Clinical Trials

Across numerous clinical trials spanning Early Phase 1 through Phase 4, busulfan has been extensively evaluated in conditioning regimens for hematopoietic stem cell transplantation. These studies target conditions such as acute myeloid leukemia, myelodysplastic syndrome, severe immunodeficiencies, and neuroblastoma, with recruitment statuses ranging from recruiting and completed to active not recruiting and terminated. Spearheaded by diverse sponsors—including the Fred Hutchinson Cancer Center, the National Institute of Allergy and Infectious Diseases, and Great Ormond Street Hospital for Children—this research encompasses targeted pharmacokinetic and gene therapy protocols.

NCT Number Recruitment Conditions Sponsor/Collaborators Start Date Phases
NCT03538899 RECRUITING
Severe Combined Immunodeficiency
University of California, San Francisco
2018-05-31 PHASE1; PHASE2
NCT06851767 ENROLLING_BY_INVITATION
X-linked Severe Combined Immunodeficiency; X-SCID; XSCID
National Institute of Allergy and Infectious Diseases (NIAID)
2025-05-09 PHASE1; PHASE2
NCT07524530 NOT_YET_RECRUITING
Core Binding Factor Alpha Subunits; Hematologic Neoplasms; Leukemia; Lymphoma
National Cancer Institute (NCI)
2026-09-09 PHASE2
NCT05565105 NOT_YET_RECRUITING
Leukemia, Myeloid, Acute; Leukemia, Lymphocytic, Acute
Guenther Koehne
2026-06 PHASE2
NCT05617625 SUSPENDED
Myelodysplastic Syndromes; Graft Vs Host Disease; Graft-versus-host-disease
Guenther Koehne
2026-06 PHASE2
NCT01306019 RECRUITING
X-linked Severe Combined Immunodeficiency (XSCID)
National Institute of Allergy and Infectious Diseases (NIAID)
2012-09-25 PHASE1; PHASE2
NCT06325709 RECRUITING
Chronic Granulomatous Disease (CGD); X-Linked Chronic Granulomatous Disease
National Institute of Allergy and Infectious Diseases (NIAID)
2024-04-17 PHASE1; PHASE2
NCT05463133 RECRUITING
Chronic Granulomatous Disease
National Institute of Allergy and Infectious Diseases (NIAID)
2022-07-08 PHASE1; PHASE2
NCT07759102 NOT_YET_RECRUITING
Recurrent Multiple Myeloma; Refractory Multiple Myeloma
University of California, Davis
2026-09-01 PHASE1
NCT04982354 WITHDRAWN
Acute Myeloid Leukemia
Guenther Koehne
2022-07-05 PHASE1; PHASE2
NCT05027945 RECRUITING
Immunodeficiency; Hematopoietic Stem Cell Transplantation
National Cancer Institute (NCI)
2023-02-23 PHASE2
NCT07228624 RECRUITING
Myelodysplastic/Myeloproliferative Neoplasm; Primary Myelofibrosis; Secondary Myelofibrosis
Fred Hutchinson Cancer Center
2026-02-04 PHASE2
NCT07792369 NOT_YET_RECRUITING
Busulfan Pharmacokinetic Analysis; Busulfan Dosing; Hematopoietic Stem Cell Transplant (HSCT); Busulfan; Glutathione
Children's Hospital of Philadelphia
2026-09 PHASE1
NCT01949129 RECRUITING
Acute Lymphoblastic Leukaemia
St. Anna Kinderkrebsforschung
2013-04 PHASE2; PHASE3
NCT06872333 RECRUITING
Graft Failure; Sickle Cell Disease; Hemoglobinopathies
Masonic Cancer Center, University of Minnesota
2024-11-19 PHASE2
NCT07566377 RECRUITING
Acute Myelogenous Leukemia; Acute Lymphoblastic Leukemia; Myelodysplastic Syndromes; Non-hodgkin Lymphoma; Hodgkin Lymphoma; Leukemia; Lymphoma; Graft-versus-host Disease
Memorial Sloan Kettering Cancer Center
2026-04-28 PHASE2
NCT04282174 WITHDRAWN
Hematologic Diseases; Hematologic Malignancy; Acute Lymphoblastic Leukemia; Acute Myeloid Leukemia; Chronic Myelogenous Leukemia; Chronic Lymphocytic Leukemia
Baptist Health South Florida
2022-09 PHASE2
NCT07074470 RECRUITING
Primary Central Nervous System Lymphoma (PCNSL)
The First Affiliated Hospital of Soochow University
2025-01-02
NCT05477589 RECRUITING
Acute Myeloid Leukemia (AML) in Remission; Stem Cell Transplantation
Vastra Gotaland Region
2022-06-07 PHASE3
NCT07644481 NOT_YET_RECRUITING
AML (Acute Myelogenous Leukemia); Allogeneic Hematopoietic Stem Cell Transplantation Recipient
Institute of Hematology & Blood Diseases Hospital, China
2026-07-20
NCT07276737 NOT_YET_RECRUITING
NK T-Cell Lymphoma
Shanghai General Hospital, Shanghai Jiao Tong University School of Medicine
2025-12-30 PHASE2
NCT06506461 RECRUITING
Sickle Cell Disease
