer Center
2026-06-30 PHASE2
NCT06973668 RECRUITING
AML
M.D. Anderson Cancer Center
2025-07-22 PHASE2
NCT03670966 RECRUITING
Acute Lymphoblastic Leukemia in Remission; Acute Myeloid Leukemia Arising From Previous Myelodysplastic Syndrome; Acute Myeloid Leukemia in Remission; Chronic Myelomonocytic Leukemia; Myelodysplastic Syndrome With Excess Blasts; Recurrent Acute Lymphoblastic Leukemia; Recurrent Acute Myeloid Leukemia; Refractory Acute Lymphoblastic Leukemia; Refractory Acute Myeloid Leukemia; Recurrent Mixed Phenotype Acute Leukemia; Refractory Mixed Phenotype Acute Leukemia; Hematopoietic and Lymphoid Cell Neoplasm
Fred Hutchinson Cancer Center
2019-07-10 PHASE1; PHASE2
NCT01861106 RECRUITING
GATA2; Immunodeficiency; MDS
National Cancer Institute (NCI)
2013-07-24 PHASE2
NCT07548983 RECRUITING
Acute Myeloid Leukemia
OHSU Knight Cancer Institute
2026-04-21 PHASE1
NCT04232085 RECRUITING
Primary Immune Deficiency Disorder; Immune Deficiency Disease; Bone Marrow Failure; Short Telomere Length; Fanconi Anemia; Non Fanconi DNA-DSB Repair Disorder; Hoyeraal-Hreidarsson Syndrome; Dyskeratosis Congenita; Telomere Biology Disorder; Short Telomere Syndrome
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
2020-02-12 PHASE2
NCT06680661 RECRUITING
Acute Myelogenous Leukemia; Acute Lymphatic Leukemia; Chronic Myelogenous Leukemia; Myelodysplastic Syndromes; Myelodysplastic Syndrome Other; Chronic Myelomonocytic Leukemia; Lymphoma; Hodgkin Lymphoma
Leland Metheny
2025-02-25 PHASE2
NCT05805605 RECRUITING
Acute Myelogenous Leukemia; Acute Lymphocytic Leukemia; Biphenotypic Acute Leukemia; Undifferentiated Leukemia; Prolymphocytic Leukemia; Chronic Myelogenous Leukemia; Plasma Cell Leukemia; Myelodysplastic Syndromes; Leukemia, Myeloid; Myelodysplastic Syndrome With Excess Blasts-1; Burkitt Lymphoma; Relapsed T-Cell Lymphoma; Relapsed Chronic Lymphocytic Leukemia; Small Lymphocytic Lymphoma; Marginal Zone Lymphoma; Follicular Lymphoma; Myeloproliferative Neoplasm; Myelofibrosis
Masonic Cancer Center, University of Minnesota
2023-05-01 PHASE2
NCT07796620 NOT_YET_RECRUITING
Acute Leukemia; Myelodysplastic Syndromes; Severe Aplastic Anemia (SAA)
Peking University People's Hospital
2026-10-01 PHASE1; PHASE2
NCT04888741 RECRUITING
Acute Myeloid Leukemia; Acute Lymphoblastic Leukemia; Chronic Myelomonocytic Leukemia; Myelodysplastic Syndromes; Non Hodgkin Lymphoma; Hodgkin Lymphoma; Multiple Myeloma; Chronic Myelogenous Leukemia; Myelofibrosis
University of Birmingham
2021-02-22 PHASE2
NCT04022239 RECRUITING
Hematopoietic and Lymphoid System Neoplasm
M.D. Anderson Cancer Center
2020-03-13 PHASE1; PHASE2
NCT04469842 RECRUITING
Lung Transplant; Complications
Vanderbilt University Medical Center
2023-12-01 EARLY_PHASE1
NCT05436418 RECRUITING
Peripheral Blood Stem Cell Transplantation; Hematopoietic Stem Cell Transplantation
National Cancer Institute (NCI)
2022-11-18 PHASE1; PHASE2
NCT06258915 NOT_YET_RECRUITING
Non Infectious Uveitis
Assistance Publique - Hôpitaux de Paris
2024-03-01 PHASE3
NCT07785128 NOT_YET_RECRUITING
IgA Nephropathy
Shaheed Suhrawardy Medical College and Hospital
2026-09-01 PHASE2
NCT04370301 RECRUITING
Primary Myelofibrosis; Secondary Myelofibrosis
Fred Hutchinson Cancer Center
2021-02-09 PHASE2
NCT04959175 RECRUITING
Hematologic Neoplasms
National Cancer Institute (NCI)
2021-09-23 PHASE1; PHASE2
NCT04375631 RECRUITING
Recurrent Acute Myeloid Leukemia; Recurrent Chronic Myelomonocytic Leukemia; Recurrent Myelodysplastic Syndrome; Refractory Acute Myeloid Leukemia; Refractory Chronic Myelomonocytic Leukemia; Refractory Mixed Phenotype Acute Leukemia; Refractory Myelodysplastic Syndrome; Refractory Acute Leukemia of Ambiguous Lineage; Refractory Acute Undifferentiated Leukemia
Fred Hutchinson Cancer Center
2020-12-03 PHASE1
NCT05736419 RECRUITING
Sickle Cell Disease; Thalassemia, Beta; Thalassemia
Memorial Sloan Kettering Cancer Center
2023-02-09 PHASE2
NCT05951517 RECRUITING
Henoch-Schönlein Purpura; Gastrointestinal Injury; Mycophenolate Mofetil
Sun Yat-Sen Memorial Hospital of Sun Yat-Sen University
2023-01-01
NCT06001385 ACTIVE_NOT_RECRUITING
Acute Lymphoblastic Leukemia; Acute Myeloid Leukemia; Acute Leukemia; Myelodysplastic Syndromes; Chronic Myeloid Leukemia; Chronic Lymphocytic Leukemia; Myeloproliferative Neoplasm; Lymphoma; Chronic Myelomonocytic Leukemia; Pro-Lymphocytic Leukemia; Myelofibrosis
Center for International Blood and Marrow Transplant Research
2023-12-08 PHASE2
NCT04644016 RECRUITING
AML; ALL; MDS; MPD Withou Myelofibrosis; NHL or HL; Inherited Metabolic Disorders; Hemoglobinopathies; Bone Marrow Failure; HLH
Memorial Sloan Kettering Cancer Center
2020-11-20 PHASE2
NCT01659606 ACTIVE_NOT_RECRUITING
Dyskeratosis Congenita; Hoyeraal Hreidarsson Syndrome; Revesz Syndrome; Aplastic Anemia
Boston Children's Hospital
2012-07 PHASE2
NCT05626387 ACTIVE_NOT_RECRUITING
Hypersensitivity Pneumonitis
Post Graduate Institute of Medical Education and Research, Chandigarh
2022-11-23 PHASE4
NCT04477629 RECRUITING
Heart Transplantation
NYU Langone Health
2020-08-06 PHASE2
NCT04904588 ACTIVE_NOT_RECRUITING
Acute Lymphoblastic Leukemia; Acute Myelogenous Leukemia; Mixed Phenotype Acute Leukemia; Acute Leukemia; Myelodysplastic Syndromes; Chronic Myelogenous Leukemia; Chronic Lymphocytic Leukemia; Lymphoma
Center for International Blood and Marrow Transplant Research
2021-09-30 PHASE2
NCT05843968 UNKNOWN
Nephrotic Syndrome in Children
Children's Hospital of Chongqing Medical University
2023-01-29 PHASE2
NCT05622318 ACTIVE_NOT_RECRUITING
Graft-versus-host Disease
Medical College of Wisconsin
2023-08-29 PHASE2
NCT05193565 ACTIVE_NOT_RECRUITING
Kidney Transplantation
Chong Kun Dang Pharmaceutical
2021-11-19 PHASE4
NCT04384692 ACTIVE_NOT_RECRUITING
Primary Myelofibrosis; Secondary Myelofibrosis
Fred Hutchinson Cancer Center
2020-12-18 PHASE2
NCT04547049 ACTIVE_NOT_RECRUITING
Leukemia; MDS
First Affiliated Hospital of Zhejiang University
2020-09-01 PHASE3
NCT03292861 ENROLLING_BY_INVITATION
Heart Transplantation
Cedars-Sinai Medical Center
2018-09-13 PHASE2
NCT06789315 NOT_YET_RECRUITING
Alcoholic Hepatitis
Institute of Liver and Biliary Sciences, India
2025-01-20
NCT05807932 RECRUITING
Myelodysplastic Syndromes; Secondary Acute Myeloid Leukemia; Chronic Myelomonocytic Leukemia
Heinrich-Heine University, Duesseldorf
2023-06-26 PHASE1; PHASE2
NCT06752694 ACTIVE_NOT_RECRUITING
Aplastic Anemia
Fred Hutchinson Cancer Center
2025-09-25 PHASE2
NCT06650124 NOT_YET_RECRUITING
Autoimmune Hepatitis
Institute of Liver and Biliary Sciences, India
2024-11-01 PHASE2; PHASE3
NCT04207177 UNKNOWN
Kidney Transplant; Complications; Immune Suppression
Oslo University Hospital
2019-10-30 PHASE4
NCT06044493 COMPLETED
Kidney Transplant
Chong Kun Dang Pharmaceutical
2023-11-14 PHASE4
NCT05907746 ACTIVE_NOT_RECRUITING
GATA2; Immunodeficiency
National Cancer Institute (NCI)
2023-11-29 PHASE2
NCT05916781 UNKNOWN
Systemic Lupus Erythematosus; Lupus Nephritis
Chinese SLE Treatment And Research Group
2023-07-01 PHASE4
NCT02416388 RECRUITING
Acute Myeloid Leukemia (AML)
University Hospital, Angers
2015-01 PHASE2; PHASE3
NCT04868786 UNKNOWN
Hematopoietic Stem Cell Transplantation
Seoul National University Hospital
2020-10-26 PHASE1
NCT03797196 ACTIVE_NOT_RECRUITING
Renal Transplant Recipients; Elderly Patients; Immunosuppression
University Medical Center Groningen
2019-07-29 PHASE4
NCT05495893 UNKNOWN
Mycophenolate Mofetil; Cyclophosphamide; Lupus Nephritis
Second Xiangya Hospital of Central South University
2022-07-25 PHASE4
NCT05115630 COMPLETED
Myeloid Malignancies; Acute Myeloid Leukemia; Myelodysplastic Syndrome; Chronic Myeloid Leukemia
M.D. Anderson Cancer Center
2022-04-08 PHASE2
NCT03246906 TERMINATED
Acute Lymphoblastic Leukemia; Acute Myeloid Leukemia; Aggressive Non-Hodgkin Lymphoma; Chronic Lymphocytic Leukemia; Diffuse Large B-Cell Lymphoma; Mantle Cell Lymphoma; Myelodysplastic Syndrome; Myelodysplastic/Myeloproliferative Neoplasm; Prolymphocytic Leukemia; Recurrent Chronic Lymphocytic Leukemia; Recurrent Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Recurrent Hodgkin Lymphoma; Recurrent Plasma Cell Myeloma; Recurrent Small Lymphocytic Lymphoma; Recurrent Waldenstrom Macroglobulinemia; Hematologic and Lymphocytic Disorder; Blastic Plasmacytoid Dendritic Cell Neoplasm
Fred Hutchinson Cancer Center
2017-09-11 PHASE2
NCT03434730 COMPLETED
Acute Myeloid Leukemia; Acute Lymphoblastic Leukemia; Acute Leukemia; Myelodysplastic Syndromes; Myelodysplastic-Myeloproliferative Diseases; Myeloproliferative Disorder; Non Hodgkin Lymphoma; Hodgkin Lymphoma; Leukemia
Memorial Sloan Kettering Cancer Center
2018-02-07 PHASE2
NCT05570409 TERMINATED
Inflammatory Cardiomyopathy
LMU Klinikum
2023-03-28 PHASE2; PHASE3
NCT05113004 RECRUITING
Primary Sjögren's Syndrome (pSS)
Assistance Publique - Hôpitaux de Paris
2022-01-20 PHASE2
NCT02220985 COMPLETED
Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Acute Biphenotypic Leukemia; Acute Leukemia of Ambiguous Lineage; Acute Undifferentiated Leukemia; Allogeneic Hematopoietic Stem Cell Transplant Recipient; Blast Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Blastic Plasmacytoid Dendritic Cell Neoplasm; Childhood Acute Lymphoblastic Leukemia in Remission; Childhood Acute Myeloid Leukemia in Remission; Donor; Lymphoblastic Lymphoma; Myelodysplastic Syndrome With Excess Blasts; Myelodysplastic Syndrome With Excess Blasts-1; Myelodysplastic Syndrome With Excess Blasts-2; Recurrent Acute Lymphoblastic Leukemia; Recurrent Acute Myeloid Leukemia; Recurrent Childhood Acute Lymphoblastic Leukemia; Recurrent Childhood Acute Myeloid Leukemia; Recurrent Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Refractory Acute Lymphoblastic Leukemia; Refractory Acute Myeloid Leukemia; Acute Lymphoblastic Leukemia in Remission; Acute Myeloid Leukemia in Remission
Fred Hutchinson Cancer Center
2015-03-23 PHASE2
NCT03712878 COMPLETED
Hematopoietic and Lymphoid Cell Neoplasm
Sidney Kimmel Comprehensive Cancer Center at Thomas Jefferson University
2018-09-19 PHASE2
NCT04477200 ACTIVE_NOT_RECRUITING
Recurrent Glioblastoma; Recurrent Gliosarcoma; Recurrent Astrocytoma, Grade IV; Newly Diagnosed Glioblastoma; Newly Diagnosed Gliosarcoma; Newly Diagnosed Astrocytoma, Grade IV
University of Michigan Rogel Cancer Center
2020-08-05 PHASE1
NCT06365437 TERMINATED
Kidney Transplantation
ITB-Med LLC
2021-06-06 PHASE2
NCT04838704 COMPLETED
Graft Versus Host Disease
Zhejiang University
2021-04-01
NCT01428973 UNKNOWN
Graft-Versus-Host Disease; Hematological Malignancies
University of Liege
2011-09 PHASE2
NCT05049863 TERMINATED
Small-cell Lung Cancer; Small Cell Lung Carcinoma
Washington University School of Medicine
2023-02-27 PHASE1
NCT05256537 ACTIVE_NOT_RECRUITING
Hematologic Neoplasms
Ronald Paquette
2022-04-26 PHASE2
NCT04530487 TERMINATED
Desmoplastic Small Round Cell Tumor; Ewing Sarcoma/Peripheral Primitive Neuroectodermal Tumor; Recurrent Desmoplastic Small Round Cell Tumor; Recurrent Malignant Peripheral Nerve Sheath Tumor; Recurrent Malignant Solid Neoplasm; Recurrent Neuroblastoma; Recurrent Rhabdomyosarcoma; Refractory Desmoplastic Small Round Cell Tumor; Refractory Malignant Peripheral Nerve Sheath Tumor; Refractory Malignant Solid Neoplasm; Refractory Neuroblastoma; Refractory Rhabdomyosarcoma
M.D. Anderson Cancer Center
2020-08-19 PHASE2
NCT03216967 COMPLETED
BK Virus Nephropathy After Kidney Transplantation
University Hospital, Strasbourg, France
2018-01-15 PHASE4
NCT05666336 UNKNOWN
Systemic Lupus Erythematosus
Fen Li
2022-12-31 PHASE4
NCT05306873 TERMINATED
Systemic Lupus Erythematosus
National Institute of Allergy and Infectious Diseases (NIAID)
2022-11-30 PHASE2
NCT01701986 COMPLETED
Hematopoietic Cell Transplantation Recipient; Refractory B-Cell Non-Hodgkin Lymphoma; Refractory Hodgkin Lymphoma; Refractory T-Cell Non-Hodgkin Lymphoma
M.D. Anderson Cancer Center
2012-10-25 PHASE1; PHASE2
NCT00357565 COMPLETED
Leukemia; Myelodysplastic Syndromes; Childhood Acute Myeloid Leukemia in Remission; Recurrent Childhood Acute Myeloid Leukemia; Secondary Acute Myeloid Leukemia; Childhood Acute Lymphoblastic Leukemia in Remission; Previously Treated Myelodysplastic Syndrome; Secondary Myelodysplastic Syndrome; Refractory Anemia With Excess Blasts in Transformation; Refractory Anemia With Excess Blasts; Refractory Anemia; De Novo Myelodysplastic Syndrome; Childhood Myelodysplastic Syndrome
Masonic Cancer Center, University of Minnesota
2005-11 PHASE2
NCT06279494 UNKNOWN
Acute Leukemia; Myelodysplastic Syndromes; Severe Aplastic Anemia
Peking University People's Hospital
2024-03 PHASE1; PHASE2
NCT01203722 COMPLETED
Hematologic Malignancies
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
2010-09 PHASE1; PHASE2
NCT04942730 COMPLETED
Leukemia, Acute Lymphoblastic; Myeloid Leukemia, Acute; Biphenotypic Acute Leukemia; Lymphoblastic Lymphoma; Myelodysplastic Syndromes; Myeloproliferative Neoplasm
St. Petersburg State Pavlov Medical University
2021-01-21 PHASE2
NCT05702931 Not yet recruiting
Hyperglycemia|Renal Transplant Complication Primary Non-Function|Diabetes
Rigshospitalet Denmark|Aarhus University Hospital|Odense University Hospital
2024-04-01 Phase 4
NCT05170828 WITHDRAWN
Acute Leukemia; Myelodysplastic Syndromes; T-lymphoblastic Lymphoma; Acute Lymphocytic Leukemia; Acute Myeloid Leukemia; Acute Biphenotypic Leukemia; Acute Undifferentiated Leukemia
Ossium Health, Inc.
