Clinical Trials

Niclosamide has been evaluated across multiple clinical trials spanning Phase 1 through Phase 4 for various indications, including COVID-19, acute myeloid leukemia, advanced prostate carcinoma, ulcerative colitis, and intestinal parasitism. Spearheaded by both academic institutions and pharmaceutical entities, these protocols reflect a range of recruitment statuses, including active recruitment, completed safety evaluations, and terminated or withdrawn studies.

NCT Number Recruitment Conditions Sponsor/Collaborators Start Date Phases
NCT05188170 RECRUITING
Acute Myeloid Leukemia (AML)
Stanford University
2022-11-21 PHASE1
NCT02807805 ACTIVE_NOT_RECRUITING
Metastatic Prostate Carcinoma; Recurrent Prostate Carcinoma; Stage IV Prostate Cancer
Mamta Parikh
2016-10 PHASE2
NCT04870333 COMPLETED
Covid19
Cambridge University Hospitals NHS Foundation Trust
2021-02-19 PHASE2; PHASE3
NCT04372082 WITHDRAWN
Sars-CoV2
University Hospital, Lille
2020-05 PHASE3
NCT04296851 UNKNOWN
Familial Adenomatous Polyposis
Yonsei University
2020-02-14 PHASE2
NCT05188170 Recruiting
Acute Myeloid Leukemia (AML)
Stanford University
2022-11-21 Phase 1
NCT03521232 TERMINATED
Ulcerative Colitis; Ulcerative Proctitis; Ulcerative Proctosigmoiditis
Entero Therapeutics
2018-05-15 PHASE1; PHASE2
NCT05087381 COMPLETED
Treatment Efficacy
Chulalongkorn University
2021-10-01 PHASE4
NCT04858425 TERMINATED
Covid19
Entero Therapeutics
2021-04-30 PHASE2
NCT04317430 COMPLETED
Diabetic Nephropathies
Tanta University
2020-02-01 PHASE3
NCT04603924 COMPLETED
COVID-19
NeuroBo Pharmaceuticals Inc.
2020-10-07 PHASE2; PHASE3
NCT05168644 COMPLETED
Healthy
TFF Pharmaceuticals, Inc.
2021-11-14 PHASE1
NCT04436458 WITHDRAWN
COVID
Entero Therapeutics
2022-01-20 PHASE2
NCT04542434 WITHDRAWN
Covid19
Entero Therapeutics
2022-01-20 PHASE2
NCT03123978 COMPLETED
Metastatic Prostate Carcinoma; Recurrent Prostate Carcinoma; Stage IV Prostate Cancer
University of California, Davis
2017-01-09 PHASE1
NCT04932915 TERMINATED
Covid19
UNION therapeutics
2021-09-03 PHASE2
NCT04436458 Withdrawn
COVID
First Wave BioPharma Inc.
2022-01-20 Phase 2
NCT04753619 UNKNOWN
Covid-19; SARS Pneumonia
University of Baghdad
2021-01-03 PHASE2
NCT05168644 Completed
Healthy
TFF Pharmaceuticals Inc.
2021-11-14 Phase 1
NCT04750759 TERMINATED
Covid19
Charité Research Organisation GmbH
2021-02-03 PHASE2
NCT04705415 COMPLETED
Healthy
NeuroBo Pharmaceuticals Inc.
2020-11-17 PHASE1
NCT04749173 COMPLETED
Covid19
Daewoong Pharmaceutical Co. LTD.
2020-11-21 PHASE1
NCT04644705 COMPLETED
Healthy Volunteers
Charité Research Organisation GmbH
2020-11-02 PHASE1
NCT04399356 COMPLETED
COVID-19
Tufts Medical Center
2020-10-01 PHASE2
NCT04541485 TERMINATED
COVID-19 Patients
Daewoong Pharmaceutical Co. LTD.
2020-12-04 PHASE1
NCT04558021 UNKNOWN
Covid19
Imuneks Farma ilac San. Tic. A.S.
2020-10-08 PHASE3
NCT04592835 UNKNOWN
COVID-19 Patients
Daewoong Pharmaceutical Co. LTD.
2020-10-19 PHASE1
NCT04524052 UNKNOWN
Healthy
Daewoong Pharmaceutical Co. LTD.
2020-08 PHASE1
NCT04644705 Completed
Healthy Volunteers
Charité Research Organisation GmbH|Bayer
2020-11-02 Phase 1
NCT04592835 Unknown status
COVID-19 Patients
Daewoong Pharmaceutical Co. LTD.|Novotech (Australia) Pty Limited
2020-10-19 Phase 1
NCT04524052 Unknown status
Healthy
Daewoong Pharmaceutical Co. LTD.
2020-08 Phase 1
NCT02519582 UNKNOWN
Colorectal Cancer
Charite University, Berlin, Germany
2015-08 PHASE2
NCT03160001 COMPLETED
Rheumatoid Arthritis (RA)
Faiq Gorial
2017-08-15 PHASE1; PHASE2
NCT02687009 TERMINATED
Colon Cancer
Michael Morse, MD
2017-11-07 PHASE1
NCT02532114 COMPLETED
Castration Levels of Testosterone; Castration-Resistant Prostate Carcinoma; Metastatic Prostate Carcinoma; Recurrent Prostate Carcinoma; Stage IV Prostate Adenocarcinoma
University of Washington
2015-12-31 PHASE1
NCT01296958 COMPLETED
Taenia Solium Taeniasis
Oregon Health and Science University
2011-05
NCT00138359 TERMINATED
Intestinal Parasitism
National Institute of Allergy and Infectious Diseases (NIAID)
2004-12