St. Jude Children's Research Hospital
2025-03-21 PHASE1
NCT06673459 NOT_YET_RECRUITING
T-Cell Lymphocytic Leukemia; ALLOGENEIC HEMATOPOIETIC STEM CELL TRANSPLANTATION; Total Body Irradiation; Chemotherapy
The First Affiliated Hospital of Soochow University
2024-12-01 PHASE3
NCT07762508 NOT_YET_RECRUITING
Leukemia, Myeloid, Acute(AML); Hematopoietic Stem Cell Transplantation (HSCT)
The First Affiliated Hospital of Soochow University
2026-08
NCT07563920 NOT_YET_RECRUITING
Acute Myeloid Leukemia
Shanghai General Hospital, Shanghai Jiao Tong University School of Medicine
2026-06
NCT07500753 RECRUITING
Relapsed or Refractory Acute Myeloid Leukemia (AML); MDS (Myelodysplastic Syndrome)
The First Affiliated Hospital of Soochow University
2026-04-01
NCT03779854 ACTIVE_NOT_RECRUITING
Acute Biphenotypic Leukemia; Acute Leukemia; Acute Leukemia of Ambiguous Lineage; Acute Lymphoblastic Leukemia; Acute Undifferentiated Leukemia; Allogeneic Hematopoietic Stem Cell Transplantation Recipient; Blastic Plasmacytoid Dendritic Cell Neoplasm; Blasts Under 25 Percent of Bone Marrow Nucleated Cells; Blasts Under 5 Percent of Bone Marrow Nucleated Cells; Mixed Phenotype Acute Leukemia; Myelodysplastic Syndrome With Excess Blasts-1; Myelodysplastic Syndrome/Acute Myeloid Leukemia; Burkitt Leukemia; Chronic Monocytic Leukemia; Lymphoblastic Lymphoma; Mast Cell Leukemia; Myeloproliferative Neoplasm
Fred Hutchinson Cancer Center
2019-08-29 PHASE2
NCT07737769 NOT_YET_RECRUITING
Acute Myeloid Leukemia; Myelodysplastic Syndrome
University of Michigan Rogel Cancer Center
2026-11 PHASE1
NCT06158828 RECRUITING
AML, Childhood; Aml; Acute Myeloid Leukemia, Pediatric; Acute Myeloid Leukemia
Washington University School of Medicine
2024-11-15 PHASE1; PHASE2
NCT07113743 ENROLLING_BY_INVITATION
Chronic Granulomatous Disease (CGD)
National Institute of Allergy and Infectious Diseases (NIAID)
2025-09-10 PHASE1; PHASE2
NCT02861417 ACTIVE_NOT_RECRUITING
Hematopoietic and Lymphoid Cell Neoplasm; High Risk Acute Myeloid Leukemia; High Risk Myelodysplastic Syndrome; Lymphoproliferative Disorder; Myelodysplastic Syndrome; Myelodysplastic/Myeloproliferative Neoplasm; Recurrent Acute Lymphoblastic Leukemia; Recurrent Acute Myeloid Leukemia; Recurrent Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Recurrent High Risk Myelodysplastic Syndrome; Recurrent Hodgkin Lymphoma; Recurrent Myelodysplastic Syndrome; Recurrent Non-Hodgkin Lymphoma; Recurrent Plasma Cell Myeloma
M.D. Anderson Cancer Center
2016-08-05 PHASE2
NCT05327023 RECRUITING
Hematologic Neoplasms
National Cancer Institute (NCI)
2022-05-23 PHASE1; PHASE2
NCT06477549 RECRUITING
Acute Lymphoblastic Leukemia; Acute Myeloid Leukemia; Biphenotypic Acute Leukemia; Lymphoblastic Lymphoma; Myeloproliferative Neoplasm; Myelodysplastic Syndromes
St. Petersburg State Pavlov Medical University
2024-06-21 PHASE2
NCT06954987 NOT_YET_RECRUITING
Acute Myeloid Leukemia
National Cancer Institute (NCI)
2026-07-17 PHASE2
NCT07085156 NOT_YET_RECRUITING
MDS
Ruijin Hospital
2025-08-01 PHASE2
NCT04708054 RECRUITING
Acute Myeloid Leukemia; Chronic Myelomonocytic Leukemia; Myelodysplastic Syndrome
M.D. Anderson Cancer Center
2021-10-21 PHASE2; PHASE3
NCT07677306 NOT_YET_RECRUITING
Myelodysplastic Syndromes
Peking University People's Hospital
2026-07-15 PHASE2
NCT07052422 NOT_YET_RECRUITING
Older Patients; Myeloid Malignancies; Conditioning; Hematopoietic Stem Cell Transplantation (HSCT)
Nanfang Hospital, Southern Medical University
2025-07-15 PHASE2; PHASE3
NCT01861106 RECRUITING
GATA2; Immunodeficiency; MDS
National Cancer Institute (NCI)
2013-07-24 PHASE2
NCT03970096 RECRUITING
Acute Leukemia; Acute Lymphoblastic Leukemia; Acute Myeloid Leukemia; Myelodysplastic Syndrome; Myeloproliferative Neoplasm
Fred Hutchinson Cancer Center
2019-11-19 PHASE2
NCT02629120 ACTIVE_NOT_RECRUITING
Chronic Granulomatous Disease Transplant
National Institute of Allergy and Infectious Diseases (NIAID)
2015-12-17 PHASE1; PHASE2
NCT07441967 NOT_YET_RECRUITING
Hematologic Malignancies
Institute of Hematology & Blood Diseases Hospital, China
2026-02-20 PHASE2