2022-09 PHASE1
NCT04773392 TERMINATED
Kidney Transplantation; Kidney Transplant Rejection
University of Southern California
2021-11-23 PHASE4
NCT06288932 COMPLETED
Immune Thrombocytopenia Purpura
National Institute of Blood and Marrow Transplant (NIBMT), Pakistan
2023-08-18 PHASE3
NCT02566304 COMPLETED
Acute Myeloid Leukemia; Acute Myeloid Leukemia in Remission; Aplastic Anemia; Chronic Myelomonocytic Leukemia; Hodgkin Lymphoma; Indolent Non-Hodgkin Lymphoma; Malignant Neoplasm; Myelodysplastic Syndrome; Myeloproliferative Neoplasm; Plasma Cell Myeloma; Refractory Anemia; Refractory Anemia With Excess Blasts; Refractory Anemia With Ring Sideroblasts; Refractory Cytopenia With Multilineage Dysplasia; Refractory Cytopenia With Multilineage Dysplasia and Ring Sideroblasts
Sidney Kimmel Comprehensive Cancer Center at Thomas Jefferson University
2015-11-13 PHASE2
NCT04927390 UNKNOWN
Systemic Sclerosis; Limited Cutaneous Systemic Sclerosis
University College, London
2021-12-08 PHASE2
NCT02880293 COMPLETED
Hematologic Malignancy
Memorial Sloan Kettering Cancer Center
2016-08-23
NCT01850108 UNKNOWN
Sickle Cell Disease; Hemoglobinopathies
Vanderbilt-Ingram Cancer Center
2013-05
NCT04311632 COMPLETED
Kidney Transplantation
ITB-Med LLC
2021-05-26 PHASE2
NCT05293509 WITHDRAWN
Stem Cell Transplantation
M.D. Anderson Cancer Center
2022-03-02 PHASE2
NCT01413100 COMPLETED
Systemic Scleroderma
Fred Hutchinson Cancer Center
2011-09-15 PHASE2
NCT04066114 COMPLETED
Living-Donor Kidney Transplant; Kidney Transplant Recipients
National Institute of Allergy and Infectious Diseases (NIAID)
2019-12-11 PHASE1; PHASE2
NCT03899103 COMPLETED
Steroid-Dependent Nephrotic Syndrome
Nilratan Sircar Medical College
2019-05-15 PHASE3
NCT03192397 ACTIVE_NOT_RECRUITING
Acute Myeloid Leukemia in Remission; Adult Acute Lymphoblastic Leukemia in Complete Remission; Chronic Myelogenous Leukemia, BCR-ABL1 Positive in Remission; Chronic Myelomonocytic Leukemia in Remission; Graft Versus Host Disease; Hodgkin Lymphoma; Minimal Residual Disease; Myelodysplastic Syndrome; Myeloproliferative Neoplasm; Non-Hodgkin Lymphoma; Plasma Cell Myeloma; Severe Aplastic Anemia; Waldenstrom Macroglobulinemia
Roswell Park Cancer Institute
2017-08-09 PHASE1; PHASE2
NCT01810588 COMPLETED
Hematologic Malignancies
Weill Medical College of Cornell University
2012-10-16 PHASE2
NCT02711826 COMPLETED
Kidney Transplant; Adult Living Donor Kidney Transplant Recipients; Renal Transplant; Living Kidney Donor
National Institute of Allergy and Infectious Diseases (NIAID)
2016-09-20 PHASE1; PHASE2
NCT04895423 UNKNOWN
Atopic Dermatitis
National Medical Research Center for Children's Health, Russian Federation
2021-11-25 PHASE4
NCT05859191 Recruiting
Systemic Lupus Erythematosus|Physiopathology
University Hospital Tours|Research Center for Respiratory Diseases Inserm U1100
2023-07-21 --
NCT02900443 UNKNOWN
Autoimmune Hepatitis
Radboud University Medical Center
2017-01 PHASE4
NCT04048161 COMPLETED
Nephrotic Syndrome in Children
The Children's Hospital of Zhejiang University School of Medicine
2019-11-12 PHASE4
NCT03386539 COMPLETED
Pediatric Heart Transplantation; Immunosuppression; Chronic Kidney Diseases; Cardiac Allograft Vasculopathy; Heart Transplant Failure and Rejection; Post-transplant Lymphoproliferative Disorder; Heart Transplant Infection
Boston Children's Hospital
2018-01-29 PHASE3
NCT01811368 UNKNOWN
Refractory Non Hodgkin Lymphoma; Relapsed Non Hodgkin Lymphoma
Joseph Tuscano
2013-03-12 PHASE2
NCT04669210 COMPLETED
Graft-versus-host-disease; Stem Cell Transplant Complications; Acute Myeloid Leukemia; Acute Lymphoid Leukemia
St. Petersburg State Pavlov Medical University
2020-11-03 PHASE2
NCT04473924 WITHDRAWN
Infection; Transplant;Failure,Kidney
University of California, San Francisco
2022-07 PHASE2
NCT05221411 UNKNOWN
Autoimmune Hepatitis
Leiden University Medical Center
2022-01-19 PHASE4
NCT05057481 UNKNOWN
Autoimmune Hemolytic Anemia; Systemic Lupus Erythematosus
Assiut University
2021-09-15 PHASE3
NCT04444843 UNKNOWN
Kidney Transplant Recipients
First Affiliated Hospital Xi'an Jiaotong University
2021-01-22 PHASE4
NCT04776850 WITHDRAWN
Beta Thalassemia Major; Sickle Beta 0 Thalassemia; Sickle Beta Plus Thalassemia; Sickle Beta Thalassemia; Sickle Cell Disease; Sickle Cell-SS Disease
M.D. Anderson Cancer Center
2020-12-29 EARLY_PHASE1
NCT02582775 COMPLETED
Epidermolysis Bullosa
Masonic Cancer Center, University of Minnesota
2016-03 PHASE2
NCT04903054 WITHDRAWN
Kidney Transplantation; Renal Transplant Recipients
National Institute of Allergy and Infectious Diseases (NIAID)
2022-01-10 PHASE2
NCT03959241 COMPLETED
Acute Leukemia; Chronic Myelogenous Leukemia (CML); Myelodysplasia; Lymphoma
Medical College of Wisconsin
2019-06-25 PHASE3
NCT05303272 UNKNOWN
Pemphigus Vulgaris
Tongji Hospital
2021-02-01 PHASE4
NCT04531865 WITHDRAWN
Frequently Relapsing Nephrotic Syndrome; Steroid-Dependent Nephrotic Syndrome
Children's Hospital of Fudan University
2021-01-01 PHASE3
NCT02342145 COMPLETED
Beta-Thalassemia Major; Graft-versus-host Disease (GVHD)
Zhongming Zhang
2015-04 PHASE4
NCT03794492 COMPLETED
Kidney Transplant
Chong Kun Dang Pharmaceutical
2018-03-31 PHASE4
NCT05284942 UNKNOWN
Rosai-Dorfman Disease; Langerhans Cell Histiocytosis
Tongji Hospital
2011-10-01 PHASE4
NCT01760655 COMPLETED
Acute Myeloid Leukemia With FLT3/ITD Mutation; Acute Myeloid Leukemia With Gene Mutations; Acute Myeloid Leukemia With Inv(3) (q21.3;q26.2); GATA2, MECOM; Acute Myeloid Leukemia With t(6;9) (p23;q34.1); DEK-NUP214; Aplastic Anemia; Chronic Lymphocytic Leukemia; Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Chronic Myelomonocytic Leukemia; Follicular Lymphoma; Hodgkin Lymphoma; Myelodysplastic Syndrome; Myelofibrosis; Myeloid Leukemia; Non-Hodgkin Lymphoma; Plasma Cell Myeloma; Polycythemia Vera; Recurrent Adult Acute Myeloid Leukemia; Recurrent Childhood Acute Myeloid Leukemia; Refractory Acute Myeloid Leukemia; Secondary Acute Myeloid Leukemia; Therapy-Related Acute Myeloid Leukemia
Sidney Kimmel Comprehensive Cancer Center at Thomas Jefferson University
2012-12-24 PHASE2
NCT03789006 UNKNOWN
Kidney Transplant Rejection
University of Khartoum
2018-03-21 PHASE4
NCT05120570 Recruiting
Acute Leukemia|Myelodysplastic Syndromes|Myeloproliferative Neoplasm|Lymphoma
Masonic Cancer Center University of Minnesota
2022-03-17 Phase 1|Phase 2
NCT01904136 COMPLETED
Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Acute Myeloid Leukemia Arising From Previous Myelodysplastic Syndrome; Acute Myeloid Leukemia With Gene Mutations; Blast Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive; de Novo Myelodysplastic Syndrome; Myelodysplastic Syndrome; Recurrent Acute Myeloid Leukemia; Recurrent Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Therapy-Related Acute Myeloid Leukemia
M.D. Anderson Cancer Center
2014-04-22 PHASE1; PHASE2
NCT03088709 TERMINATED
Acute Myeloid Leukemia; Acute Lymphocytic Leukemia; Myelodysplastic Syndrome; Non-hodgkin Lymphoma; Chronic Lymphocytic Leukemia
Loyola University
2017-01-18 PHASE2
NCT02248597 COMPLETED
Graft Versus Host Disease; Hematopoietic/Lymphoid Cancer
Wake Forest University Health Sciences
2015-02-25 PHASE2
NCT02498977 TERMINATED
Transplantation, Liver
King's College London
2015-10 PHASE4
NCT03171831 UNKNOWN
Thalassemia Major
First Affiliated Hospital of Guangxi Medical University
2017-04-01 PHASE4
NCT02867800 COMPLETED
Sickle Cell Disease; Graft Versus Host Disease
Monica Bhatia
2016-07 PHASE1
NCT00796068 COMPLETED
Acute Biphenotypic Leukemia; Acute Lymphoblastic Leukemia in Remission; Acute Myeloid Leukemia in Remission; Blasts Under 5 Percent of Bone Marrow Nucleated Cells; Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Chronic Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Myelodysplastic Syndrome (MDS)
Fred Hutchinson Cancer Center
2009-02-24 PHASE2
NCT02909335 WITHDRAWN
Liver Transplantation
Rennes University Hospital
2016-11 PHASE3
NCT01807611 COMPLETED
Leukemia; Lymphoma
St. Jude Children's Research Hospital
2013-05-16 PHASE2
NCT02918292 COMPLETED
Severe Aplastic Anemia
Medical College of Wisconsin
2017-07-03 PHASE2
NCT03828682 UNKNOWN
Kidney Transplantation; Immunosuppression
Simon Tremblay, PharmD, PhD
2019-06-21 PHASE4
NCT03492255 TERMINATED
Systemic Lupus Erythematosus (SLE)
University of Sao Paulo General Hospital
2018-04-12
NCT02833805 COMPLETED
Severe Aplastic Anemia; Aplastic Anemia; Bone Marrow Failure; Immunosuppression
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
2016-09 PHASE2
NCT00423514 COMPLETED
Graft Versus Host Disease; Leukemia; Myelodysplastic Syndromes
Memorial Sloan Kettering Cancer Center
2006-11-20 PHASE1; PHASE2
NCT03580291 UNKNOWN
Lupus Nephritis
Lingyun Sun
2018-08-01 PHASE2
NCT04205240 TERMINATED
Recurrent Plasma Cell Myeloma
Srinivas Devarakonda
2020-12-22 PHASE2
NCT02556931 COMPLETED
Myelodysplastic Syndrome; Chronic Myelomonocytic Leukemia; Small Lymphocytic Lymphoma; Chronic Lymphocytic Leukemia; Prolymphocytic Leukemia; Chronic Myeloid Leukemia; Chronic Myeloproliferative Disorders; Multiple Myeloma; Plasma Cell Neoplasm; Plasma Cell Dyscrasia; Myelofibrosis; Polycythemia Vera; Essential Thrombocythemia; Plasma Cell Leukemia
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
2015-12 PHASE2
NCT02921789 COMPLETED
Kidney Transplantation; Primary Focal Segmental Glomerulosclerosis (FSGS)
Astellas Pharma Global Development, Inc.
2017-05-22 PHASE2
NCT00352976 COMPLETED
Fanconi Anemia
Masonic Cancer Center, University of Minnesota
2006-05-18 PHASE2; PHASE3
NCT02423915 COMPLETED
Leukemia; Lymphoma
M.D. Anderson Cancer Center
2015-07-30 PHASE1
NCT02540395 COMPLETED
Disorder Related to Renal Transplantation; Effects of Immunosuppressant Therapy
Prof. Dr. Petra Reinke
2015-03
NCT04402580 TERMINATED
Nephrotic Syndrome Steroid-Dependent
Istituto Giannina Gaslini
2019-07-01 PHASE2
NCT03128359 COMPLETED
Acute Leukemia; Chronic Lymphocytic Leukemia/Small Lymphocytic Lymphoma; Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Diffuse Large B-Cell Lymphoma; Follicular Lymphoma; Graft Versus Host Disease; Hodgkin Lymphoma; Mantle Cell Lymphoma; Marginal Zone Lymphoma; Myelodysplastic Syndrome; Myeloproliferative Neoplasm; Recurrent Acute Myeloid Leukemia With Myelodysplasia-Related Changes; Recurrent Plasma Cell Myeloma; Refractory Plasma Cell Myeloma; Secondary Myelodysplastic Syndrome
City of Hope Medical Center
2017-05-30 PHASE2
NCT02532777 UNKNOWN
Henoch-Schoenlein Purpura Nephritis
Nanjing Children's Hospital
2015-08 PHASE2
NCT04258423 TERMINATED
Kidney Failure
Indiana University
2019-12-19 PHASE3
NCT03674411 ACTIVE_NOT_RECRUITING
Acute Myeloid Leukemia; Acute Lymphocytic Leukemia; Biphenotypic/Undifferentiated Leukemia; Chronic Myelogenous Leukemia; Myelodysplasia; Relapsed Large Cell Lymphoma; Mantle Cell Lymphoma; Hodgkin Lymphoma; Burkitt Lymphoma; Relapsed T-Cell Lymphoma; Lymphoplasmacytic Lymphoma
Masonic Cancer Center, University of Minnesota
2019-01-02 PHASE2
NCT02904772 WITHDRAWN
LPL Deficiency
UniQure Biopharma B.V.