(data from https://clinicaltrials.gov, updated on 2026-08-12)

Check the Niclosamide product page for in-depth specifications, including solubility, stock solutions, MOA, and working concentrations.

Compliance for Clinical Use

Mechanism and Biochemical Profile

Niclosamide directly targets and selectively inhibits the phosphorylation of signal transducer and activator of transcription 3 (STAT3) with a half-maximal inhibitory concentration of 0.7 μM, thereby blocking downstream STAT3-mediated signaling pathways and suppressing cellular DNA replication. By suppressing STAT3 activation and inhibiting DNA synthesis in proliferating target cells, niclosamide demonstrates therapeutic potential in clinical trial evaluations for hyperproliferative malignancies such as acute myeloid leukemia and prostate cancer.

Appendix RUO and cGMP Quality Standards

Quality Dimension RUO (Research Use Only) cGMP (Current Good Manufacturing Practice)
Clinical Applicability Prohibited in human clinical trials or medical diagnostics. Mandatory for human clinical trials (Phase I–III) and therapies.
Regulatory Status Non-regulated grade; exempt from drug manufacturing laws. Legally enforced by health authorities (e.g., FDA, EMA, NMPA).
Facility Environment Unclassified analytical or research laboratories. Validated Cleanrooms (ISO Class 5–8) with continuous monitoring.
Quality Control Basic purity and activity testing. Rigorous safety release testing (Sterility, Endotoxin, Mycoplasma).
Process Validation Basic equipment calibration; no process validation required. Full qualification (IQ/OQ/PQ) and complete batch records.
Quality Assurance Vendor self-declared without required formal QMS. Mandatory QA/QC unit, Change Control, CAPA, and vendor audits.
Regulatory Impact High risk of IND rejection if used as a critical raw material. Required for IND/NDA filings, supported by Drug Master Files (DMF).

Footnotes

Regulatory Note: Governed by FDA (21 CFR Parts 210/211/312), EMA (EudraLex Vol 4), ICH Guidelines (E6/Q7/Q9/Q10), and compendial standards (USP <71>/<85>/<1043>).

Note: Technical data last updated: Sep 1, 2026.