NCT03619551 ACTIVE_NOT_RECRUITING
SCID
Center for International Blood and Marrow Transplant Research
2018-10-22 PHASE2
NCT05735717 RECRUITING
Hematologic Malignancy; Acute Leukemia; Remission; Acute Myeloid Leukemia; Acute Lymphoblastic Leukemia; AML; TP53; Intrachromosomal Amplification of Chromosome 21; Cytogenetic Abnormality; CNS Leukemia; Minimal Residual Disease; Myelodysplasia; Juvenile Myelomonocytic Leukemia; Somatic Mutation; PTPN11 Gene Mutation; N-RAS Gene Amplification; Neurofibromatosis 1; NF1 Mutation; CBL Gene Mutation; Monosomy 7; Chromosome Abnormality; Fetal Hemoglobin; Lymphoblastic Lymphoma; High Grade Non-Hodgkin's Lymphoma, Adult
Masonic Cancer Center, University of Minnesota
2023-05-11 PHASE2
NCT06879847 RECRUITING
Relapsed or Refractory Acute Myeloid Leukemia
The First Affiliated Hospital of Soochow University
2024-12-01
NCT06959771 RECRUITING
CD40L-HyperIgM Syndrome
National Institute of Allergy and Infectious Diseases (NIAID)
2025-07-16 PHASE1; PHASE2
NCT06252870 RECRUITING
Graft Versus Host Disease; Hematologic Malignancy
Nantes University Hospital
2024-07-18 PHASE2
NCT06613035 NOT_YET_RECRUITING
Acute Myeloid Leukemia
Institute of Hematology & Blood Diseases Hospital, China
2024-09-30 PHASE3
NCT07183878 RECRUITING
Acute Myeloid Leukemia; High-Risk Acute Myeloid Leukemia; Myelodysplastic Syndromes; High-Risk Myelodysplastic Syndromes
First Affiliated Hospital of Zhejiang University
2025-08-20
NCT06079879 ACTIVE_NOT_RECRUITING
Essential Thrombocythemia
Merck Sharp & Dohme LLC
2023-12-31 PHASE3
NCT01961063 ACTIVE_NOT_RECRUITING
AIDS-related Non-Hodgkin Lymphoma; AIDS-related Plasmablastic Lymphoma; AIDS-related Primary Effusion Lymphoma; HIV Infection
City of Hope Medical Center
2015-12-31 PHASE1
NCT03597594 ACTIVE_NOT_RECRUITING
Severe Combined Immunodeficiency
St. Jude Children's Research Hospital
2021-09-02 PHASE1; PHASE2
NCT02727803 RECRUITING
Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Acute Biphenotypic Leukemia; Acute Lymphoblastic Leukemia; Acute Lymphoblastic Leukemia in Remission; Acute Myeloid Leukemia With Myelodysplasia-Related Changes; Acute Myeloid Leukemia With Variant MLL Translocations; B Acute Lymphoblastic Leukemia With t(9;22)(q34.1;q11.2); BCR-ABL1; Chemotherapy-Related Leukemia; Chronic Myelomonocytic Leukemia; Chronic Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive; High Grade B-Cell Lymphoma With MYC and BCL2 or BCL6 Rearrangements; ISS Stage II Plasma Cell Myeloma; ISS Stage III Plasma Cell Myeloma; Myelodysplastic Syndrome; Myelodysplastic Syndrome With Excess Blasts; Myelodysplastic Syndrome With Gene Mutation; Myelodysplastic/Myeloproliferative Neoplasm; Previously Treated Myelodysplastic Syndrome; Recurrent Acute Myeloid Leukemia; Recurrent Adult Acute Myeloid Leukemia; Recurrent Hodgkin Lymphoma; Recurrent Non-Hodgkin Lymphoma; Refractory Acute Lymphoblastic Leukemia; Refractory Adult Acute Lymphoblastic Leukemia; Secondary Acute Myeloid Leukemia; Therapy-Related Myelodysplastic Syndrome
M.D. Anderson Cancer Center
2016-05-19 PHASE2
NCT06996119 RECRUITING
Acute Myeloid Leukemia; Graft Versus Host Disease; Myelodysplastic Syndrome
City of Hope Medical Center
2026-06-12 PHASE1
NCT04859946 ACTIVE_NOT_RECRUITING
Hematologic and Lymphocytic Disorder
M.D. Anderson Cancer Center
2022-01-11 PHASE2
NCT04872595 ACTIVE_NOT_RECRUITING
Acute Myeloid Leukemia (AML); Acute Lymphoid Leukemia (ALL); Myelodysplastic Syndromes (MDS)
Memorial Sloan Kettering Cancer Center
2021-04-30 PHASE2
NCT06548958 RECRUITING
Malignant Hematological Diseases
The First Affiliated Hospital of Soochow University
2024-07-10
NCT06345495 RECRUITING
Splenomegaly; Myelofibrosis
M.D. Anderson Cancer Center
2024-10-01 PHASE2
NCT03579875 RECRUITING
Fanconi Anemia; Severe Aplastic Anemia; Myelodysplastic Syndromes; T Cell Receptor Alpha/Beta Depletion; Telomere Biology Disorder; Bone Marrow Failure; Dyskeratosis Congenita; Telomere Biology Disorders
Masonic Cancer Center, University of Minnesota
2018-11-13 PHASE2
NCT06385808 NOT_YET_RECRUITING