2016-10 PHASE2
NCT03112603 COMPLETED
Graft-versus-host Disease (GVHD)
Incyte Corporation
2017-06-29 PHASE3
NCT02756572 COMPLETED
Blasts 10 Percent or More of Bone Marrow Nucleated Cells; Chronic Myelomonocytic Leukemia-2; High Grade Malignant Neoplasm; Myelodysplastic Syndrome; Myelodysplastic Syndrome With Excess Blasts-2; Myeloid Neoplasm; Previously Treated Myelodysplastic Syndrome; Recurrent Acute Myeloid Leukemia; Refractory Acute Myeloid Leukemia
University of Washington
2016-09-22 PHASE2
NCT04147390 UNKNOWN
Keratopathy
Shahid Beheshti University of Medical Sciences
2019-11 PHASE2; PHASE3
NCT02793544 COMPLETED
Myelodysplastic Syndrome (MDS); Chronic Lymphocytic Leukemia (CLL); Chemotherapy-sensitive Lymphoma; Acute Lymphoblastic Leukemia (ALL)/T Lymphoblastic Lymphoma; Acute Myelogenous Leukemia (AML); Acute Biphenotypic Leukemia (ABL); Acute Undifferentiated Leukemia (AUL)
Center for International Blood and Marrow Transplant Research
2016-12 PHASE2
NCT01685411 TERMINATED
Acute Lymphoblastic Leukemia; Acute Myeloid Leukemia; Myelodysplastic Syndrome
Masonic Cancer Center, University of Minnesota
2013-01
NCT02487069 COMPLETED
Acute Leukemia; Chronic Myeloid Leukemia; Myelodysplastic Syndrome
Nanfang Hospital, Southern Medical University
2015-06
NCT03920059 TERMINATED
Lupus Nephritis
Chulalongkorn University
2019-08-20 PHASE4
NCT02677181 COMPLETED
aGVHD
Chinese PLA General Hospital
2016-01 PHASE4
NCT03734601 COMPLETED
Acute Myeloid Leukemia; Myelodysplastic Syndromes; Myeloproliferative Disorder; Chronic Lymphocytic Leukemia; B-cell Lymphoma; T-cell Lymphoma; Non Hodgkin Lymphoma; Hodgkin Lymphoma; Chronic Myelomonocytic Leukemia
Stanford University
2018-11-05 PHASE2
NCT02181478 COMPLETED
Acute Lymphoblastic Leukemia; Acute Myelogenous Leukemia; Myelodysplastic Syndromes; Myelofibrosis; Relapsed Non-Hodgkin Lymphoma; Refractory Non-Hodgkin Lymphoma; Hodgkin Lymphoma; Refractory Hodgkin Lymphoma; Relapsed Chronic Lymphocytic Leukemia; Refractory Chronic Lymphocytic Leukemia; Lymphoid Malignancies; Chronic Myelogenous Leukemia
Case Comprehensive Cancer Center
2015-07-22 EARLY_PHASE1
NCT01921218 COMPLETED
Failing Renal Allograft
Andrew B Adams
2013-08 PHASE3
NCT03099122 COMPLETED
End-stage Renal Disease
Sanofi
2017-08-16 PHASE4
NCT02432339 UNKNOWN
Psychological Stress; Hypertension, Renal
Augusta University
2014-04-22 PHASE1; PHASE2
NCT00309842 COMPLETED
Acute Myeloid Leukemia; Acute Lymphocytic Leukemia; Chronic Myelogenous Leukemia; Myelofibrosis; MDS; Refractory Anemia; Chronic Lymphocytic Leukemia; Prolymphocytic Leukemia; Non-Hodgkin's Lymphoma; Leukemia; Lymphoma; Multiple Myeloma; Myelodysplastic Syndromes
Masonic Cancer Center, University of Minnesota
2005-07-28 PHASE2
NCT02990286 COMPLETED
Lung Disease, Interstitial
University Hospital, Tours
2017-01-20 PHASE3
NCT01946880 TERMINATED
Systemic Lupus Erythematosus; SLE
National Institute of Allergy and Infectious Diseases (NIAID)
2013-11-20 PHASE2
NCT02839941 UNKNOWN
Kidney Transplantation
The First Affiliated Hospital with Nanjing Medical University
2016-08
NCT02188719 TERMINATED
Liver Transplantation
National Institute of Allergy and Infectious Diseases (NIAID)
2014-12-17 PHASE1
NCT00303719 TERMINATED
Kidney Cancer; Leukemia; Lymphoma; Multiple Myeloma; Plasma Cell Neoplasm; Myelodysplastic Syndromes
Masonic Cancer Center, University of Minnesota
2002-03-26 PHASE2
NCT02627573 TERMINATED
Leukemia, Chronic Myeloid; Myelodysplastic Syndromes; Leukemia, Myeloid, Chronic, Atypical, BCR-ABL Negative
St. Petersburg State Pavlov Medical University
2015-07 PHASE2
NCT02435901 COMPLETED
Sickle Cell Disease; Beta Thalassemia-Major
Northwell Health
2008-12 PHASE1; PHASE2
NCT01570348 TERMINATED
Crohn Disease
Fred Hutchinson Cancer Center
2012-07-17 PHASE2
NCT01252667 COMPLETED
Acute Myeloid Leukemia
Fred Hutchinson Cancer Center
2011-01-25 PHASE2
NCT02550652 COMPLETED
Lupus Nephritis
Hoffmann-La Roche
2015-11-13 PHASE2
NCT02077556 COMPLETED
Drug Interaction Potentiation
National Taiwan University Hospital
2014-04 PHASE4
NCT02954198 COMPLETED
Immunosuppression
Medical University of South Carolina
2016-12-01
NCT02383589 COMPLETED
Pemphigus Vulgaris
Hoffmann-La Roche
2015-05-26 PHASE3
NCT01251575 COMPLETED
Adult Acute Lymphoblastic Leukemia; Adult Acute Myeloid Leukemia; Adult Diffuse Large B-Cell Lymphoma; Adult Myelodysplastic Syndrome; Adult Non-Hodgkin Lymphoma; Aggressive Non-Hodgkin Lymphoma; Childhood Acute Lymphoblastic Leukemia; Childhood Acute Myeloid Leukemia; Childhood Diffuse Large B-Cell Lymphoma; Childhood Myelodysplastic Syndrome; Childhood Non-Hodgkin Lymphoma; Chronic Lymphocytic Leukemia; Chronic Lymphocytic Leukemia in Remission; Chronic Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Hematopoietic and Lymphoid Cell Neoplasm; Mantle Cell Lymphoma; Plasma Cell Myeloma; Prolymphocytic Leukemia; Recurrent Chronic Lymphocytic Leukemia; Refractory Chronic Lymphocytic Leukemia; T-Cell Prolymphocytic Leukemia; Waldenstrom Macroglobulinemia; Recurrent Diffuse Large B-Cell Lymphoma; Recurrent Hodgkin Lymphoma
Fred Hutchinson Cancer Center
2010-12-01 PHASE2
NCT03660436 COMPLETED
Healthy Participants
Bristol-Myers Squibb
2018-08-14 PHASE1
NCT01527045 COMPLETED
Aggressive Non-Hodgkin Lymphoma; Blasts Under 5 Percent of Bone Marrow Nucleated Cells; Chronic Lymphocytic Leukemia; Loss of Chromosome 17p; Myelodysplastic/Myeloproliferative Neoplasm; Non-Hodgkin Lymphoma; Prolymphocytic Leukemia; Recurrent Adult Acute Lymphoblastic Leukemia; Recurrent Adult Acute Myeloid Leukemia; Recurrent Aggressive Adult Non-Hodgkin Lymphoma; Recurrent Childhood Acute Lymphoblastic Leukemia; Recurrent Childhood Acute Myeloid Leukemia; Recurrent Chronic Lymphocytic Leukemia; Recurrent Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Recurrent Diffuse Large B-Cell Lymphoma; Recurrent Hodgkin Lymphoma; Recurrent Mantle Cell Lymphoma; Recurrent Non-Hodgkin Lymphoma; Recurrent Plasma Cell Myeloma; Recurrent Small Lymphocytic Lymphoma; Waldenstrom Macroglobulinemia
Fred Hutchinson Cancer Center
2012-09-25 PHASE2
NCT02953873 COMPLETED
Immunosuppression
Medical University of South Carolina
2017-05-05 PHASE4
NCT02652468 COMPLETED
Lymphoma
University of Wisconsin, Madison
2016-03-10
NCT00358657 TERMINATED
Immunodeficiency Syndrome; Severe Aplastic Anemia; Genetic Disorder
Fred Hutchinson Cancer Center
2006-05-24 PHASE2
NCT00723099 COMPLETED
Acute Lymphoblastic Leukemia; Acute Myeloid Leukemia; Aggressive Non-Hodgkin Lymphoma; Chronic Myelogenous Leukemia; Chronic Phase Chronic Myelogenous Leukemia; Indolent Non-Hodgkin Lymphoma; Lymphoma; Mixed Phenotype Acute Leukemia; Myelodysplastic Syndrome; Myeloproliferative Neoplasm; Recurrent Chronic Lymphocytic Leukemia; Recurrent Follicular Lymphoma; Recurrent Lymphoplasmacytic Lymphoma; Recurrent Mantle Cell Lymphoma; Recurrent Marginal Zone Lymphoma; Recurrent Plasma Cell Myeloma; Recurrent Small Lymphocytic Lymphoma; Recurrent T-Cell Non-Hodgkin Lymphoma; Refractory Chronic Lymphocytic Leukemia; Refractory Chronic Myelogenous Leukemia; Refractory Follicular Lymphoma; Refractory Hodgkin Lymphoma; Refractory Lymphoplasmacytic Lymphoma; Refractory Mantle Cell Lymphoma; Refractory Small Lymphocytic Lymphoma; T-Cell Non-Hodgkin Lymphoma
Fred Hutchinson Cancer Center
2008-06-25 PHASE2
NCT01008462 COMPLETED
B-Cell Prolymphocytic Leukemia; Hypodiploidy; Loss of Chromosome 17p; Plasma Cell Leukemia; Progression of Multiple Myeloma or Plasma Cell Leukemia; Recurrent Adult Hodgkin Lymphoma; Recurrent Adult Non-Hodgkin Lymphoma; Recurrent Childhood Hodgkin Lymphoma; Recurrent Childhood Non-Hodgkin Lymphoma; Recurrent Chronic Lymphocytic Leukemia; Recurrent Plasma Cell Myeloma; Recurrent Small Lymphocytic Lymphoma; Refractory Childhood Hodgkin Lymphoma; Refractory Chronic Lymphocytic Leukemia; Refractory Non-Hodgkin Lymphoma; Refractory Plasma Cell Myeloma; Refractory Small Lymphocytic Lymphoma; t(14;16); t(4;14); T-Cell Prolymphocytic Leukemia; Waldenstrom Macroglobulinemia
Fred Hutchinson Cancer Center
2010-03-18 PHASE2
NCT02120157 COMPLETED
Myeloablative Conditioning; HLA-mismatched Bone Marrow Transplantation; Graft Survival; Transplantation, Bone Marrow
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
2015-07-02 PHASE2
NCT00104858 COMPLETED
Chronic Lymphocytic Leukemia; Prolymphocytic Leukemia; Recurrent Small Lymphocytic Lymphoma; Refractory Chronic Lymphocytic Leukemia; Stage III Chronic Lymphocytic Leukemia; Stage III Small Lymphocytic Lymphoma; Stage IV Chronic Lymphocytic Leukemia; Stage IV Small Lymphocytic Lymphoma; T-Cell Large Granular Lymphocyte Leukemia
Fred Hutchinson Cancer Center
2004-12 PHASE2
NCT01824693 COMPLETED
Juvenile Myelomonocytic Leukemia
Children's Oncology Group
2013-06-24 PHASE2
NCT02809079 UNKNOWN
Neuromyelitis Optica Spectrum Disorders; Mycophenolate Mofetil; Efficacy and Safety
Third Affiliated Hospital, Sun Yat-Sen University
2016-01 PHASE4
NCT02217410 COMPLETED
Kidney Transplantation
Novartis Pharmaceuticals
2015-02-05 PHASE1; PHASE2
NCT01878786 TERMINATED
Delayed Graft Function
Matthew Cooper
2013-06 PHASE2; PHASE3
NCT01300572 COMPLETED
Chronic Myelomonocytic Leukemia; Previously Treated Myelodysplastic Syndrome; Recurrent Adult Acute Lymphoblastic Leukemia; Recurrent Adult Acute Myeloid Leukemia; Refractory Anemia With Excess Blasts; Secondary Acute Myeloid Leukemia
Fred Hutchinson Cancer Center
2012-01 PHASE1
NCT02208037 COMPLETED
Acute Leukemia; Chronic Myelogenous Leukemia; Myelodysplasia; Chronic Lymphocytic Leukemia; Small Lymphocytic Lymphoma; Lymphoma, B-Cell; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Hodgkin's Lymphoma
National Heart, Lung, and Blood Institute (NHLBI)
2014-08 PHASE2
NCT02864706 COMPLETED
Heart Transplantation
Novartis Pharmaceuticals
2016-01-18 PHASE4
NCT01047072 WITHDRAWN
Systemic Scleroderma
Fred Hutchinson Cancer Research Center/University of Washington Cancer Consortium
PHASE2
NCT00397813 COMPLETED
Atypical Chronic Myeloid Leukemia, BCR-ABL1 Negative; Chronic Myelomonocytic Leukemia; de Novo Myelodysplastic Syndrome; Essential Thrombocythemia; Myeloproliferative Neoplasm; Paroxysmal Nocturnal Hemoglobinuria; Polycythemia Vera; Polycythemia Vera, Post-Polycythemic Myelofibrosis Phase; Primary Myelofibrosis; Refractory Anemia; Refractory Anemia With Excess Blasts; Refractory Anemia With Ring Sideroblasts; Refractory Cytopenia With Multilineage Dysplasia; Refractory Cytopenia With Multilineage Dysplasia and Ring Sideroblasts
Fred Hutchinson Cancer Center
2006-01 PHASE2
NCT02653196 TERMINATED
Neuroepithelial Tumor; Solid Tumor; Allogeneic Hematopoietic Stem Cell Transplantation
Montefiore Medical Center
2015-09 EARLY_PHASE1
NCT01707004 COMPLETED
Acute Myeloid Leukemia With Multilineage Dysplasia Following Myelodysplastic Syndrome; Adult Acute Myeloid Leukemia in Remission; Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities; Adult Acute Myeloid Leukemia With Del(5q); Adult Acute Myeloid Leukemia With Inv(16)(p13;q22); Adult Acute Myeloid Leukemia With t(15;17)(q22;q12); Adult Acute Myeloid Leukemia With t(16;16)(p13;q22); Adult Acute Myeloid Leukemia With t(8;21)(q22;q22); de Novo Myelodysplastic Syndromes; Previously Treated Myelodysplastic Syndromes; Recurrent Adult Acute Myeloid Leukemia; Secondary Acute Myeloid Leukemia
University of Wisconsin, Madison
2013-05-16 PHASE2
NCT02896205 COMPLETED
Systemic Sclerosis; Scleroderma; Interstitial Lung Disease
Post Graduate Institute of Medical Education and Research, Chandigarh
2016-10 PHASE3
NCT03108274 COMPLETED
Healthy
Alexion Pharmaceuticals, Inc.
2017-04-18 PHASE1
NCT02458196 UNKNOWN
Autoimmune Disease
Peking Union Medical College Hospital
2015-04 PHASE2
NCT02199041 TERMINATED
Hematological Malignancies
St. Jude Children's Research Hospital
2014-07-11 PHASE2
NCT01471067 COMPLETED
Blood And Marrow Transplantation; Leukemia; Lymphoma; Transplantation Infection; Transplantation, Bone Marrow
M.D. Anderson Cancer Center
2012-07-13 PHASE1
NCT01982682 COMPLETED
Hematopoietic/Lymphoid Cancer
Sidney Kimmel Comprehensive Cancer Center at Thomas Jefferson University
2013-11-04 PHASE2
NCT01580865 COMPLETED
Lupus Nephritis
Ramathibodi Hospital
2012-05
NCT02083991 COMPLETED
Diabetes Mellitus
Vastra Gotaland Region
2013-01 PHASE4
NCT01652014 WITHDRAWN
Accelerated Phase Chronic Myelogenous Leukemia; Acute Myeloid Leukemia With Multilineage Dysplasia Following Myelodysplastic Syndrome; Adult Acute Lymphoblastic Leukemia in Remission; Adult Acute Myeloid Leukemia in Remission; Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities; Adult Acute Myeloid Leukemia With Inv(16)(p13;q22); Adult Acute Myeloid Leukemia With t(15;17)(q22;q12); Adult Acute Myeloid Leukemia With t(16;16)(p13;q22); Adult Acute Myeloid Leukemia With t(8;21)(q22;q22); Adult Nasal Type Extranodal NK/T-cell Lymphoma; Anaplastic Large Cell Lymphoma; Angioimmunoblastic T-cell Lymphoma; Blastic Phase Chronic Myelogenous Leukemia; Cutaneous B-cell Non-Hodgkin Lymphoma; de Novo Myelodysplastic Syndromes; Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue; Hepatosplenic T-cell Lymphoma; Intraocular Lymphoma; Myelodysplastic/Myeloproliferative Neoplasm, Unclassifiable; Nodal Marginal Zone B-cell Lymphoma; Noncutaneous Extranodal Lymphoma; Peripheral T-cell Lymphoma; Post-transplant Lymphoproliferative Disorder; Previously Treated Myelodysplastic Syndromes; Recurrent Adult Acute Lymphoblastic Leukemia; Recurrent Adult Acute Myeloid Leukemia; Recurrent Adult Burkitt Lymphoma; Recurrent Adult Diffuse Large Cell Lymphoma; Recurrent Adult Diffuse Mixed Cell Lymphoma; Recurrent Adult Diffuse Small Cleaved Cell Lymphoma; Recurrent Adult Grade III Lymphomatoid Granulomatosis; Recurrent Adult Hodgkin Lymphoma; Recurrent Adult Immunoblastic Large Cell Lymphoma; Recurrent Adult Lymphoblastic Lymphoma; Recurrent Adult T-cell Leukemia/Lymphoma; Recurrent Cutaneous T-cell Non-Hodgkin Lymphoma; Recurrent Grade 1 Follicular Lymphoma; Recurrent Grade 2 Follicular Lymphoma; Recurrent Grade 3 Follicular Lymphoma; Recurrent Mantle Cell Lymphoma; Recurrent Marginal Zone Lymphoma; Recurrent Mycosis Fungoides/Sezary Syndrome; Recurrent Small Lymphocytic Lymphoma; Refractory Chronic Lymphocytic Leukemia; Refractory Hairy Cell Leukemia; Refractory Multiple Myeloma; Relapsing Chronic Myelogenous Leukemia; Secondary Acute Myeloid Leukemia; Secondary Myelodysplastic Syndromes; Small Intestine Lymphoma; Splenic Marginal Zone Lymphoma; T-cell Large Granular Lymphocyte Leukemia; Testicular Lymphoma; Waldenström Macroglobulinemia
University of Medicine and Dentistry of New Jersey
2014-01 PHASE2
NCT02949349 COMPLETED
Lupus Nephritis
Genovate Biotechnology Co., Ltd.,
2015-07 PHASE2
NCT02390362 TERMINATED
Frequent Relapsing Nephrotic Syndrome; Steroid Dependent Nephrotic Syndrome
Nationwide Children's Hospital
2015-01 PHASE3
NCT02178683 UNKNOWN
Graft Versus Host Disease
Colorado Blood Cancer Institute
2010-11 PHASE3
NCT01714817 TERMINATED
Lupus Nephritis
Bristol-Myers Squibb
2013-01-22 PHASE3
NCT00686556 COMPLETED
Acute Lymphoblastic Leukemia; Myelodysplastic Syndrome; Multiple Myeloma
Masonic Cancer Center, University of Minnesota
2012-08 PHASE1
NCT01544491 COMPLETED
Prevention of Acute Rejection in Paediatric Recipients of a Renal Transplant
Novartis Pharmaceuticals
2012-08-17 PHASE3
NCT00589316 TERMINATED
Acute Myeloid Leukemia Arising From Previous Myelodysplastic Syndrome; Adult Acute Lymphoblastic Leukemia in Remission; Adult Acute Myeloid Leukemia in Remission; CD45-Positive Neoplastic Cells Present; Chronic Myelomonocytic Leukemia; Previously Treated Myelodysplastic Syndrome; Refractory Anemia With Excess Blasts; Refractory Anemia With Ring Sideroblasts; Refractory Cytopenia With Multilineage Dysplasia; Refractory Cytopenia With Multilineage Dysplasia and Ring Sideroblasts
Fred Hutchinson Cancer Center
2007-10-05 PHASE1
NCT00793572 COMPLETED
Refractory Plasma Cell Myeloma
Fred Hutchinson Cancer Center
2008-10 PHASE2
NCT00498316 COMPLETED
Myelodysplastic Syndrome; Leukemia
M.D. Anderson Cancer Center
2007-07-03 PHASE1
NCT01582048 TERMINATED
Patients Receiving Mismatched Allogeneic HCT
Prof. Dr. med. Wolfgang Bethge
2012-04 PHASE2
NCT01790594 TERMINATED
Simultaneous Kidney and Pancreas Transplantation
National Institute of Allergy and Infectious Diseases (NIAID)
2013-02 PHASE2
NCT00494741 COMPLETED
Kidney Transplant
Mario Negri Institute for Pharmacological Research
2007-05 PHASE4
NCT01318915 TERMINATED
Renal Transplant Recipients
National Institute of Allergy and Infectious Diseases (NIAID)
2011-07-25 EARLY_PHASE1
NCT01392989 COMPLETED
Neural Tube Defects; Anemia; Leukemia, Myeloid; Bone Marrow Transplant Failure; Myelodysplastic Syndromes (MDS); Myeloproliferative Disorders
Everett Meyer
2011-03 PHASE2
NCT01860183 COMPLETED
Kidney Transplantation; Kidney Failure
Clinical Hospital Merkur
2013-05 PHASE4
NCT00533442 COMPLETED
Type 1 Diabetes
University of Miami
2000-09 PHASE2
NCT01903798 COMPLETED
Alcoholic Hepatitis
Southern California Institute for Research and Education
2014-12 PHASE2
NCT02743247 COMPLETED
Healthy Volunteers
Seoul National University Hospital
2015-10 PHASE1
NCT01856257 TERMINATED
Primary Renal Allograft Candidate; Kidney Transplantation
National Institute of Allergy and Infectious Diseases (NIAID)
2013-07 PHASE2
NCT01843348 COMPLETED
Kidney Transplantation; Renal Transplantation
Novartis Pharmaceuticals
2012-12-27 PHASE3
NCT01284725 COMPLETED
Nephritis of Lupus
Assistance Publique Hopitaux De Marseille
2011-02-16 PHASE3
NCT00566696 COMPLETED
Leukemia, Acute Lymphocytic (ALL); Leukemia, Myeloid, Acute(AML); Leukemia, Myeloid, Chronic(CML); Juvenile Myelomonocytic Leukemia (JMML); Hemoglobinuria, Paroxysmal Nocturnal (PNH); Hodgkin Lymphoma; Lymphoma, Non-Hodgkin (NHL); Myelodysplastic Syndrome (MDS)
St. Jude Children's Research Hospital
2007-12-14 PHASE2
NCT01680952 COMPLETED
Kidney Transplant Patients
Yonsei University
2012-09 PHASE4
NCT00005803 COMPLETED
Prolymphocytic Leukemia; Recurrent Adult Hodgkin Lymphoma; Recurrent Childhood Hodgkin Lymphoma; Recurrent Childhood Non-Hodgkin Lymphoma; Recurrent Chronic Lymphocytic Leukemia; Recurrent Non-Hodgkin Lymphoma; Recurrent Small Lymphocytic Lymphoma; Refractory Childhood Hodgkin Lymphoma; Refractory Chronic Lymphocytic Leukemia; Refractory Hodgkin Lymphoma; Refractory Non-Hodgkin Lymphoma; Refractory Small Lymphocytic Lymphoma; T-Cell Chronic Lymphocytic Leukemia; T-Cell Prolymphocytic Leukemia
Fred Hutchinson Cancer Center
1999-09 PHASE1; PHASE2
NCT01884571 COMPLETED
Amyotrophic Lateral Sclerosis (ALS)
Emory University
2013-10 PHASE2
NCT01930890 TERMINATED
Lupus Nephritis
Biogen
2013-11 PHASE2
NCT01766375 UNKNOWN
Acute Myeloid Leukemia
Guangxi Medical University
2012-08 PHASE3
NCT01093586 COMPLETED
Acute Myeloid Leukemia With Multilineage Dysplasia Following Myelodysplastic Syndrome; Adult Acute Lymphoblastic Leukemia in Remission; Adult Acute Megakaryoblastic Leukemia (M7); Adult Acute Minimally Differentiated Myeloid Leukemia (M0); Adult Acute Monoblastic Leukemia (M5a); Adult Acute Monocytic Leukemia (M5b); Adult Acute Myeloid Leukemia in Remission; Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities; Adult Acute Myeloid Leukemia With t(16;16)(p13;q22); Adult Erythroleukemia (M6a); Adult Nasal Type Extranodal NK/T-cell Lymphoma; Adult Pure Erythroid Leukemia (M6b); B-cell Adult Acute Lymphoblastic Leukemia; B-cell Childhood Acute Lymphoblastic Leukemia; Blastic Phase Chronic Myelogenous Leukemia; Burkitt Lymphoma; Childhood Acute Erythroleukemia (M6); Childhood Acute Lymphoblastic Leukemia in Remission; Childhood Acute Megakaryocytic Leukemia (M7); Childhood Acute Minimally Differentiated Myeloid Leukemia (M0); Childhood Acute Monoblastic Leukemia (M5a); Childhood Acute Monocytic Leukemia (M5b); Childhood Acute Myeloid Leukemia in Remission; Childhood Chronic Myelogenous Leukemia; Childhood Diffuse Large Cell Lymphoma; Childhood Immunoblastic Large Cell Lymphoma; Childhood Myelodysplastic Syndromes; Childhood Nasal Type Extranodal NK/T-cell Lymphoma; Chronic Myelomonocytic Leukemia; Chronic Phase Chronic Myelogenous Leukemia; Cutaneous B-cell Non-Hodgkin Lymphoma; de Novo Myelodysplastic Syndromes; Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue; Juvenile Myelomonocytic Leukemia; Myelodysplastic/Myeloproliferative Neoplasm, Unclassifiable; Nodal Marginal Zone B-cell Lymphoma; Previously Treated Myelodysplastic Syndromes; Prolymphocytic Leukemia; Recurrent Adult Acute Lymphoblastic Leukemia; Recurrent Adult Acute Myeloid Leukemia; Recurrent Adult Burkitt Lymphoma; Recurrent Adult Diffuse Large Cell Lymphoma; Recurrent Adult Diffuse Mixed Cell Lymphoma; Recurrent Adult Diffuse Small Cleaved Cell Lymphoma; Recurrent Adult Grade III Lymphomatoid Granulomatosis; Recurrent Adult Immunoblastic Large Cell Lymphoma; Recurrent Adult Lymphoblastic Lymphoma; Recurrent Childhood Acute Lymphoblastic Leukemia; Recurrent Childhood Acute Myeloid Leukemia; Recurrent Childhood Anaplastic Large Cell Lymphoma; Recurrent Childhood Grade III Lymphomatoid Granulomatosis; Recurrent Childhood Large Cell Lymphoma; Recurrent Childhood Lymphoblastic Lymphoma; Recurrent Childhood Small Noncleaved Cell Lymphoma; Recurrent Cutaneous T-cell Non-Hodgkin Lymphoma; Recurrent Grade 1 Follicular Lymphoma; Recurrent Grade 2 Follicular Lymphoma; Recurrent Grade 3 Follicular Lymphoma; Recurrent Mantle Cell Lymphoma; Recurrent Marginal Zone Lymphoma; Recurrent Mycosis Fungoides/Sezary Syndrome; Recurrent Small Lymphocytic Lymphoma; Refractory Chronic Lymphocytic Leukemia; Relapsing Chronic Myelogenous Leukemia; Secondary Acute Myeloid Leukemia; Secondary Myelodysplastic Syndromes; Secondary Myelofibrosis; Splenic Marginal Zone Lymphoma; Stage I Chronic Lymphocytic Leukemia; Stage II Chronic Lymphocytic Leukemia; Stage III Chronic Lymphocytic Leukemia; Stage IV Chronic Lymphocytic Leukemia; T-cell Adult Acute Lymphoblastic Leukemia; T-cell Childhood Acute Lymphoblastic Leukemia; T-cell Large Granular Lymphocyte Leukemia; Waldenstrom Macroglobulinemia
Case Comprehensive Cancer Center
2007-09 PHASE2
NCT01399047 COMPLETED
Juvenile Neuronal Ceroid Lipofuscinosis
University of Rochester
2011-07 PHASE2
NCT00245037 COMPLETED
Chronic Myeloproliferative Disorders; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Neoplasms; Precancerous Condition
OHSU Knight Cancer Institute
2005-06 PHASE1; PHASE2
NCT03200002 COMPLETED
To Compare the Effects of Mycophenolate Mofetil With Cyclophosphamide in Neplaese Lupus Nephritis Patients
Chitwan Medical College
2014-01-01 PHASE2
NCT00970073 COMPLETED
Liver Transplantation
The Cleveland Clinic
2009-08
NCT01842269 COMPLETED
Kidney Transplantation
Chong Kun Dang Pharmaceutical
2013-01 PHASE4
NCT01822483 COMPLETED
Renal Transplantation
Irmandade Santa Casa de Misericórdia de Porto Alegre
2013-04 PHASE4
NCT00096161 COMPLETED
Acute Lymphoblastic Leukemia; Acute Myeloid Leukemia; Chronic Lymphocytic Leukemia; Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Graft Versus Host Disease; Hodgkin Lymphoma; Myelodysplastic/Myeloproliferative Neoplasm; Non-Hodgkin Lymphoma; Plasma Cell Myeloma; Waldenstrom Macroglobulinemia
Fred Hutchinson Cancer Center
2003-05 PHASE2
NCT00103792 COMPLETED
Wegener's Granulomatosis; Vasculitis
University Medical Center Groningen
2004-12 PHASE3
NCT01446484 UNKNOWN
End-Stage Renal Disease; Kidney Failure
Pirogov Russian National Research Medical University
2011-10 PHASE1; PHASE2
NCT01175785 COMPLETED
Accelerated Phase Chronic Myelogenous Leukemia; Adult Acute Myeloid Leukemia in Remission; Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities; Adult Acute Myeloid Leukemia With Del(5q); Adult Acute Myeloid Leukemia With Inv(16)(p13;q22); Adult Acute Myeloid Leukemia With t(15;17)(q22;q12); Adult Acute Myeloid Leukemia With t(16;16)(p13;q22); Adult Acute Myeloid Leukemia With t(8;21)(q22;q22); Childhood Acute Lymphoblastic Leukemia in Remission; Childhood Acute Myeloid Leukemia in Remission; Childhood Chronic Myelogenous Leukemia; Childhood Myelodysplastic Syndromes; Chronic Phase Chronic Myelogenous Leukemia; de Novo Myelodysplastic Syndromes; Previously Treated Myelodysplastic Syndromes; Refractory Anemia; Refractory Anemia With Excess Blasts; Refractory Anemia With Excess Blasts in Transformation; Relapsing Chronic Myelogenous Leukemia; Secondary Myelodysplastic Syndromes
Nohla Therapeutics, Inc.
2010-08 PHASE2
NCT00119366 TERMINATED
Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities; Adult Acute Myeloid Leukemia With Del(5q); Adult Acute Myeloid Leukemia With Inv(16)(p13;q22); Adult Acute Myeloid Leukemia With t(15;17)(q22;q12); Adult Acute Myeloid Leukemia With t(16;16)(p13;q22); Adult Acute Myeloid Leukemia With t(8;21)(q22;q22); Childhood Myelodysplastic Syndromes; Chronic Myelomonocytic Leukemia; Previously Treated Myelodysplastic Syndromes; Recurrent Adult Acute Myeloid Leukemia; Recurrent Childhood Acute Myeloid Leukemia; Refractory Anemia With Excess Blasts; Refractory Anemia With Excess Blasts in Transformation; Refractory Anemia With Ringed Sideroblasts; Refractory Cytopenia With Multilineage Dysplasia; Secondary Acute Myeloid Leukemia; Secondary Myelodysplastic Syndromes
Fred Hutchinson Cancer Center
2003-05 PHASE2
NCT00036738 COMPLETED
Adult Acute Lymphoblastic Leukemia in Remission; Adult B Acute Lymphoblastic Leukemia With t(9;22)(q34.1;q11.2); BCR-ABL1; Blastic Phase; Childhood Acute Lymphoblastic Leukemia in Remission; Childhood B Acute Lymphoblastic Leukemia With t(9;22)(q34.1;q11.2); BCR-ABL1; Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Chronic Phase of Disease; Recurrent Adult Acute Lymphoblastic Leukemia; Recurrent Childhood Acute Lymphoblastic Leukemia; Recurrent Disease
Fred Hutchinson Cancer Center
2001-07-13 PHASE2
NCT01780844 COMPLETED
Kidney Transplantation
Astellas Pharma Global Development, Inc.