Relapse Leukemia; Refractory Acute Myeloid Leukemia; Conditioning; Hematopoietic Stem Cell Transplantation
First Affiliated Hospital Xi'an Jiaotong University
2024-05-01
NCT07014943 RECRUITING
Primary Central Nervous System Lymphoma (PCNSL)
Sichuan University
2022-01-01 PHASE2
NCT06001385 ACTIVE_NOT_RECRUITING
Acute Lymphoblastic Leukemia; Acute Myeloid Leukemia; Acute Leukemia; Myelodysplastic Syndromes; Chronic Myeloid Leukemia; Chronic Lymphocytic Leukemia; Myeloproliferative Neoplasm; Lymphoma; Chronic Myelomonocytic Leukemia; Pro-Lymphocytic Leukemia; Myelofibrosis
Center for International Blood and Marrow Transplant Research
2023-12-08 PHASE2
NCT04644016 RECRUITING
AML; ALL; MDS; MPD Withou Myelofibrosis; NHL or HL; Inherited Metabolic Disorders; Hemoglobinopathies; Bone Marrow Failure; HLH
Memorial Sloan Kettering Cancer Center
2020-11-20 PHASE2
NCT05436561 RECRUITING
Disease-free Survival
Shanghai Jiao Tong University School of Medicine
2022-06-01 PHASE2
NCT02143830 RECRUITING
Fanconi Anemia; Severe Marrow Failure; Myelodysplastic Syndrome (MDS); Acute Myelogenous Leukemia (AML)
Children's Hospital Medical Center, Cincinnati
2014-04 PHASE2
NCT01176006 ACTIVE_NOT_RECRUITING
DOCK8 Deficiency
National Cancer Institute (NCI)
2010-10-05 PHASE2
NCT06809712 RECRUITING
Hematologic Disease
He Huang
2022-08-04 PHASE1
NCT06809699 RECRUITING
Hematologic Diseases
He Huang
2022-08-04 PHASE1
NCT04098393 ACTIVE_NOT_RECRUITING
Hematologic Malignancies
Memorial Sloan Kettering Cancer Center
2019-09-18 PHASE1
NCT06337331 WITHDRAWN
Acute Myeloid Leukemia; Myelodysplastic Syndromes
Northside Hospital, Inc.
2024-08-31 PHASE2
NCT02500849 ACTIVE_NOT_RECRUITING
HIV
City of Hope Medical Center
2016-03-10 PHASE1
NCT04904588 ACTIVE_NOT_RECRUITING
Acute Lymphoblastic Leukemia; Acute Myelogenous Leukemia; Mixed Phenotype Acute Leukemia; Acute Leukemia; Myelodysplastic Syndromes; Chronic Myelogenous Leukemia; Chronic Lymphocytic Leukemia; Lymphoma
Center for International Blood and Marrow Transplant Research
2021-09-30 PHASE2
NCT01512888 SUSPENDED
Severe Combined Immunodeficiency Disease, X-linked
St. Jude Children's Research Hospital
2016-08-17 PHASE1; PHASE2
NCT03601286 UNKNOWN
Severe Combined Immunodeficiency, X-Linked
Great Ormond Street Hospital for Children NHS Foundation Trust
2018-12-21 PHASE1
NCT01985061 ACTIVE_NOT_RECRUITING
Myelodysplastic Syndrome; Acute Myeloid Leukemia
Institut Paoli-Calmettes
2013-12 PHASE2
NCT06829472 RECRUITING
Toxicities; Survivorship
Shanghai Jiao Tong University School of Medicine
2023-12-01 PHASE3
NCT02061800 UNKNOWN
Chronic Myeloid Leukemia (CML); Acute Myelogenous Leukemia (AML); Myelodysplastic Syndrome (MDS); Juvenile Myelomonocytic Leukemia (JMML); Acute Lymphoblastic Leukemia (ALL); Lymphoma (Hodgkin's and Non-Hodgkin's)
Diane George
2013-06-03 PHASE1; PHASE2
NCT05457556 ACTIVE_NOT_RECRUITING
Acute Lymphoblastic Leukemia; Acute Myeloid Leukemia; Mixed Phenotype Acute Leukemia; Myelodysplastic Syndrome
Children's Oncology Group
2023-03-15 PHASE3
NCT03613532 ACTIVE_NOT_RECRUITING
Acute Myeloid Leukemia (AML); Myelodysplastic Syndrome (MDS); Chronic Myelomonocytic Leukemia (CMML); MDS/Myeloproliferative Neoplasm-unclassifiable (MDS/MPN-unclassifiable); Hematopoietic Stem Cell Transplant
Jacqueline Garcia, MD
2018-10-24 PHASE1
NCT04384692 ACTIVE_NOT_RECRUITING
Primary Myelofibrosis; Secondary Myelofibrosis
Fred Hutchinson Cancer Center
2020-12-18 PHASE2
NCT04547049 ACTIVE_NOT_RECRUITING
Leukemia; MDS
First Affiliated Hospital of Zhejiang University
2020-09-01 PHASE3
NCT03121014 ACTIVE_NOT_RECRUITING
Acute Myeloid Leukemia; Myelodysplastic Syndromes
University of Illinois at Chicago
2017-04-24 PHASE2
NCT05870995 RECRUITING
Refractory Leukemia
Shanghai Jiao Tong University School of Medicine
2023-02-01 PHASE2
NCT05674539 ENROLLING_BY_INVITATION
Acute Myeloid Leukemia, Adult; Myelodysplastic Syndrome(MDS); Allogeneic Hematopoietic Stem Cell Transplantation
Union Hospital, Tongji Medical College, Huazhong University of Science and Technology
2023-02-15 PHASE3
NCT05466318 UNKNOWN
Lymphoma, Large B-Cell, Diffuse; Lymphoma, T-Cell