2013-03-05 PHASE2
NCT00371319 COMPLETED
Lupus Nephritis
Tuen Mun Hospital
2005-09 PHASE4
NCT01766518 UNKNOWN
Evidence of Liver Transplantation
Chong Kun Dang Pharmaceutical
2009-11 PHASE4
NCT00185640 COMPLETED
Blood Cancer; Leukemia
Stanford University
2003-03 PHASE2
NCT00387959 COMPLETED
Leukemia; Lymphoma
Memorial Sloan Kettering Cancer Center
2006-07 PHASE2
NCT00089011 COMPLETED
Accelerated Phase Chronic Myelogenous Leukemia; Adult Acute Lymphoblastic Leukemia in Remission; Adult Acute Myeloid Leukemia in Remission; Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities; Adult Acute Myeloid Leukemia With Del(5q); Adult Acute Myeloid Leukemia With Inv(16)(p13;q22); Adult Acute Myeloid Leukemia With t(15;17)(q22;q12); Adult Acute Myeloid Leukemia With t(16;16)(p13;q22); Adult Acute Myeloid Leukemia With t(8;21)(q22;q22); Adult Nasal Type Extranodal NK/T-cell Lymphoma; Anaplastic Large Cell Lymphoma; Angioimmunoblastic T-cell Lymphoma; Blastic Phase Chronic Myelogenous Leukemia; Childhood Acute Lymphoblastic Leukemia in Remission; Childhood Acute Myeloid Leukemia in Remission; Childhood Burkitt Lymphoma; Childhood Chronic Myelogenous Leukemia; Childhood Diffuse Large Cell Lymphoma; Childhood Immunoblastic Large Cell Lymphoma; Childhood Myelodysplastic Syndromes; Childhood Nasal Type Extranodal NK/T-cell Lymphoma; Chronic Phase Chronic Myelogenous Leukemia; Contiguous Stage II Adult Burkitt Lymphoma; Contiguous Stage II Adult Diffuse Large Cell Lymphoma; Contiguous Stage II Adult Diffuse Mixed Cell Lymphoma; Contiguous Stage II Adult Diffuse Small Cleaved Cell Lymphoma; Contiguous Stage II Adult Immunoblastic Large Cell Lymphoma; Contiguous Stage II Adult Lymphoblastic Lymphoma; Contiguous Stage II Grade 1 Follicular Lymphoma; Contiguous Stage II Grade 2 Follicular Lymphoma; Contiguous Stage II Grade 3 Follicular Lymphoma; Contiguous Stage II Mantle Cell Lymphoma; Contiguous Stage II Marginal Zone Lymphoma; Contiguous Stage II Small Lymphocytic Lymphoma; Cutaneous B-cell Non-Hodgkin Lymphoma; de Novo Myelodysplastic Syndromes; Essential Thrombocythemia; Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue; Hepatosplenic T-cell Lymphoma; Intraocular Lymphoma; Nodal Marginal Zone B-cell Lymphoma; Noncontiguous Stage II Adult Burkitt Lymphoma; Noncontiguous Stage II Adult Diffuse Large Cell Lymphoma; Noncontiguous Stage II Adult Diffuse Mixed Cell Lymphoma; Noncontiguous Stage II Adult Diffuse Small Cleaved Cell Lymphoma; Noncontiguous Stage II Adult Immunoblastic Large Cell Lymphoma; Noncontiguous Stage II Adult Lymphoblastic Lymphoma; Noncontiguous Stage II Grade 1 Follicular Lymphoma; Noncontiguous Stage II Grade 2 Follicular Lymphoma; Noncontiguous Stage II Grade 3 Follicular Lymphoma; Noncontiguous Stage II Mantle Cell Lymphoma; Noncontiguous Stage II Marginal Zone Lymphoma; Noncontiguous Stage II Small Lymphocytic Lymphoma; Noncutaneous Extranodal Lymphoma; Peripheral T-cell Lymphoma; Polycythemia Vera; Post-transplant Lymphoproliferative Disorder; Previously Treated Myelodysplastic Syndromes; Primary Myelofibrosis; Prolymphocytic Leukemia; Recurrent Adult Acute Lymphoblastic Leukemia; Recurrent Adult Acute Myeloid Leukemia; Recurrent Adult Burkitt Lymphoma; Recurrent Adult Diffuse Large Cell Lymphoma; Recurrent Adult Diffuse Mixed Cell Lymphoma; Recurrent Adult Diffuse Small Cleaved Cell Lymphoma; Recurrent Adult Grade III Lymphomatoid Granulomatosis; Recurrent Adult Hodgkin Lymphoma; Recurrent Adult Immunoblastic Large Cell Lymphoma; Recurrent Adult Lymphoblastic Lymphoma; Recurrent Adult T-cell Leukemia/Lymphoma; Recurrent Childhood Acute Lymphoblastic Leukemia; Recurrent Childhood Acute Myeloid Leukemia; Recurrent Childhood Anaplastic Large Cell Lymphoma; Recurrent Childhood Grade III Lymphomatoid Granulomatosis; Recurrent Childhood Large Cell Lymphoma; Recurrent Childhood Lymphoblastic Lymphoma; Recurrent Childhood Small Noncleaved Cell Lymphoma; Recurrent Cutaneous T-cell Non-Hodgkin Lymphoma; Recurrent Grade 1 Follicular Lymphoma; Recurrent Grade 2 Follicular Lymphoma; Recurrent Grade 3 Follicular Lymphoma; Recurrent Mantle Cell Lymphoma; Recurrent Marginal Zone Lymphoma; Recurrent Mycosis Fungoides/Sezary Syndrome; Recurrent Small Lymphocytic Lymphoma; Recurrent/Refractory Childhood Hodgkin Lymphoma; Refractory Chronic Lymphocytic Leukemia; Refractory Hairy Cell Leukemia; Refractory Multiple Myeloma; Relapsing Chronic Myelogenous Leukemia; Small Intestine Lymphoma; Splenic Marginal Zone Lymphoma; Stage I Adult Burkitt Lymphoma; Stage I Adult Diffuse Large Cell Lymphoma; Stage I Adult Diffuse Mixed Cell Lymphoma; Stage I Adult Diffuse Small Cleaved Cell Lymphoma; Stage I Adult Immunoblastic Large Cell Lymphoma; Stage I Adult Lymphoblastic Lymphoma; Stage I Adult T-cell Leukemia/Lymphoma; Stage I Childhood Anaplastic Large Cell Lymphoma; Stage I Childhood Large Cell Lymphoma; Stage I Childhood Lymphoblastic Lymphoma; Stage I Childhood Small Noncleaved Cell Lymphoma; Stage I Chronic Lymphocytic Leukemia; Stage I Cutaneous T-cell Non-Hodgkin Lymphoma; Stage I Grade 1 Follicular Lymphoma; Stage I Grade 2 Follicular Lymphoma; Stage I Grade 3 Follicular Lymphoma; Stage I Mantle Cell Lymphoma; Stage I Marginal Zone Lymphoma; Stage I Multiple Myeloma; Stage I Small Lymphocytic Lymphoma; Stage IA Mycosis Fungoides/Sezary Syndrome; Stage IB Mycosis Fungoides/Sezary Syndrome; Stage II Adult T-cell Leukemia/Lymphoma; Stage II Childhood Anaplastic Large Cell Lymphoma; Stage II Childhood Large Cell Lymphoma; Stage II Childhood Lymphoblastic Lymphoma; Stage II Childhood Small Noncleaved Cell Lymphoma; Stage II Chronic Lymphocytic Leukemia; Stage II Cutaneous T-cell Non-Hodgkin Lymphoma; Stage II Multiple Myeloma; Stage IIA Mycosis Fungoides/Sezary Syndrome; Stage IIB Mycosis Fungoides/Sezary Syndrome; Stage III Adult Burkitt Lymphoma; Stage III Adult Diffuse Large Cell Lymphoma; Stage III Adult Diffuse Mixed Cell Lymphoma; Stage III Adult Diffuse Small Cleaved Cell Lymphoma; Stage III Adult Immunoblastic Large Cell Lymphoma; Stage III Adult Lymphoblastic Lymphoma; Stage III Adult T-cell Leukemia/Lymphoma; Stage III Childhood Anaplastic Large Cell Lymphoma; Stage III Childhood Large Cell Lymphoma; Stage III Childhood Lymphoblastic Lymphoma; Stage III Childhood Small Noncleaved Cell Lymphoma; Stage III Chronic Lymphocytic Leukemia; Stage III Cutaneous T-cell Non-Hodgkin Lymphoma; Stage III Grade 1 Follicular Lymphoma; Stage III Grade 2 Follicular Lymphoma; Stage III Grade 3 Follicular Lymphoma; Stage III Mantle Cell Lymphoma; Stage III Marginal Zone Lymphoma; Stage III Multiple Myeloma; Stage III Small Lymphocytic Lymphoma; Stage IIIA Mycosis Fungoides/Sezary Syndrome; Stage IIIB Mycosis Fungoides/Sezary Syndrome; Stage IV Adult Burkitt Lymphoma; Stage IV Adult Diffuse Large Cell Lymphoma; Stage IV Adult Diffuse Mixed Cell Lymphoma; Stage IV Adult Diffuse Small Cleaved Cell Lymphoma; Stage IV Adult Immunoblastic Large Cell Lymphoma; Stage IV Adult Lymphoblastic Lymphoma; Stage IV Adult T-cell Leukemia/Lymphoma; Stage IV Childhood Anaplastic Large Cell Lymphoma; Stage IV Childhood Large Cell Lymphoma; Stage IV Childhood Lymphoblastic Lymphoma; Stage IV Childhood Small Noncleaved Cell Lymphoma; Stage IV Chronic Lymphocytic Leukemia; Stage IV Cutaneous T-cell Non-Hodgkin Lymphoma; Stage IV Grade 1 Follicular Lymphoma; Stage IV Grade 2 Follicular Lymphoma; Stage IV Grade 3 Follicular Lymphoma; Stage IV Mantle Cell Lymphoma; Stage IV Marginal Zone Lymphoma; Stage IV Small Lymphocytic Lymphoma; Stage IVA Mycosis Fungoides/Sezary Syndrome; Stage IVB Mycosis Fungoides/Sezary Syndrome; Testicular Lymphoma; Untreated Adult Acute Lymphoblastic Leukemia; Untreated Adult Acute Myeloid Leukemia; Untreated Childhood Acute Lymphoblastic Leukemia; Untreated Childhood Acute Myeloid Leukemia and Other Myeloid Malignancies; Waldenström Macroglobulinemia
Fred Hutchinson Cancer Center
2004-04 PHASE2
NCT00412360 COMPLETED
Acute Myelogenous Leukemia; Acute Lymphocytic Leukemia; Chronic Myelogenous Leukemia; Myelodysplastic Syndrome; Natural Killer Cell Lymphoblastic Leukemia/Lymphoma
Medical College of Wisconsin
2006-12 PHASE3
NCT01321112 UNKNOWN
Gene Expression; Immunosuppression Conversion; Liver Transplantation
Pontificia Universidad Catolica de Chile
2011-02
NCT00709592 COMPLETED
Non-Hodgkin's Lymphoma; Leukemia; Multiple Myeloma; Acute Myeloid Leukemia; Hodgkin Lymphoma; Chronic Lymphocytic Leukemia; Chronic Myelogenous Leukemia; Myelodysplastic Syndrome
Virginia Commonwealth University
2008-07-21 PHASE2
NCT00075478 COMPLETED
Acute Lymphoblastic Leukemia in Remission; Acute Myeloid Leukemia in Remission; Aggressive Non-Hodgkin Lymphoma; Chronic Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Diffuse Large B-Cell Lymphoma; Hematopoietic and Lymphoid Cell Neoplasm; Indolent Non-Hodgkin Lymphoma; Mantle Cell Lymphoma; Myelodysplastic/Myeloproliferative Neoplasm; Plasma Cell Myeloma; Refractory Chronic Lymphocytic Leukemia; Refractory Hodgkin Lymphoma; Waldenstrom Macroglobulinemia
Fred Hutchinson Cancer Center
2003-10 PHASE3
NCT00263328 COMPLETED
Kidney Transplantation
Pfizer
2005-12 PHASE2
NCT01509300 UNKNOWN
Acute Leukemia; Myelodysplastic Syndrome; Solid Tumors
Asan Medical Center
2012-01 PHASE1; PHASE2
NCT00811915 TERMINATED
Kidney Transplantation
University Hospital, Rouen
2009-01 PHASE3
NCT01017029 COMPLETED
Cardiac Transplantation
Novartis Pharmaceuticals
2009-09 PHASE4
NCT01363752 COMPLETED
Kidney Transplantation
Astellas Pharma Inc
2011-03-08 PHASE4
NCT00548717 TERMINATED
Graft-vs-Host Disease
Dana-Farber Cancer Institute
2007-10 PHASE2
NCT00789308 COMPLETED
Diabetes Mellitus, Type I
National Institute of Allergy and Infectious Diseases (NIAID)
2008-07-11 PHASE2
NCT00453388 COMPLETED
Acute Myeloid Leukemia in Remission; de Novo Myelodysplastic Syndrome; Fanconi Anemia; Previously Treated Myelodysplastic Syndrome
Fred Hutchinson Cancer Center
2007-02 PHASE2
NCT01566006 UNKNOWN
Diabetic Nephropathy; Chronic Kidney Disease
The Nazareth Hospital, Israel
2012-04
NCT01154387 UNKNOWN
End Stage Renal Disease; Renal Transplant
Tolera Therapeutics, Inc
2010-07 PHASE1; PHASE2
NCT01109498 UNKNOWN
Familial Lipoprotein Lipase Deficiency
Amsterdam Molecular Therapeutics
2007-08 PHASE2; PHASE3
NCT01304836 COMPLETED
Kidney Transplantation
Astellas Pharma Inc
2011-01-22 PHASE4
NCT01350245 COMPLETED
Acute Myeloid Leukemia; Myelodysplastic Syndromes; Biphenotypic Leukemia; Acute Lymphocytic Leukemia; Chronic Myeloid Leukemia; Chronic Lymphocytic Leukemia; Plasma Cell Neoplasms; Lymphoma; Hodgkin's Disease; Aplastic Anemia
Sidney Kimmel Comprehensive Cancer Center at Thomas Jefferson University
2010-07 PHASE2
NCT00693446 UNKNOWN
Pancreas Transplantation; Kidney Transplantation
Nantes University Hospital
2004-04 PHASE4
NCT01056822 COMPLETED
Prophilaxis of Acute Rejection in Patients Receiving a Renal Allograft
Novartis Pharmaceuticals
2010-05 PHASE4
NCT01187953 COMPLETED
Renal Failure
Veloxis Pharmaceuticals
2010-09 PHASE3
NCT00255684 TERMINATED
Chronic Myeloproliferative Disorders; Graft Versus Host Disease; Leukemia; Lymphoma; Multiple Myeloma; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Neoplasms
University of Rochester
2003-12
NCT00763490 COMPLETED
Hematological Malignancies
University of Michigan Rogel Cancer Center
2008-12 PHASE2
NCT01044745 TERMINATED
Accelerated Phase Chronic Myelogenous Leukemia; Adult Acute Lymphoblastic Leukemia in Remission; Adult Acute Myeloid Leukemia in Remission; Adult Nasal Type Extranodal NK/T-cell Lymphoma; Blastic Phase Chronic Myelogenous Leukemia; Contiguous Stage II Adult Burkitt Lymphoma; Contiguous Stage II Adult Diffuse Large Cell Lymphoma; Contiguous Stage II Adult Diffuse Mixed Cell Lymphoma; Contiguous Stage II Adult Diffuse Small Cleaved Cell Lymphoma; Contiguous Stage II Adult Immunoblastic Large Cell Lymphoma; Contiguous Stage II Adult Lymphoblastic Lymphoma; Contiguous Stage II Grade 1 Follicular Lymphoma; Contiguous Stage II Grade 2 Follicular Lymphoma; Contiguous Stage II Grade 3 Follicular Lymphoma; Contiguous Stage II Mantle Cell Lymphoma; Contiguous Stage II Marginal Zone Lymphoma; Contiguous Stage II Small Lymphocytic Lymphoma; de Novo Myelodysplastic Syndromes; Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue; Graft Versus Host Disease; Nodal Marginal Zone B-cell Lymphoma; Noncontiguous Stage II Adult Burkitt Lymphoma; Noncontiguous Stage II Adult Diffuse Large Cell Lymphoma; Noncontiguous Stage II Adult Diffuse Mixed Cell Lymphoma; Noncontiguous Stage II Adult Diffuse Small Cleaved Cell Lymphoma; Noncontiguous Stage II Adult Immunoblastic Large Cell Lymphoma; Noncontiguous Stage II Adult Lymphoblastic Lymphoma; Noncontiguous Stage II Grade 1 Follicular Lymphoma; Noncontiguous Stage II Grade 2 Follicular Lymphoma; Noncontiguous Stage II Grade 3 Follicular Lymphoma; Noncontiguous Stage II Mantle Cell Lymphoma; Noncontiguous Stage II Marginal Zone Lymphoma; Noncontiguous Stage II Small Lymphocytic Lymphoma; Previously Treated Myelodysplastic Syndromes; Recurrent Adult Acute Lymphoblastic Leukemia; Recurrent Adult Acute Myeloid Leukemia; Recurrent Adult Burkitt Lymphoma; Recurrent Adult Diffuse Large Cell Lymphoma; Recurrent Adult Diffuse Mixed Cell Lymphoma; Recurrent Adult Diffuse Small Cleaved Cell Lymphoma; Recurrent Adult Grade III Lymphomatoid Granulomatosis; Recurrent Adult Immunoblastic Large Cell Lymphoma; Recurrent Adult Lymphoblastic Lymphoma; Recurrent Adult T-cell Leukemia/Lymphoma; Recurrent Cutaneous T-cell Non-Hodgkin Lymphoma; Recurrent Grade 1 Follicular Lymphoma; Recurrent Grade 2 Follicular Lymphoma; Recurrent Grade 3 Follicular Lymphoma; Recurrent Mantle Cell Lymphoma; Recurrent Marginal Zone Lymphoma; Recurrent Mycosis Fungoides/Sezary Syndrome; Recurrent Small Lymphocytic Lymphoma; Refractory Chronic Lymphocytic Leukemia; Relapsing Chronic Myelogenous Leukemia; Secondary Myelodysplastic Syndromes; Splenic Marginal Zone Lymphoma; Stage I Adult Burkitt Lymphoma; Stage I Adult Diffuse Large Cell Lymphoma; Stage I Adult Diffuse Mixed Cell Lymphoma; Stage I Adult Diffuse Small Cleaved Cell Lymphoma; Stage I Adult Immunoblastic Large Cell Lymphoma; Stage I Adult Lymphoblastic Lymphoma; Stage I Adult T-cell Leukemia/Lymphoma; Stage I Chronic Lymphocytic Leukemia; Stage I Cutaneous T-cell Non-Hodgkin Lymphoma; Stage I Grade 1 Follicular Lymphoma; Stage I Grade 2 Follicular Lymphoma; Stage I Grade 3 Follicular Lymphoma; Stage I Mantle Cell Lymphoma; Stage I Marginal Zone Lymphoma; Stage I Mycosis Fungoides/Sezary Syndrome; Stage I Small Lymphocytic Lymphoma; Stage II Adult T-cell Leukemia/Lymphoma; Stage II Chronic Lymphocytic Leukemia; Stage II Cutaneous T-cell Non-Hodgkin Lymphoma; Stage II Mycosis Fungoides/Sezary Syndrome; Stage III Adult Burkitt Lymphoma; Stage III Adult Diffuse Large Cell Lymphoma; Stage III Adult Diffuse Mixed Cell Lymphoma; Stage III Adult Diffuse Small Cleaved Cell Lymphoma; Stage III Adult Immunoblastic Large Cell Lymphoma; Stage III Adult Lymphoblastic Lymphoma; Stage III Adult T-cell Leukemia/Lymphoma; Stage III Chronic Lymphocytic Leukemia; Stage III Cutaneous T-cell Non-Hodgkin Lymphoma; Stage III Grade 1 Follicular Lymphoma; Stage III Grade 2 Follicular Lymphoma; Stage III Grade 3 Follicular Lymphoma; Stage III Mantle Cell Lymphoma; Stage III Marginal Zone Lymphoma; Stage III Mycosis Fungoides/Sezary Syndrome; Stage III Small Lymphocytic Lymphoma; Stage IV Adult Burkitt Lymphoma; Stage IV Adult Diffuse Large Cell Lymphoma; Stage IV Adult Diffuse Mixed Cell Lymphoma; Stage IV Adult Diffuse Small Cleaved Cell Lymphoma; Stage IV Adult Immunoblastic Large Cell Lymphoma; Stage IV Adult Lymphoblastic Lymphoma; Stage IV Adult T-cell Leukemia/Lymphoma; Stage IV Chronic Lymphocytic Leukemia; Stage IV Cutaneous T-cell Non-Hodgkin Lymphoma; Stage IV Grade 1 Follicular Lymphoma; Stage IV Grade 2 Follicular Lymphoma; Stage IV Grade 3 Follicular Lymphoma; Stage IV Mantle Cell Lymphoma; Stage IV Marginal Zone Lymphoma; Stage IV Mycosis Fungoides/Sezary Syndrome; Stage IV Small Lymphocytic Lymphoma; Untreated Adult Acute Lymphoblastic Leukemia; Untreated Adult Acute Myeloid Leukemia; Waldenström Macroglobulinemia
University of Nebraska
2009-12-10 PHASE2
NCT00934791 TERMINATED
Polycystic Liver Disease
Mayo Clinic
2009-02
NCT00669890 TERMINATED
Acute Myeloid Leukemia; Juvenile Myelomonocytic Leukemia; Myelodysplastic Syndrome
New York Medical College
2004-05 PHASE1
NCT01266148 COMPLETED
Renal Function and Chronic Allograft Vasculopathy
Novartis Pharmaceuticals
2009-11 PHASE4
NCT00555373 COMPLETED
Renal Transplant
Pediatric Nephrology of Alabama
2007-11
NCT00824135 COMPLETED
Hematologic Malignancies
St. Jude Children's Research Hospital
2009-01 PHASE1
NCT00959231 UNKNOWN
Hematopoietic/Lymphoid Cancer
Cancer Research UK
2009-01 PHASE2
NCT00859131 COMPLETED
End Stage Renal Disease
Medical University of South Carolina
2009-03
NCT01044667 TERMINATED
Lung Transplantation
Vanderbilt University
2010-01
NCT01014442 COMPLETED
Lung Transplantation
Hoffmann-La Roche
2010-01 PHASE3
NCT01742624 COMPLETED
de Novo Kidney Transplantation
Astellas Pharma Korea, Inc.
2012-04 PHASE4
NCT00618527 COMPLETED
Multiple Sclerosis
Aaron Boster
2006-08 EARLY_PHASE1
NCT01135329 TERMINATED
Lymphoma; Leukemia; Myelodysplastic Syndrome
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
2010-08 PHASE2
NCT00322101 COMPLETED
Acute Myeloid Leukemia With Multilineage Dysplasia Following Myelodysplastic Syndrome; Acute Myeloid Leukemia/Transient Myeloproliferative Disorder; Adult Acute Myeloid Leukemia in Remission; Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities; Adult Acute Myeloid Leukemia With Del(5q); Adult Acute Myeloid Leukemia With Inv(16)(p13;q22); Adult Acute Myeloid Leukemia With t(15;17)(q22;q12); Adult Acute Myeloid Leukemia With t(16;16)(p13;q22); Adult Acute Myeloid Leukemia With t(8;21)(q22;q22); Childhood Acute Myeloid Leukemia in Remission; Childhood Myelodysplastic Syndromes; de Novo Myelodysplastic Syndromes; Myelodysplastic Syndrome With Isolated Del(5q); Myelodysplastic/Myeloproliferative Neoplasm, Unclassifiable; Previously Treated Myelodysplastic Syndromes; Recurrent Adult Acute Myeloid Leukemia; Recurrent Childhood Acute Myeloid Leukemia; Secondary Acute Myeloid Leukemia; Secondary Myelodysplastic Syndromes
Fred Hutchinson Cancer Center
2006-01 PHASE3
NCT01711489 COMPLETED
Healthy Subjects; Pharmacokinetics of Isavuconazole; Pharmacokinetics of Plasma Mycophenolic Acid (MPA); Pharmacokinetics of Plasma Phenolic Glucuronide of MPA (MPAG)
Astellas Pharma Global Development, Inc.
2012-03 PHASE1
NCT00943228 COMPLETED
Acute Rejection of Renal Transplant
Nova Scotia Health Authority
2010-02 PHASE4
NCT01002742 COMPLETED
Graft-versus-Host Disease; Immune System Disorders
Medical College of Wisconsin
2010-01 PHASE3
NCT00817687 COMPLETED
Kidney Transplantation
Hoffmann-La Roche
2009-01 PHASE4
NCT01288131 TERMINATED
Anti-r-HuEpo Associated PRCA Subjects
Chulalongkorn University
2009-01 PHASE3
NCT01042457 COMPLETED
Lupus Nephritis
Chulalongkorn University
2009-05 PHASE3
NCT00008450 COMPLETED
Adenosine Deaminase Deficiency; Autosomal Recessive Disorder; Immune System Disorder; Purine-Nucleoside Phosphorylase Deficiency; Severe Combined Immunodeficiency; Severe Combined Immunodeficiency With Absence of T and B Cells; X-Linked Severe Combined Immunodeficiency
Fred Hutchinson Cancer Center
1997-08-11 PHASE1
NCT00972101 WITHDRAWN
Stem Cell Transplantation; Leukemia; Lymphoma; Pediatric Disorders
M.D. Anderson Cancer Center
2009-09 PHASE1
NCT00737659 UNKNOWN
Renal Transplant
Rabin Medical Center
2008-08 PHASE4
NCT00204022 COMPLETED
Lupus Nephritis
Frédéric A. Houssiau, MD, PhD
2001-02 PHASE3
NCT00539838 TERMINATED
Systemic Lupus Erythematosus
Genentech, Inc.
2007-12-19 PHASE3
NCT00414128 COMPLETED
Vasculitis
Cambridge University Hospitals NHS Foundation Trust
2007-03 PHASE2; PHASE3
NCT00300274 COMPLETED
Graft Rejection
Novartis Pharmaceuticals
2006-01 PHASE3
NCT00717314 COMPLETED
Liver Transplantation
Hoffmann-La Roche
2008-05 PHASE4
NCT00307671 COMPLETED
Vasculitis; Wegener's Granulomatosis; Microscopic Polyangiitis; Churg-Strauss Syndrome; Polyarteritis Nodosa
Assistance Publique - Hôpitaux de Paris
2005-07 PHASE4
NCT00246129 COMPLETED
Kidney Transplantation; Kidney Diseases; Kidney Failure
EMagnusson
2005-10 PHASE4
NCT00876616 COMPLETED
Lupus Nephritis
Zhi-Hong Liu, M.D.
2009-04
NCT00105001 COMPLETED
Myelodysplastic/Myeloproliferative Neoplasm, Unclassifiable; Previously Treated Myelodysplastic Syndrome; Refractory Chronic Lymphocytic Leukemia; Refractory Plasma Cell Myeloma; Waldenstrom Macroglobulinemia; Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Adult Acute Lymphoblastic Leukemia in Remission; Adult Acute Myeloid Leukemia in Remission; Adult Acute Myeloid Leukemia With t(9;11)(p22;q23); MLLT3-MLL; Adult Acute Myeloid Leukemia With Inv(16)(p13.1q22); CBFB-MYH11; Adult Acute Promyelocytic Leukemia With t(15;17)(q22;q12); PML-RARA; Adult Acute Myeloid Leukemia With t(8;21)(q22;q22); RUNX1-RUNX1T1; Atypical Chronic Myeloid Leukemia, BCR-ABL1 Negative; Blast Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Childhood Acute Lymphoblastic Leukemia in Remission; Childhood Acute Myeloid Leukemia in Remission; Childhood Burkitt Lymphoma; Childhood Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Childhood Diffuse Large Cell Lymphoma; Childhood Immunoblastic Lymphoma; Childhood Myelodysplastic Syndrome; Stage II Contiguous Adult Burkitt Lymphoma; Stage II Contiguous Adult Diffuse Large Cell Lymphoma; Stage II Contiguous Adult Diffuse Mixed Cell Lymphoma; Stage II Contiguous Adult Diffuse Small Cleaved Cell Lymphoma; Stage II Adult Contiguous Immunoblastic Lymphoma; Stage II Contiguous Adult Lymphoblastic Lymphoma; Stage II Grade 1 Contiguous Follicular Lymphoma; Stage II Grade 2 Contiguous Follicular Lymphoma; Stage II Grade 3 Contiguous Follicular Lymphoma; Stage II Contiguous Mantle Cell Lymphoma; Stage II Non-Contiguous Adult Burkitt Lymphoma; Stage II Non-Contiguous Adult Diffuse Large Cell Lymphoma; Stage II Non-Contiguous Adult Diffuse Mixed Cell Lymphoma; Stage II Non-Contiguous Adult Diffuse Small Cleaved Cell Lymphoma; Stage II Adult Non-Contiguous Immunoblastic Lymphoma; Stage II Non-Contiguous Adult Lymphoblastic Lymphoma; Stage II Grade 1 Non-Contiguous Follicular Lymphoma; Stage II Grade 2 Non-Contiguous Follicular Lymphoma; Stage II Grade 3 Non-Contiguous Follicular Lymphoma; Stage II Non-Contiguous Mantle Cell Lymphoma; Stage II Small Lymphocytic Lymphoma; Recurrent Adult Acute Lymphoblastic Leukemia; Recurrent Adult Acute Myeloid Leukemia; Recurrent Adult Burkitt Lymphoma; Recurrent Adult Diffuse Large Cell Lymphoma; Recurrent Adult Diffuse Mixed Cell Lymphoma; Recurrent Adult Diffuse Small Cleaved Cell Lymphoma; Recurrent Adult Hodgkin Lymphoma; Recurrent Adult Immunoblastic Lymphoma; Recurrent Adult Lymphoblastic Lymphoma; Recurrent Childhood Acute Lymphoblastic Leukemia; Recurrent Childhood Acute Myeloid Leukemia; Recurrent Childhood Anaplastic Large Cell Lymphoma; Recurrent Childhood Large Cell Lymphoma; Recurrent Childhood Lymphoblastic Lymphoma; Recurrent Childhood Burkitt Lymphoma; Recurrent Grade 1 Follicular Lymphoma; Recurrent Grade 2 Follicular Lymphoma; Recurrent Grade 3 Follicular Lymphoma; Recurrent Mantle Cell Lymphoma; Recurrent Marginal Zone Lymphoma; Recurrent Small Lymphocytic Lymphoma; Recurrent Childhood Hodgkin Lymphoma; Recurrent Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Secondary Myelodysplastic Syndrome; Stage I Adult Burkitt Lymphoma; Stage I Adult Diffuse Large Cell Lymphoma; Stage I Adult Diffuse Mixed Cell Lymphoma; Stage I Adult Immunoblastic Lymphoma; Stage I Adult Lymphoblastic Lymphoma; Stage I Childhood Anaplastic Large Cell Lymphoma; Stage I Childhood Large Cell Lymphoma; Stage I Childhood Lymphoblastic Lymphoma; Stage I Childhood Burkitt Lymphoma; Stage I Grade 1 Follicular Lymphoma; Stage I Grade 2 Follicular Lymphoma; Stage I Grade 3 Follicular Lymphoma; Stage I Mantle Cell Lymphoma; Stage I Marginal Zone Lymphoma; Stage I Small Lymphocytic Lymphoma; Stage II Childhood Anaplastic Large Cell Lymphoma; Stage II Childhood Lymphoblastic Lymphoma; Stage II Childhood Burkitt Lymphoma; Stage III Adult Burkitt Lymphoma; Stage III Adult Diffuse Large Cell Lymphoma; Stage III Adult Diffuse Mixed Cell Lymphoma; Stage III Adult Diffuse Small Cleaved Cell Lymphoma; Stage III Adult Immunoblastic Lymphoma; Stage III Adult Lymphoblastic Lymphoma; Stage III Childhood Anaplastic Large Cell Lymphoma; Stage III Childhood Large Cell Lymphoma; Stage III Childhood Lymphoblastic Lymphoma; Stage III Childhood Burkitt Lymphoma; Stage III Grade 1 Follicular Lymphoma; Stage III Grade 2 Follicular Lymphoma; Stage III Grade 3 Follicular Lymphoma; Stage III Mantle Cell Lymphoma; Stage III Marginal Zone Lymphoma; Stage III Small Lymphocytic Lymphoma; Stage IV Adult Burkitt Lymphoma; Stage IV Adult Diffuse Large Cell Lymphoma; Stage IV Adult Diffuse Mixed Cell Lymphoma; Stage IV Adult Diffuse Small Cleaved Cell Lymphoma; Stage IV Adult Immunoblastic Lymphoma; Stage IV Adult Lymphoblastic Lymphoma; Stage IV Childhood Anaplastic Large Cell Lymphoma; Stage IV Childhood Large Cell Lymphoma; Stage IV Childhood Lymphoblastic Lymphoma; Stage IV Childhood Burkitt Lymphoma; Stage IV Grade 1 Follicular Lymphoma; Stage IV Grade 2 Follicular Lymphoma; Stage IV Grade 3 Follicular Lymphoma; Stage IV Mantle Cell Lymphoma; Stage IV Marginal Zone Lymphoma; Stage IV Small Lymphocytic Lymphoma
Fred Hutchinson Cancer Center
2004-11 PHASE2
NCT00782379 COMPLETED
Leukemia; Lymphoma; Myelodysplastic Syndromes
Northside Hospital, Inc.
2008-10 PHASE2
NCT00433186 COMPLETED
Diffuse Cutaneous Systemic Sclerosis
Boston University
2006-03 PHASE1
NCT00049504 COMPLETED
Accelerated Phase Chronic Myelogenous Leukemia; Adult Acute Lymphoblastic Leukemia in Remission; Adult Acute Myeloid Leukemia in Remission; Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities; Adult Acute Myeloid Leukemia With Del(5q); Adult Acute Myeloid Leukemia With Inv(16)(p13;q22); Adult Acute Myeloid Leukemia With t(15;17)(q22;q12); Adult Acute Myeloid Leukemia With t(16;16)(p13;q22); Adult Acute Myeloid Leukemia With t(8;21)(q22;q22); Adult Nasal Type Extranodal NK/T-cell Lymphoma; Anaplastic Large Cell Lymphoma; Angioimmunoblastic T-cell Lymphoma; Childhood Acute Lymphoblastic Leukemia in Remission; Childhood Acute Myeloid Leukemia in Remission; Childhood Burkitt Lymphoma; Childhood Chronic Myelogenous Leukemia; Childhood Myelodysplastic Syndromes; Childhood Nasal Type Extranodal NK/T-cell Lymphoma; Cutaneous B-cell Non-Hodgkin Lymphoma; de Novo Myelodysplastic Syndromes; Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue; Hematopoietic/Lymphoid Cancer; Hepatosplenic T-cell Lymphoma; Intraocular Lymphoma; Nodal Marginal Zone B-cell Lymphoma; Peripheral T-cell Lymphoma; Post-transplant Lymphoproliferative Disorder; Previously Treated Myelodysplastic Syndromes; Recurrent Adult Burkitt Lymphoma; Recurrent Adult Diffuse Large Cell Lymphoma; Recurrent Adult Diffuse Mixed Cell Lymphoma; Recurrent Adult Diffuse Small Cleaved Cell Lymphoma; Recurrent Adult Grade III Lymphomatoid Granulomatosis; Recurrent Adult Hodgkin Lymphoma; Recurrent Adult Immunoblastic Large Cell Lymphoma; Recurrent Adult Lymphoblastic Lymphoma; Recurrent Adult T-cell Leukemia/Lymphoma; Recurrent Childhood Anaplastic Large Cell Lymphoma; Recurrent Childhood Grade III Lymphomatoid Granulomatosis; Recurrent Childhood Large Cell Lymphoma; Recurrent Childhood Lymphoblastic Lymphoma; Recurrent Childhood Small Noncleaved Cell Lymphoma; Recurrent Cutaneous T-cell Non-Hodgkin Lymphoma; Recurrent Grade 1 Follicular Lymphoma; Recurrent Grade 2 Follicular Lymphoma; Recurrent Grade 3 Follicular Lymphoma; Recurrent Mantle Cell Lymphoma; Recurrent Marginal Zone Lymphoma; Recurrent Mycosis Fungoides/Sezary Syndrome; Recurrent Small Lymphocytic Lymphoma; Recurrent/Refractory Childhood Hodgkin Lymphoma; Refractory Chronic Lymphocytic Leukemia; Refractory Multiple Myeloma; Relapsing Chronic Myelogenous Leukemia; Secondary Myelodysplastic Syndromes; Small Intestine Lymphoma; Splenic Marginal Zone Lymphoma; Stage II Multiple Myeloma; Stage III Adult Burkitt Lymphoma; Stage III Adult Diffuse Large Cell Lymphoma; Stage III Adult Diffuse Mixed Cell Lymphoma; Stage III Adult Diffuse Small Cleaved Cell Lymphoma; Stage III Adult Hodgkin Lymphoma; Stage III Adult Immunoblastic Large Cell Lymphoma; Stage III Adult Lymphoblastic Lymphoma; Stage III Adult T-cell Leukemia/Lymphoma; Stage III Childhood Hodgkin Lymphoma; Stage III Chronic Lymphocytic Leukemia; Stage III Cutaneous T-cell Non-Hodgkin Lymphoma; Stage III Grade 1 Follicular Lymphoma; Stage III Grade 2 Follicular Lymphoma; Stage III Grade 3 Follicular Lymphoma; Stage III Mantle Cell Lymphoma; Stage III Marginal Zone Lymphoma; Stage III Multiple Myeloma; Stage III Mycosis Fungoides/Sezary Syndrome; Stage III Small Lymphocytic Lymphoma; Stage IV Adult Burkitt Lymphoma; Stage IV Adult Diffuse Large Cell Lymphoma; Stage IV Adult Diffuse Mixed Cell Lymphoma; Stage IV Adult Diffuse Small Cleaved Cell Lymphoma; Stage IV Adult Hodgkin Lymphoma; Stage IV Adult Immunoblastic Large Cell Lymphoma; Stage IV Adult Lymphoblastic Lymphoma; Stage IV Adult T-cell Leukemia/Lymphoma; Stage IV Childhood Hodgkin Lymphoma; Stage IV Chronic Lymphocytic Leukemia; Stage IV Cutaneous T-cell Non-Hodgkin Lymphoma; Stage IV Grade 1 Follicular Lymphoma; Stage IV Grade 2 Follicular Lymphoma; Stage IV Grade 3 Follicular Lymphoma; Stage IV Mantle Cell Lymphoma; Stage IV Marginal Zone Lymphoma; Stage IV Mycosis Fungoides/Sezary Syndrome; Stage IV Small Lymphocytic Lymphoma; Testicular Lymphoma; Waldenström Macroglobulinemia
Fred Hutchinson Cancer Center
2002-01 PHASE2
NCT00758602 COMPLETED
Kidney Transplantation
Hoffmann-La Roche
2008-09 PHASE4
NCT00316810 COMPLETED
Pancreas-Kidney Transplantation
Dr. Claudia Bösmüller
2006-04 PHASE3
NCT00543569 COMPLETED
Kidney Transplantation
Astellas Pharma Inc
2008-02 PHASE2
NCT00360685 COMPLETED
Mucositis; Graft-versus-host Disease
H. Lee Moffitt Cancer Center and Research Institute
2005-09
NCT00169910 COMPLETED
Cardiovascular Disease
Leiden University Medical Center
2005-12 PHASE4
NCT00311311 TERMINATED
Atherosclerosis; Kidney Failure
Pfizer
2006-04 PHASE3
NCT00354419 TERMINATED
Aplastic Anemia
Fred Hutchinson Cancer Center
2006-02 PHASE1
NCT00334672 UNKNOWN
Nonneoplastic Condition
Children's Cancer and Leukaemia Group
2006-03 PHASE3
NCT00506948 TERMINATED
Hematological Malignancies; Myelodysplastic Syndrome; Leukemia; Lymphoma
M.D. Anderson Cancer Center
2006-09 PHASE2
NCT00991510 TERMINATED
Stable Renal Transplant Recipients
Teva Branded Pharmaceutical Products R&D, Inc.