Sichuan University
2022-07-01 PHASE3
NCT02859402 RECRUITING
T-cell Non-Hodgkin Lymphoma; Lymphoma, Extranodal NK-T-Cell
Keimyung University Dongsan Medical Center
2016-12 PHASE2
NCT04370795 WITHDRAWN
Severe Combined Immune Deficiency (SCID)
National Institute of Allergy and Infectious Diseases (NIAID)
2025-11-26 PHASE1; PHASE2
NCT06399107 RECRUITING
Sickle Cell Disease; Sickle-Cell Disease With Crisis
Essen Biotech
2024-08-01 PHASE1; PHASE2
NCT03259503 COMPLETED
Recurrent Diffuse Large B-Cell Lymphoma; Recurrent T-Cell Non-Hodgkin Lymphoma; Refractory Diffuse Large B-Cell Lymphoma; Refractory Hodgkin Lymphoma; Refractory T-Cell Non-Hodgkin Lymphoma
M.D. Anderson Cancer Center
2019-09-13 PHASE1
NCT05991908 RECRUITING
Acute Myeloid Leukemia; Myelodysplastic Syndromes
Shanghai Jiao Tong University School of Medicine
2023-10-19 PHASE3
NCT05807659 UNKNOWN
Myeloid Malignancies
Sichuan University
2023-03-16 PHASE2
NCT05907486 UNKNOWN
Thrombotic Disorder
The First Affiliated Hospital of Soochow University
2023-08-01 PHASE3
NCT04945096 UNKNOWN
Engraft Failure; Relapse; GVHD
The First Affiliated Hospital of Soochow University
2021-07-01 PHASE3
NCT04822532 UNKNOWN
Hematopoietic Stem Cell Transplantation; Allogeneic Hematopoietic Stem Cell Transplantation; Autologous Hematopoietic Stem Cell Transplantation
University Hospital, Geneva
2021-06-15
NCT06125483 RECRUITING
Hematopoietic Malignancy; Relapse/Recurrence; Hematopoietic Stem Cell Transplantation
The First Affiliated Hospital of Soochow University
2023-11-01
NCT01758328 COMPLETED
Multiple Myeloma
Memorial Sloan Kettering Cancer Center
2012-12 PHASE1
NCT00408447 UNKNOWN
Sickle Cell Disease; Beta Thalassemia
Columbia University
2004-09 PHASE2
NCT06069180 UNKNOWN
Severe Aplastic Anemia
Peking University People's Hospital
2023-11-15 PHASE4
NCT06247917 UNKNOWN
Myelodysplastic Syndrome With Excess Blasts-1; Myelodysplastic Syndrome With Excess Blasts-2; Myelodysplastic Syndromes
Ruijin Hospital
2024-03-03 PHASE2
NCT06625359 TERMINATED
Central Nervous System Lymphoma
Seoul National University Hospital
2015-06-01 PHASE2
NCT05598593 UNKNOWN
Cytarabine+Thiotepa + Fludarabine + Busulfan; T Cell Acute Lymphoblastic Leukemia/Lymphoblastic Lymphoma
First Affiliated Hospital of Zhejiang University
2022-10-23 PHASE2
NCT01701986 COMPLETED
Hematopoietic Cell Transplantation Recipient; Refractory B-Cell Non-Hodgkin Lymphoma; Refractory Hodgkin Lymphoma; Refractory T-Cell Non-Hodgkin Lymphoma
M.D. Anderson Cancer Center
2012-10-25 PHASE1; PHASE2
NCT02506959 COMPLETED
Plasma Cell Leukemia; Plasmacytoma; Recurrent Plasma Cell Myeloma; Refractory Plasma Cell Myeloma
M.D. Anderson Cancer Center
2015-09-14 PHASE2
NCT00357565 COMPLETED
Leukemia; Myelodysplastic Syndromes; Childhood Acute Myeloid Leukemia in Remission; Recurrent Childhood Acute Myeloid Leukemia; Secondary Acute Myeloid Leukemia; Childhood Acute Lymphoblastic Leukemia in Remission; Previously Treated Myelodysplastic Syndrome; Secondary Myelodysplastic Syndrome; Refractory Anemia With Excess Blasts in Transformation; Refractory Anemia With Excess Blasts; Refractory Anemia; De Novo Myelodysplastic Syndrome; Childhood Myelodysplastic Syndrome
Masonic Cancer Center, University of Minnesota
2005-11 PHASE2
NCT05579769 TERMINATED
Hematologic Malignancy; Myeloid Malignancy
St. Jude Children's Research Hospital
2023-03-14 PHASE2
NCT04942730 COMPLETED
Leukemia, Acute Lymphoblastic; Myeloid Leukemia, Acute; Biphenotypic Acute Leukemia; Lymphoblastic Lymphoma; Myelodysplastic Syndromes; Myeloproliferative Neoplasm
St. Petersburg State Pavlov Medical University
2021-01-21 PHASE2
NCT03615105 TERMINATED
Acute Lymphoid Leukemia (ALL); Acute Myeloid Leukemia (AML); Chronic Myeloid Leukemia (CML); Hodgkin Lymphoma; Non-Hodgkin Lymphoma; Chronic Lymphocytic Leukemia
Memorial Sloan Kettering Cancer Center
2018-07-25 PHASE2
NCT05170828 WITHDRAWN
Acute Leukemia; Myelodysplastic Syndromes; T-lymphoblastic Lymphoma; Acute Lymphocytic Leukemia; Acute Myeloid Leukemia; Acute Biphenotypic Leukemia; Acute Undifferentiated Leukemia
Ossium Health, Inc.
2022-09 PHASE1
NCT01505569 COMPLETED
Ewing's Family Tumors; Renal Tumors; Hepatoblastoma; Rhabdomyosarcoma; Soft Tissue Sarcoma; Primary Malignant Brain Neoplasms; Retinoblastoma; Medulloblastoma; Supra-tentorial Primative Neuro-Ectodermal Tumor (PNET); Atypical Teratoid/Rhabdoid Tumor (AT/RT); CNS Tumors; Germ Cell Tumors
Masonic Cancer Center, University of Minnesota
2011-10-20
NCT04904237 UNKNOWN
Refractory Acute Myeloid Leukemia
Shanghai Jiao Tong University School of Medicine
2021-01-01 PHASE2
NCT05449899 UNKNOWN
Secondary Acute Myeloid Leukemia Evolving From MDS; Allogeneic Hematopoietic Stem Cell Transplantation; Conditioning
Nanfang Hospital, Southern Medical University
2022-07 PHASE2; PHASE3
NCT02034630 UNKNOWN
Genetic Rare Disease
Seoul National University Hospital
2014-07-21 PHASE1; PHASE2
NCT05453552 UNKNOWN
Myelodysplastic Syndrome; Allogeneic Hematopoietic Stem Cell Transplantation; Conditioning
Nanfang Hospital, Southern Medical University
2022-07-01 PHASE2; PHASE3
NCT02047578 UNKNOWN
Acute Lymphoblastic Leukemia
Seoul National University Hospital
2014-02-05 PHASE2
NCT04451200 NOT_YET_RECRUITING
Acute Leukemia; Mielodysplasic Syndrome; Myeloproliferative Neoplasm
Institut Paoli-Calmettes
2020-11 PHASE2
NCT03240861 TERMINATED
HLA-A*0201 Positive Cells Present; Locally Advanced Malignant Neoplasm; NY-ESO-1 Positive; Unresectable Malignant Neoplasm; Sarcoma
Jonsson Comprehensive Cancer Center
2017-07-26 PHASE1
NCT02512497 COMPLETED
Cutaneous T-cell Lymphoma; T-Prolymphocytic Leukemia; T-Large Granulocytic Leukemia; T-Lymphoblastic Leukemia/Lymphoma; Peripheral T-Cell Lymphoma
Ohio State University Comprehensive Cancer Center
2017-12-08 PHASE1
NCT05569512 TERMINATED
Acute Myeloid Leukemia; Pediatric Cancer
Malika Kapadia
2022-10-06 PHASE1
NCT05293509 WITHDRAWN
Stem Cell Transplantation
M.D. Anderson Cancer Center
2022-03-02 PHASE2
NCT03602898 WITHDRAWN
Acute Lymphoblastic Leukemia in Remission; Acute Myeloid Leukemia Arising From Previous Myelodysplastic Syndrome; Chronic Myelomonocytic Leukemia; Chronic Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Hematopoietic and Lymphoid System Neoplasm; Myelodysplastic Syndrome; Myelofibrosis; Myeloproliferative Neoplasm; Recurrent Acute Myeloid Leukemia; Recurrent Hodgkin Lymphoma; Recurrent Non-Hodgkin Lymphoma; Refractory Acute Myeloid Leukemia; Therapy-Related Acute Myeloid Leukemia
Fred Hutchinson Cancer Center
2021-06-01 PHASE2
NCT04151706 COMPLETED
Acute Myeloid Leukemia; Acute Lymphoblastic Leukemia; Myelodysplastic Syndromes; Acute Leukemia; Chronic Myeloid Leukemia
Robert Lowsky
2020-02-27 PHASE2
NCT04713956 UNKNOWN
Myelodysplastic Syndrome; Allogeneic Hematopoietic Stem Cell Transplantation; Conditioning
Nanfang Hospital, Southern Medical University
2021-01-15 PHASE2; PHASE3
NCT03852498 COMPLETED
Cerebral Adrenoleukodystrophy (CALD)
Genetix Biotherapeutics Inc.