2009-08 PHASE4
NCT00060424 COMPLETED
B-Cell Prolymphocytic Leukemia; Chronic Lymphocytic Leukemia; Prolymphocytic Leukemia; Recurrent Chronic Lymphocytic Leukemia; Recurrent Small Lymphocytic Lymphoma; Refractory Chronic Lymphocytic Leukemia; T-Cell Prolymphocytic Leukemia
Fred Hutchinson Cancer Center
2003-03 PHASE2
NCT00430677 TERMINATED
Systemic Lupus Erythematosus
Bristol-Myers Squibb
2007-06 PHASE2; PHASE3
NCT00891306 COMPLETED
Familial Lipoprotein Lipase Deficiency
Amsterdam Molecular Therapeutics
2009-02 PHASE2; PHASE3
NCT01220297 TERMINATED
Hematologic Diseases; Acute-graft-versus-host Disease; Leukemia; Non-Hodgkin Lymphoma (NHL); Hodgkin Lymphoma
Stanford University
2006-08 PHASE2
NCT00771745 COMPLETED
Renal Transplant Rejection; Transplants and Implants
University of Cincinnati
2008-09 PHASE4
NCT01033864 COMPLETED
Kidney Transplantation
Hoffmann-La Roche
2009-11 PHASE4
NCT00275509 COMPLETED
Kidney Failure, Chronic
Johns Hopkins University
2007-01 PHASE3
NCT00695344 UNKNOWN
Cardiac Transplant
Fundacion Investigacion y Desarrollo
2006-01 PHASE4
NCT00555321 TERMINATED
Immunosuppression in Solid Organ Transplant
Bristol-Myers Squibb
2008-01 PHASE2
NCT00733733 UNKNOWN
Renal Transplant Patients; Recipients of a Kidney From a Non-Heart-Beating Donor
Radboud University Medical Center
2008-01 PHASE3
NCT00740467 UNKNOWN
Graft Versus Host Disease; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Precancerous Condition
Institut Paoli-Calmettes
2008-01 PHASE2
NCT00040846 COMPLETED
Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities; Adult Acute Myeloid Leukemia With Del(5q); Adult Acute Myeloid Leukemia With Inv(16)(p13;q22); Adult Acute Myeloid Leukemia With t(15;17)(q22;q12); Adult Acute Myeloid Leukemia With t(16;16)(p13;q22); Adult Acute Myeloid Leukemia With t(8;21)(q22;q22); Adult Nasal Type Extranodal NK/T-cell Lymphoma; Anaplastic Large Cell Lymphoma; Angioimmunoblastic T-cell Lymphoma; Childhood Burkitt Lymphoma; Childhood Chronic Myelogenous Leukemia; Childhood Diffuse Large Cell Lymphoma; Childhood Immunoblastic Large Cell Lymphoma; Childhood Nasal Type Extranodal NK/T-cell Lymphoma; Chronic Phase Chronic Myelogenous Leukemia; Contiguous Stage II Adult Diffuse Small Cleaved Cell Lymphoma; Contiguous Stage II Grade 1 Follicular Lymphoma; Contiguous Stage II Grade 2 Follicular Lymphoma; Contiguous Stage II Marginal Zone Lymphoma; Contiguous Stage II Small Lymphocytic Lymphoma; Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue; Hepatosplenic T-cell Lymphoma; Myelodysplastic/Myeloproliferative Neoplasm, Unclassifiable; Nodal Marginal Zone B-cell Lymphoma; Noncontiguous Stage II Adult Diffuse Small Cleaved Cell Lymphoma; Noncontiguous Stage II Grade 1 Follicular Lymphoma; Noncontiguous Stage II Grade 2 Follicular Lymphoma; Noncontiguous Stage II Marginal Zone Lymphoma; Noncontiguous Stage II Small Lymphocytic Lymphoma; Peripheral T-cell Lymphoma; Previously Treated Myelodysplastic Syndromes; Progressive Hairy Cell Leukemia, Initial Treatment; Recurrent Adult Acute Myeloid Leukemia; Recurrent Adult Burkitt Lymphoma; Recurrent Adult Diffuse Large Cell Lymphoma; Recurrent Adult Diffuse Mixed Cell Lymphoma; Recurrent Adult Diffuse Small Cleaved Cell Lymphoma; Recurrent Adult Grade III Lymphomatoid Granulomatosis; Recurrent Adult Hodgkin Lymphoma; Recurrent Adult Immunoblastic Large Cell Lymphoma; Recurrent Adult Lymphoblastic Lymphoma; Recurrent Adult T-cell Leukemia/Lymphoma; Recurrent Childhood Acute Lymphoblastic Leukemia; Recurrent Childhood Acute Myeloid Leukemia; Recurrent Childhood Anaplastic Large Cell Lymphoma; Recurrent Childhood Large Cell Lymphoma; Recurrent Childhood Lymphoblastic Lymphoma; Recurrent Childhood Small Noncleaved Cell Lymphoma; Recurrent Cutaneous T-cell Non-Hodgkin Lymphoma; Recurrent Grade 1 Follicular Lymphoma; Recurrent Grade 2 Follicular Lymphoma; Recurrent Grade 3 Follicular Lymphoma; Recurrent Mantle Cell Lymphoma; Recurrent Marginal Zone Lymphoma; Recurrent Mycosis Fungoides/Sezary Syndrome; Recurrent Small Lymphocytic Lymphoma; Recurrent/Refractory Childhood Hodgkin Lymphoma; Refractory Chronic Lymphocytic Leukemia; Refractory Hairy Cell Leukemia; Refractory Multiple Myeloma; Relapsing Chronic Myelogenous Leukemia; Splenic Marginal Zone Lymphoma; Stage I Adult Diffuse Small Cleaved Cell Lymphoma; Stage I Childhood Anaplastic Large Cell Lymphoma; Stage I Childhood Large Cell Lymphoma; Stage I Cutaneous T-cell Non-Hodgkin Lymphoma; Stage I Grade 1 Follicular Lymphoma; Stage I Grade 2 Follicular Lymphoma; Stage I Mantle Cell Lymphoma; Stage I Marginal Zone Lymphoma; Stage I Mycosis Fungoides/Sezary Syndrome; Stage I Small Lymphocytic Lymphoma; Stage II Childhood Anaplastic Large Cell Lymphoma; Stage II Childhood Large Cell Lymphoma; Stage II Cutaneous T-cell Non-Hodgkin Lymphoma; Stage II Mycosis Fungoides/Sezary Syndrome; Stage III Adult Diffuse Large Cell Lymphoma; Stage III Adult Diffuse Small Cleaved Cell Lymphoma; Stage III Childhood Anaplastic Large Cell Lymphoma; Stage III Childhood Large Cell Lymphoma; Stage III Cutaneous T-cell Non-Hodgkin Lymphoma; Stage III Grade 1 Follicular Lymphoma; Stage III Grade 2 Follicular Lymphoma; Stage III Mantle Cell Lymphoma; Stage III Marginal Zone Lymphoma; Stage III Mycosis Fungoides/Sezary Syndrome; Stage III Small Lymphocytic Lymphoma; Stage IV Adult Diffuse Large Cell Lymphoma; Stage IV Adult Diffuse Small Cleaved Cell Lymphoma; Stage IV Childhood Anaplastic Large Cell Lymphoma; Stage IV Childhood Large Cell Lymphoma; Stage IV Cutaneous T-cell Non-Hodgkin Lymphoma; Stage IV Grade 1 Follicular Lymphoma; Stage IV Grade 2 Follicular Lymphoma; Stage IV Mantle Cell Lymphoma; Stage IV Marginal Zone Lymphoma; Stage IV Mycosis Fungoides/Sezary Syndrome; Stage IV Small Lymphocytic Lymphoma; T-cell Large Granular Lymphocyte Leukemia; Waldenström Macroglobulinemia
Fred Hutchinson Cancer Center
2001-11 PHASE2
NCT00547196 COMPLETED
Leukemia; Lymphoma; Myelodysplastic Syndromes
City of Hope Medical Center
2005-08-16
NCT00121810 COMPLETED
Kidney Transplantation
Hoffmann-La Roche
2003-08 PHASE4
NCT00240994 COMPLETED
Kidney Failure, Chronic; Kidney Transplantation; Immunosuppression
National Institute of Allergy and Infectious Diseases (NIAID)
2005-01 PHASE2
NCT00183248 COMPLETED
Kidney Transplantation; Kidney Disease; Kidney Failure
University of Miami
2004-09 PHASE1; PHASE2
NCT00790439 WITHDRAWN
Diabetes Mellitus, Type I
National Institute of Allergy and Infectious Diseases (NIAID)
2008-07 PHASE2
NCT01550445 UNKNOWN
Disorder Related to Renal Transplantation
Ajou University School of Medicine
2008-05 PHASE4
NCT00054353 COMPLETED
Refractory Multiple Myeloma
Fred Hutchinson Cancer Center
2002-10 PHASE1; PHASE2
NCT00223678 COMPLETED
Kidney Transplant
Vanderbilt University Medical Center
2000-06 PHASE4
NCT00617604 COMPLETED
De Novo Kidney Transplantation
Astellas Pharma Inc
2007-12 PHASE2
NCT01016626 COMPLETED
Healthy
Chong Kun Dang Pharmaceutical
2009-07 PHASE1
NCT00119392 COMPLETED
B-cell Chronic Lymphocytic Leukemia; Nodal Marginal Zone B-cell Lymphoma; Recurrent Adult Burkitt Lymphoma; Recurrent Adult Diffuse Large Cell Lymphoma; Recurrent Adult Diffuse Mixed Cell Lymphoma; Recurrent Adult Diffuse Small Cleaved Cell Lymphoma; Recurrent Adult Grade III Lymphomatoid Granulomatosis; Recurrent Adult Immunoblastic Large Cell Lymphoma; Recurrent Adult Lymphoblastic Lymphoma; Recurrent Grade 1 Follicular Lymphoma; Recurrent Grade 2 Follicular Lymphoma; Recurrent Grade 3 Follicular Lymphoma; Recurrent Mantle Cell Lymphoma; Recurrent Marginal Zone Lymphoma; Recurrent Small Lymphocytic Lymphoma; Splenic Marginal Zone Lymphoma; Waldenström Macroglobulinemia
Fred Hutchinson Cancer Center
2004-06 PHASE2
NCT00795132 COMPLETED
Acute Leukaemia; Chronic Disease; Leukemia; Myelodysplasia; Lymphoma
University of Utah
2004-04 PHASE2
NCT00301951 COMPLETED
Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes
University of California, San Francisco
2004-09 PHASE1
NCT00206076 COMPLETED
Liver Disease
Albert Einstein Healthcare Network
2006-08 PHASE4
NCT01364987 COMPLETED
Healthy Subjects; Drug Interactions; Pharmacokinetics of ASP015K
Astellas Pharma Inc
2009-05 PHASE1
NCT00551291 COMPLETED
Myelodysplastic Syndromes
Hoffmann-La Roche
2007-08 PHASE2
NCT00324506 COMPLETED
Multiple Sclerosis
University of Texas Southwestern Medical Center
2006-05 PHASE2
NCT00185614 COMPLETED
Blood Cancer; Multiple Myeloma
Wen-Kai Weng
2000-08 PHASE2
NCT02005562 COMPLETED
Kidney Transplantation
Hoffmann-La Roche
2006-05 PHASE3
NCT00596947 TERMINATED
Transplants and Implants
University of Pennsylvania
2005-10 PHASE4
NCT00481819 COMPLETED
Kidney Transplantation
Astellas Pharma Inc
2007-07 PHASE3
NCT00113269 COMPLETED
Kidney Transplantation
Astellas Pharma Inc
2005-05 PHASE4
NCT02091414 COMPLETED
Heart Transplantation
Hoffmann-La Roche
2006-08 PHASE3
NCT00224874 COMPLETED
Graft vs Host Disease; Immune System Disorders
National Heart, Lung, and Blood Institute (NHLBI)
2005-09 PHASE2
NCT00420537 TERMINATED
Kidney Dysfunction; Heart Transplantation
University of Bologna
2006-09 PHASE4
NCT01513044 COMPLETED
Healthy
Dr. Reddy's Laboratories Limited
2009-01 PHASE1
NCT00045435 COMPLETED
Acute Myeloid Leukemia With Multilineage Dysplasia Following Myelodysplastic Syndrome; Adult Acute Megakaryoblastic Leukemia (M7); Adult Acute Minimally Differentiated Myeloid Leukemia (M0); Adult Acute Monoblastic Leukemia (M5a); Adult Acute Monocytic Leukemia (M5b); Adult Acute Myeloblastic Leukemia With Maturation (M2); Adult Acute Myeloblastic Leukemia Without Maturation (M1); Adult Acute Myeloid Leukemia in Remission; Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities; Adult Acute Myeloid Leukemia With Del(5q); Adult Acute Myeloid Leukemia With Inv(16)(p13;q22); Adult Acute Myeloid Leukemia With t(16;16)(p13;q22); Adult Acute Myeloid Leukemia With t(8;21)(q22;q22); Adult Acute Myelomonocytic Leukemia (M4); Adult Erythroleukemia (M6a); Adult Pure Erythroid Leukemia (M6b); Secondary Acute Myeloid Leukemia
Fred Hutchinson Cancer Center
2002-04 PHASE2
NCT01513057 COMPLETED
Healthy
Dr. Reddy's Laboratories Limited
2009-01 PHASE1
NCT02081183 TERMINATED
Lupus Nephritis
Hoffmann-La Roche
2006-03 PHASE3
NCT00446459 COMPLETED
Kidney Failure, Chronic; Diabetic Nephropathies; Glomerulonephritis, IGA; Hypertension, Renal
University of Washington
2006-04 PHASE2
NCT00594308 TERMINATED
Acute Myelogenous Leukemia; Acute Lymphocytic Leukemia; Chronic Myelogenous Leukemia; Chronic Lymphocytic Leukemia; Myelodysplasia; Lymphoma, Non-Hodgkin's; Mantle-Cell Lymphoma; Hodgkin's Disease; Multiple Myeloma; Myelofibrosis
Indiana University
2007-10
NCT00400647 COMPLETED
Maintenance Kidney Transplant
Novartis
2006-07 PHASE4
NCT01292226 COMPLETED
Kidney Transplantation
Hoffmann-La Roche
2006-12 PHASE2
NCT00170053 COMPLETED
Kidney Diseases
Mayo Clinic
2005-06 PHASE1
NCT00354172 TERMINATED
Leukemia; Myelodysplastic Syndromes
Masonic Cancer Center, University of Minnesota
2006-02 PHASE2
NCT00157014 COMPLETED
Heart Diseases; Heart Transplantation
Astellas Pharma Inc
2004-05-10 PHASE3
NCT00118742 COMPLETED
Liver Transplantation
Hoffmann-La Roche
2005-08 PHASE4
NCT00405860 COMPLETED
MPO-ANCA Vasculitis; Microscopic Polyangiitis
Mayo Clinic
2002-12 PHASE1
NCT01080417 COMPLETED
Healthy Volunteers
Panacea Biotec Ltd
2008-06
NCT00195273 COMPLETED
Graft vs Host Disease; Kidney Transplantation
Wyeth is now a wholly owned subsidiary of Pfizer
2004-11 PHASE3
NCT00594932 COMPLETED
Systemic Lupus Erythematosus; Arthritis
Oklahoma Medical Research Foundation
2006-11 PHASE1; PHASE2
NCT00089141 TERMINATED
Cancer
Martin, Paul
2004-05 PHASE3
NCT01080443 COMPLETED
Healthy Volunteers
Panacea Biotec Ltd
2008-06
NCT00309218 COMPLETED
Kidney Diseases
Klinik für Kinder- und Jugendmedizin
1999-03 PHASE3
NCT00400400 COMPLETED
Renal Transplantation
Novartis Pharmaceuticals
2006-10 PHASE4
NCT00100178 COMPLETED
Diabetes Mellitus, Type 1
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)
2004-05 PHASE2
NCT00318474 TERMINATED
IgA Nephropathy
St. Joseph's Hospital and Medical Center, Phoenix
2002-01 PHASE3
NCT00608517 TERMINATED
Graft Versus Host Disease; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes
Vanderbilt-Ingram Cancer Center
2005-09
NCT00239005 COMPLETED
Renal Transplant
Novartis Pharmaceuticals
2005-09 PHASE4
NCT00321113 COMPLETED
KIDNEY TRANSPLANTATION
Astellas Pharma Inc
2004-09 PHASE3
NCT00611351 COMPLETED
Graft Versus Host Disease; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Diseases; Secondary Myelofibrosis
University of Nebraska
2005-06-07 PHASE2
NCT00281879 TERMINATED
Chronic Myeloproliferative Disorders; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Neoplasms; Unusual Cancers of Childhood
OHSU Knight Cancer Institute
2006-02 PHASE2
NCT00337493 COMPLETED
Kidney Transplantation
Hoffmann-La Roche
2005-12 PHASE4
NCT00374231 COMPLETED
Liver Transplantation
University of Cincinnati
2002-10 PHASE4
NCT02554955 COMPLETED
Heart Transplantation
Hoffmann-La Roche
2004-02 PHASE4
NCT00275522 COMPLETED
Kidney Transplant
Mayo Clinic
2005-12 PHASE4
NCT00374647 COMPLETED
Primary Renal Allograft
University of Cincinnati
2005-03 PHASE4
NCT01283841 COMPLETED
Fasting
Dr. Reddy's Laboratories Limited
2007-11 PHASE1
NCT01283867 COMPLETED
FED
Dr. Reddy's Laboratories Limited
2007-11 PHASE1
NCT00275535 COMPLETED
Kidney Diseases
Mayo Clinic
2001-04 PHASE4
NCT00997958 COMPLETED
Pancreatic Cancer
Columbia University
2004-06 PHASE1
NCT00087581 COMPLETED
Kidney Transplantation
Hoffmann-La Roche
2004-06 PHASE4
NCT00214266 COMPLETED
Renal Transplantation
University of Wisconsin, Madison
2005-01 PHASE2