2019-01-24 PHASE3
NCT02766465 COMPLETED
Sickle Cell Disease
Medical College of Wisconsin
2017-03-16 PHASE2
NCT05425654 UNKNOWN
Primary CNS Lymphoma
National Research Center for Hematology, Russia
2021-05-17 PHASE2
NCT02221310 COMPLETED
Acute Myelogenous Leukemia; Myelodysplastic Syndrome
New York Medical College
2011-12-07 PHASE2
NCT00596154 COMPLETED
CNS Lymphoma; CNS Brain Cancer; Non-Hodgkin's Lymphoma
Memorial Sloan Kettering Cancer Center
2004-12 PHASE2
NCT00588523 COMPLETED
CNS Cancer; CNS BRAIN
Memorial Sloan Kettering Cancer Center
2002-09 PHASE2
NCT00534469 COMPLETED
Leukemia
City of Hope Medical Center
2000-02-08 PHASE2
NCT02251821 COMPLETED
Primary Myelofibrosis; Secondary Myelofibrosis
Fred Hutchinson Cancer Center
2014-10-20 PHASE2
NCT04776850 WITHDRAWN
Beta Thalassemia Major; Sickle Beta 0 Thalassemia; Sickle Beta Plus Thalassemia; Sickle Beta Thalassemia; Sickle Cell Disease; Sickle Cell-SS Disease
M.D. Anderson Cancer Center
2020-12-29 EARLY_PHASE1
NCT03315078 UNKNOWN
X-Linked Combined Immunodeficiency Diseases
National Institute of Allergy and Infectious Diseases (NIAID)
2012-04 PHASE1; PHASE2
NCT02582775 COMPLETED
Epidermolysis Bullosa
Masonic Cancer Center, University of Minnesota
2016-03 PHASE2
NCT03795597 UNKNOWN
Multiple Myeloma
Loyola University
2019-05-22 PHASE1; PHASE2
NCT01349101 COMPLETED
Hematological Malignancies
Sidney Kimmel Comprehensive Cancer Center at Thomas Jefferson University
2011-02-10 PHASE2
NCT03096782 COMPLETED
Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Acute Biphenotypic Leukemia; Acute Leukemia; Acute Lymphoblastic Leukemia; Acute Lymphoblastic Leukemia in Remission; Acute Myeloid Leukemia; Acute Myeloid Leukemia Arising From Previous Myelodysplastic Syndrome; Chemotherapy-Related Leukemia; Chronic Lymphocytic Leukemia; Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Chronic Myelomonocytic Leukemia; Hodgkin Lymphoma; Langerhans Cell Histiocytosis; Minimal Residual Disease; Myelodysplastic Syndrome; Myelodysplastic Syndrome With Excess Blasts; Non-Hodgkin Lymphoma; Recurrent Hodgkin Lymphoma; Refractory Acute Lymphoblastic Leukemia; Refractory Myelodysplastic Syndrome; Small Lymphocytic Lymphoma; Therapy-Related Myelodysplastic Syndrome
M.D. Anderson Cancer Center
2017-10-13 PHASE2
NCT04123392 UNKNOWN
TP53; Myeloid Tumors; Conditioning; Allogeneic Hematopoietic Stem Cell Transplantation
Nanfang Hospital, Southern Medical University
2019-10 PHASE2; PHASE3
NCT04002115 TERMINATED
Acute Myeloid Leukemia
Milton S. Hershey Medical Center
2020-06-03 PHASE2
NCT01572662 COMPLETED
Leukemia; Acute Myeloid Leukemia; Acute Lymphocytic Leukemia; Chronic Myeloid Leukemia; Chronic Lymphocytic Leukemia; Myeloproliferative Diseases; Non-Hodgkins Lymphoma; Hodgkins Lymphoma; Multiple Myeloma; Myelodysplastic Syndrome
M.D. Anderson Cancer Center
2012-04-11 PHASE2
NCT04098653 UNKNOWN
Allogeneic Hematopoietic Stem Cell Transplantation; Conditioning; Myeloid Tumors
Nanfang Hospital, Southern Medical University
2019-09 PHASE2; PHASE3
NCT03384225 UNKNOWN
High Risk Acute Myeloid Leukemia; Allogeneic Hematopoeitic Stem Cell Transplantation
Shanghai General Hospital, Shanghai Jiao Tong University School of Medicine
2016-08-01 PHASE3
NCT00630565 TERMINATED
Leukemia
Masonic Cancer Center, University of Minnesota
2006-07-26 PHASE2; PHASE3
NCT01823198 COMPLETED
Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Acute Erythroid Leukemia; Acute Megakaryoblastic Leukemia; Acute Myeloid Leukemia; Acute Myeloid Leukemia Arising From Previous Myelodysplastic Syndrome; Acute Myeloid Leukemia in Remission; Blast Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Blasts Under 20 Percent of Bone Marrow Nucleated Cells; Blasts Under 20 Percent of Peripheral Blood White Cells; Chronic Myelomonocytic Leukemia; High Risk Myelodysplastic Syndrome; Myelodysplastic Syndrome; Recurrent Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Therapy-Related Acute Myeloid Leukemia; Therapy-Related Myelodysplastic Syndrome
M.D. Anderson Cancer Center
2013-06-11 PHASE1; PHASE2
NCT03515707 WITHDRAWN
Acute Myeloid Leukemia; Minimal Residual Disease Negativity
Fred Hutchinson Cancer Center
2018-07-10 PHASE2
NCT01760655 COMPLETED
Acute Myeloid Leukemia With FLT3/ITD Mutation; Acute Myeloid Leukemia With Gene Mutations; Acute Myeloid Leukemia With Inv(3) (q21.3;q26.2); GATA2, MECOM; Acute Myeloid Leukemia With t(6;9) (p23;q34.1); DEK-NUP214; Aplastic Anemia; Chronic Lymphocytic Leukemia; Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Chronic Myelomonocytic Leukemia; Follicular Lymphoma; Hodgkin Lymphoma; Myelodysplastic Syndrome; Myelofibrosis; Myeloid Leukemia; Non-Hodgkin Lymphoma; Plasma Cell Myeloma; Polycythemia Vera; Recurrent Adult Acute Myeloid Leukemia; Recurrent Childhood Acute Myeloid Leukemia; Refractory Acute Myeloid Leukemia; Secondary Acute Myeloid Leukemia; Therapy-Related Acute Myeloid Leukemia