NCT00350181 COMPLETED
Leukemia; Lymphoma, Non-Hodgkin; Hematologic Diseases; Acute GVHD
Stanford University
2006-08 PHASE2
NCT00004485 COMPLETED
Sickle Cell Anemia
Fred Hutchinson Cancer Center
1999-12 PHASE1; PHASE2
NCT00295594 COMPLETED
Liver Transplantation
Astellas Pharma Inc
2005-03 PHASE3
NCT00290628 TERMINATED
Chronic Myeloproliferative Disorders; Diamond-blackfan Anemia; Fanconi Anemia; Graft Versus Host Disease; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Diseases
Masonic Cancer Center, University of Minnesota
1999-10
NCT00105235 COMPLETED
Liver Disease; Liver Transplantation
National Institute of Allergy and Infectious Diseases (NIAID)
2005-06 PHASE2
NCT00133172 TERMINATED
Kidney Transplantation
Astellas Pharma Inc
2005-07 PHASE4
NCT00085449 WITHDRAWN
Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Neoplasms
Alliance for Clinical Trials in Oncology
2006-05 PHASE1; PHASE2
NCT00187941 COMPLETED
Transplantation, Renal; Immunosuppression
University of Florida
2005-08 EARLY_PHASE1
NCT00053196 COMPLETED
Leukemia; Lymphoma; Multiple Myeloma; Plasma Cell Neoplasm; Myelodysplastic Syndromes; Myeloproliferative Neoplasms
Alliance for Clinical Trials in Oncology
2002-12 PHASE2
NCT00911274 COMPLETED
Healthy
Teva Pharmaceuticals USA
2006-10 PHASE1
NCT00170859 COMPLETED
Heart Transplantation
Novartis Pharmaceuticals
2004-08 PHASE4
NCT00213590 COMPLETED
Kidney Transplantation; Primary Prevention; Kidney Failure
University Hospital, Rouen
2000-04 PHASE3
NCT00910663 COMPLETED
Healthy
Teva Pharmaceuticals USA
2006-10 PHASE1
NCT00141037 COMPLETED
Kidney Diseases; Kidney Transplantation; Kidney Transplant; Renal Transplantation; Renal Transplant
National Institute of Allergy and Infectious Diseases (NIAID)
2004-03 PHASE1; PHASE2
NCT00149942 COMPLETED
Kidney Transplantation; Liver Transplantation
Novartis
2004-10 PHASE4
NCT00296309 COMPLETED
Kidney Transplantation
Astellas Pharma Inc
2004-10 PHASE3
NCT00106639 COMPLETED
Kidney Transplantation
Pfizer
2005-05 PHASE2
NCT00296361 COMPLETED
Kidney Transplantation
Astellas Pharma Inc
2004-10 PHASE3
NCT00149903 COMPLETED
Renal Transplant
Novartis Pharmaceuticals
2005-01 PHASE3
NCT00239863 COMPLETED
Renal Transplantation
Novartis Pharmaceuticals
2004-05 PHASE3
NCT00239811 COMPLETED
Renal Transplantation
Novartis Pharmaceuticals
2004-04 PHASE3
NCT00228020 COMPLETED
Pediatric Kidney Transplantation
Novartis
2001-05 PHASE3
NCT00365287 COMPLETED
Breast Cancer; Kidney Cancer; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes
Masonic Cancer Center, University of Minnesota
2000-06 PHASE1; PHASE2
NCT00089947 COMPLETED
Renal Transplantation; Graft Rejection
Genzyme, a Sanofi Company
2003-06 PHASE2
NCT00893542 COMPLETED
Prophylaxis of Organ Rejection
Roxane Laboratories
2005-11
NCT00656266 TERMINATED
End-stage Liver Disease; Renal Insufficiency; Renal Failure
Baylor College of Medicine
2004-11 PHASE4
NCT00893919 COMPLETED
Prophylaxis of Organ Rejection
Roxane Laboratories
2005-11
NCT00006251 COMPLETED
Acute Undifferentiated Leukemia; Adult Nasal Type Extranodal NK/T-cell Lymphoma; Anaplastic Large Cell Lymphoma; Angioimmunoblastic T-cell Lymphoma; Childhood Burkitt Lymphoma; Childhood Diffuse Large Cell Lymphoma; Childhood Grade III Lymphomatoid Granulomatosis; Childhood Immunoblastic Large Cell Lymphoma; Childhood Myelodysplastic Syndromes; Childhood Nasal Type Extranodal NK/T-cell Lymphoma; Chronic Myelomonocytic Leukemia; Cutaneous B-cell Non-Hodgkin Lymphoma; de Novo Myelodysplastic Syndromes; Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue; Hepatosplenic T-cell Lymphoma; Intraocular Lymphoma; Juvenile Myelomonocytic Leukemia; Mast Cell Leukemia; Myelodysplastic/Myeloproliferative Neoplasm, Unclassifiable; Myeloid/NK-cell Acute Leukemia; Nodal Marginal Zone B-cell Lymphoma; Noncutaneous Extranodal Lymphoma; Peripheral T-cell Lymphoma; Post-transplant Lymphoproliferative Disorder; Previously Treated Myelodysplastic Syndromes; Primary Systemic Amyloidosis; Recurrent Adult Acute Lymphoblastic Leukemia; Recurrent Adult Acute Myeloid Leukemia; Recurrent Adult Burkitt Lymphoma; Recurrent Adult Diffuse Large Cell Lymphoma; Recurrent Adult Diffuse Mixed Cell Lymphoma; Recurrent Adult Diffuse Small Cleaved Cell Lymphoma; Recurrent Adult Grade III Lymphomatoid Granulomatosis; Recurrent Adult Hodgkin Lymphoma; Recurrent Adult Immunoblastic Large Cell Lymphoma; Recurrent Adult Lymphoblastic Lymphoma; Recurrent Adult T-cell Leukemia/Lymphoma; Recurrent Childhood Acute Lymphoblastic Leukemia; Recurrent Childhood Acute Myeloid Leukemia; Recurrent Childhood Anaplastic Large Cell Lymphoma; Recurrent Childhood Grade III Lymphomatoid Granulomatosis; Recurrent Childhood Large Cell Lymphoma; Recurrent Childhood Lymphoblastic Lymphoma; Recurrent Childhood Small Noncleaved Cell Lymphoma; Recurrent Cutaneous T-cell Non-Hodgkin Lymphoma; Recurrent Grade 1 Follicular Lymphoma; Recurrent Grade 2 Follicular Lymphoma; Recurrent Grade 3 Follicular Lymphoma; Recurrent Mantle Cell Lymphoma; Recurrent Marginal Zone Lymphoma; Recurrent Mycosis Fungoides/Sezary Syndrome; Recurrent Renal Cell Cancer; Recurrent Small Lymphocytic Lymphoma; Recurrent/Refractory Childhood Hodgkin Lymphoma; Refractory Chronic Lymphocytic Leukemia; Refractory Hairy Cell Leukemia; Refractory Multiple Myeloma; Small Intestine Lymphoma; Splenic Marginal Zone Lymphoma; Stage II Multiple Myeloma; Stage III Multiple Myeloma; T-cell Large Granular Lymphocyte Leukemia; Testicular Lymphoma; Waldenström Macroglobulinemia
Fred Hutchinson Cancer Center
2000-05 PHASE1; PHASE2
NCT00238901 COMPLETED
Liver Transplant
Novartis
2002-12 PHASE3
NCT00812123 COMPLETED
Kidney Transplantation; Chronic Kidney Disease
University Hospital, Basel, Switzerland
2001-01 PHASE4
NCT00053014 TERMINATED
Leukemia
SWOG Cancer Research Network
2003-04 PHASE2
NCT00005941 COMPLETED
Cervical Cancer; Vaginal Cancer
Fred Hutchinson Cancer Center
1999-11 PHASE2
NCT00301600 COMPLETED
IGA Nephropathy
Nanjing University School of Medicine
2003-01
NCT00238966 COMPLETED
Renal Transplantation
Novartis
2002-11 PHASE4
NCT00064701 COMPLETED
Kidney Transplantation
Astellas Pharma Inc
2003-06 PHASE3
NCT00166244 COMPLETED
De Novo Renal Transplant Recipient.
Erasmus Medical Center
2003-05 PHASE4
NCT00238979 COMPLETED
Renal Transplantation
Novartis Pharmaceuticals
2003-01 PHASE4
NCT02630563 TERMINATED
Pediatric Liver Transplantation
Hoffmann-La Roche
2003-05 PHASE2
NCT00363116 COMPLETED
Acute Allograft Rejection in Simultaneous Kidney/Pancreas Transplant Recipients
University of Cincinnati
1999-04 PHASE4
NCT00285233 COMPLETED
Type 1 Diabetes; Hypoglycemia
University of Minnesota
2000-09 PHASE1; PHASE2
NCT00693381 COMPLETED
Kidney Transplantation
Astellas Pharma Inc
2003-02 PHASE3
NCT00023231 COMPLETED
End-Stage Renal Disease
National Institute of Allergy and Infectious Diseases (NIAID)
2001-02
NCT00005851 COMPLETED
Recurrent Renal Cell Cancer; Stage IV Renal Cell Cancer
Fred Hutchinson Cancer Center
2000-02 PHASE1; PHASE2
NCT00863252 COMPLETED
IGA Nephropathy
The University of Hong Kong
2002-03 PHASE4
NCT00301652 COMPLETED
Vasculitis; Anti-Neutrophil Cytoplasmic Antibody
Nanjing University School of Medicine
2003-06
NCT00001964 COMPLETED
Severe Aplastic Anemia
National Heart, Lung, and Blood Institute (NHLBI)
2000-03-17 PHASE2
NCT00041288 TERMINATED
Leukemia; Lymphoma
University of Texas Southwestern Medical Center
2001-10 PHASE2
NCT00003954 COMPLETED
Refractory Multiple Myeloma; Stage I Multiple Myeloma; Stage II Multiple Myeloma; Stage III Multiple Myeloma
Fred Hutchinson Cancer Center
1999-03 PHASE1; PHASE2
NCT00048165 COMPLETED
Heart Transplantation
Hoffmann-La Roche
1999-08 PHASE4
NCT00003572 COMPLETED
Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
1998-08 PHASE2
NCT00006350 COMPLETED
Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes
University of Maryland, Baltimore
2000-01 PHASE2
NCT00110058 COMPLETED
Leukemia
Fred Hutchinson Cancer Center
2005-02 PHASE2
NCT00006233 COMPLETED
Melanoma (Skin)
Fred Hutchinson Cancer Center
2000-01 PHASE2
NCT00199667 UNKNOWN
Kidney Transplant Recipients
University Hospital, Limoges
2002-10 PHASE4
NCT00195988 COMPLETED
Liver Transplantation
Children's Memorial Health Institute, Poland
2002-09 PHASE4
NCT00198224 COMPLETED
Renal Failure
Indiana University
2003-01
NCT00285350 COMPLETED
Myasthenia Gravis
FDA Office of Orphan Products Development
2002-09 PHASE3
NCT00295997 UNKNOWN
Chronic Myeloproliferative Disorders; Kidney Cancer; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Neoplasms
University of California, San Francisco
2005-05
NCT00849238 WITHDRAWN
Primary Liver Transplant
University of Wisconsin, Madison
NCT00307645 TERMINATED
ANCA Associated Systemic Vasculitis Including Wegener's; Granulomatosis and Microscopic Polyangiitis and; Renal Limited Vasculitis
Assistance Publique - Hôpitaux de Paris
2003-05 PHASE3
NCT00140543 COMPLETED
Diabetes Mellitus, Type 1; Diabetic Nephropathy
EUROSPK Study Group
2002-02 PHASE3
NCT00261820 COMPLETED
Graft Rejection; Kidney Failure; Kidney Transplantation
Wyeth is now a wholly owned subsidiary of Pfizer
PHASE4
NCT00223015 COMPLETED
Renal Transplantation
University Hospital Schleswig-Holstein
2004-05 PHASE4
NCT00304720 UNKNOWN
Multiple Myeloma; Lymphoma; Acute Myelogenous Leukemia; Acute Lymphocytic Leukemia; Myelodysplastic Syndrome
Colorado Blood Cancer Institute
2004-03 PHASE2
NCT00411515 COMPLETED
Corneal Transplantation
University Hospital Freiburg
PHASE4
NCT00309270 COMPLETED
Kidney Transplant
Mario Negri Institute for Pharmacological Research
2003-02 PHASE2
NCT00404794 COMPLETED
Lupus Nephritis; Glomerulonephritis, Membranous
Hospital Authority, Hong Kong
2005-11 PHASE3
NCT00005935 COMPLETED
Aplastic Anemia
National Heart, Lung, and Blood Institute (NHLBI)
2000-06 PHASE2
NCT00004567 COMPLETED
Vasculitis; Wegener's Granulomatosis
National Institute of Allergy and Infectious Diseases (NIAID)
2000-02 PHASE2
NCT00420472 TERMINATED
Kidney Transplantation
Hoffmann-La Roche
2007-03 PHASE4
NCT00295425 UNKNOWN
Psoriasis
University Hospital Muenster
2000-05 PHASE2
NCT00193635 COMPLETED
Congenital Urological Abnormalities
Northwell Health
2002-03 PHASE1
NCT00027547 COMPLETED
Leukemia
Fred Hutchinson Cancer Center
2001-07 PHASE1; PHASE2
NCT00166829 UNKNOWN
Kidney Transplantation
National Taiwan University Hospital
2004-05 PHASE4
NCT00188955 COMPLETED
Kidney Transplantation
University of Manitoba
2004-03 PHASE4
NCT00247494 UNKNOWN
HIV Infection; Atherosclerosis
Academisch Medisch Centrum - Universiteit van Amsterdam (AMC-UvA)
2005-04 PHASE4
NCT00007059 COMPLETED
Graft Versus Host Disease
National Center for Research Resources (NCRR)
1998-06
NCT00431119 COMPLETED
Bullous Pemphigoid
University Hospital Muenster
1997-10 PHASE2
NCT00001764 COMPLETED
Vasculitis; Wegener's Granulomatosis
National Institute of Allergy and Infectious Diseases (NIAID)
1998-04 PHASE1
NCT00008307 UNKNOWN
Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes
Herbert Irving Comprehensive Cancer Center
1998-04 PHASE2
NCT00135967 COMPLETED
Glomerulonephritis, Membranous
Radboud University Medical Center
2002-05 PHASE2; PHASE3
NCT00204230 TERMINATED
Immunosuppressive Agents; Kidney Failure, Chronic; Kidney Transplantation
University Hospital Muenster
1999-10
NCT00729768 WITHDRAWN
Kidney Transplantation
Genentech, Inc.
PHASE2; PHASE3
NCT00021489 WITHDRAWN
HIV Infections
National Institute of Allergy and Infectious Diseases (NIAID)
PHASE2

(data from https://clinicaltrials.gov, updated on 2026-06-03)

Check the Mycophenolate mofetil product page for in-depth specifications, including solubility, stock solutions, MOA, and working concentrations.

Compliance for Clinical Use

Mechanism and Biochemical Profile

Mycophenolate mofetil is a non-competitive, selective, and reversible inhibitor of inosine monophosphate dehydrogenase I and II with IC50 values of 39 nM and 27 nM, respectively, which blocks de novo guanine nucleotide synthesis to induce cell cycle arrest and caspase-dependent apoptosis. By selectively suppressing lymphocytic proliferation while sparing non-lymphoid cells that rely on purine scavenger pathways, this target inhibition blunts autoreactive and alloimmune responses, directly underpinning its clinical evaluation in renal transplantation, systemic lupus erythematosus, and autoimmune hepatitis.

Appendix RUO and cGMP Quality Standards

Quality Dimension RUO (Research Use Only) cGMP (Current Good Manufacturing Practice)
Clinical Applicability Prohibited in human clinical trials or medical diagnostics. Mandatory for human clinical trials (Phase I–III) and therapies.
Regulatory Status Non-regulated grade; exempt from drug manufacturing laws. Legally enforced by health authorities (e.g., FDA, EMA, NMPA).
Facility Environment Unclassified analytical or research laboratories. Validated Cleanrooms (ISO Class 5–8) with continuous monitoring.
Quality Control Basic purity and activity testing. Rigorous safety release testing (Sterility, Endotoxin, Mycoplasma).
Process Validation Basic equipment calibration; no process validation required. Full qualification (IQ/OQ/PQ) and complete batch records.
Quality Assurance Vendor self-declared without required formal QMS. Mandatory QA/QC unit, Change Control, CAPA, and vendor audits.
Regulatory Impact High risk of IND rejection if used as a critical raw material. Required for IND/NDA filings, supported by Drug Master Files (DMF).

Footnotes

Regulatory Note: Governed by FDA (21 CFR Parts 210/211/312), EMA (EudraLex Vol 4), ICH Guidelines (E6/Q7/Q9/Q10), and compendial standards (USP <71>/<85>/<1043>).

Note: Technical data last updated: Sep 1, 2026.