Sidney Kimmel Comprehensive Cancer Center at Thomas Jefferson University
2012-12-24 PHASE2
NCT03513328 COMPLETED
Bone Marrow Failure Syndrome; Thalassemia; Sickle Cell Disease; Diamond Blackfan Anemia; Acquired Neutropenia in Newborn; Acquired Anemia Hemolytic; Acquired Thrombocytopenia; Hemophagocytic Lymphohistiocytoses; Wiskott-Aldrich Syndrome; Chronic Granulomatous Disease; Common Variable Immunodeficiency; X-linked Lymphoproliferative Disease; Severe Combined Immunodeficiency; Hurler Syndrome; Mannosidosis; Adrenoleukodystrophy
University of Florida
2018-06-15 PHASE1; PHASE2
NCT02248597 COMPLETED
Graft Versus Host Disease; Hematopoietic/Lymphoid Cancer
Wake Forest University Health Sciences
2015-02-25 PHASE2
NCT01498016 UNKNOWN
Acute Leukemia
Shanghai Jiao Tong University School of Medicine
2011-11 PHASE2
NCT03171831 UNKNOWN
Thalassemia Major
First Affiliated Hospital of Guangxi Medical University
2017-04-01 PHASE4
NCT02083250 COMPLETED
Acute Lymphoblastic Leukemia in Remission; Acute Myeloid Leukemia in Remission; Allogeneic Hematopoietic Stem Cell Transplantation Recipient; Myelodysplastic Syndrome; Previously Treated Myelodysplastic Syndrome; Recurrent Acute Lymphoblastic Leukemia; Recurrent Acute Myeloid Leukemia
M.D. Anderson Cancer Center
2014-03-06 PHASE1
NCT04220008 WITHDRAWN
Recurrent Aggressive Non-Hodgkin Lymphoma; Recurrent B-Cell Non-Hodgkin Lymphoma; Recurrent Burkitt Lymphoma; Recurrent Diffuse Large B-Cell Lymphoma; Recurrent High Grade B-Cell Lymphoma; Recurrent T-Cell Non-Hodgkin Lymphoma; Recurrent Transformed B-Cell Non-Hodgkin Lymphoma
M.D. Anderson Cancer Center
2021-10-29 PHASE2
NCT03733327 UNKNOWN
Primary Central Nervous System Lymphoma; Autologous Hematopoietic Stem Cell Transplantation; Conditioning
Nanfang Hospital, Southern Medical University
2018-11 PHASE2; PHASE3
NCT01704716 RECRUITING
Neuroblastoma
St. Anna Kinderkrebsforschung
2002-02 PHASE3
NCT03765632 COMPLETED
Severe Combined Immunodeficiency Due to ADA Deficiency
Great Ormond Street Hospital for Children NHS Foundation Trust
2018-01-03 PHASE1; PHASE2
NCT01019876 COMPLETED
Bone Marrow Failure; Osteopetrosis; Fanconi Anemia; Severe Combined Immunodeficiency
Columbia University
2002-09 PHASE2; PHASE3
NCT02544425 UNKNOWN
Extranodal NK-T-Cell Lymphoma
Samsung Medical Center
2016-02-21 PHASE2
NCT01033552 COMPLETED
Epidermolysis Bullosa
Masonic Cancer Center, University of Minnesota
2010-01 PHASE1; PHASE2
NCT03596892 UNKNOWN
Allogeneic Hematopoietic Stem Cell Transplantation; Conditions; Mixed-lineage-leukemia (MLL)-Rearranged Acute Leukemia
Nanfang Hospital, Southern Medical University
2018-07 PHASE2; PHASE3
NCT02961816 WITHDRAWN
Lymphoma
M.D. Anderson Cancer Center
2017-06 PHASE2
NCT03600909 TERMINATED
Fanconi Anemia; Myelodysplastic Syndrome (MDS); Acute Myelogenous Leukemia (AML)
Memorial Sloan Kettering Cancer Center
2018-05-15 PHASE2
NCT02670564 UNKNOWN
Acute Lymphoblastic Leukemia
Swiss Pediatric Oncology Group
2013-04 PHASE4
NCT01119066 COMPLETED
Acute Lymphoblastic Leukemia; Acute Myelogenous Leukemia; Myelodysplastic Syndrome; Multiple Myeloma
Memorial Sloan Kettering Cancer Center
2010-05-03 PHASE2
NCT03602131 UNKNOWN
Hodgkin Lymphoma; Non-hodgkin Lymphoma
Sichuan University
2019-01-01 PHASE2
NCT03517631 UNKNOWN
HIV Infections; AIDS
Shanghai Public Health Clinical Center
2018-02-27 PHASE1
NCT01471444 COMPLETED
Disorder Related to Bone Marrow Transplantation; Leukemia; Transplantation Infection
M.D. Anderson Cancer Center
2011-11-02 PHASE3
NCT01773395 TERMINATED
Myelodysplastic Syndrome; Acute Myeloid Leukemia; Chronic Myelomonocytic Leukemia
Dana-Farber Cancer Institute
2013-01-08 PHASE2
NCT03385096 UNKNOWN
Autologous Hematopoietic Stem Cell Transplantation; Conditioning; Multiple Myeloma
Nanfang Hospital, Southern Medical University
2018-01-02 PHASE2; PHASE3
NCT03151876 UNKNOWN
Lymphoma
Sichuan University
2017-06-12 PHASE2
NCT02605460 UNKNOWN
Acute Myeloid Leukemia; Acute Lymphoid Leukemia
Instituto Nacional de Ciencias Medicas y Nutricion Salvador Zubiran
2014-02 PHASE2
NCT04451200 Not yet recruiting
Acute Leukemia|Mielodysplasic Syndrome|Myeloproliferative Neoplasm
Institut Paoli-Calmettes
2020-11 Phase 2
NCT02799147 COMPLETED
Leukemia, Acute Lymphoblastic; Acute Myeloid Leukemia; Mixed-Lineage Acute Leukemias
St. Petersburg State Pavlov Medical University
2016-06 PHASE1; PHASE2
NCT02670109 UNKNOWN
Triple-Negative Invasive Breast Carcinoma; Residual Tumor
Instituto Nacional de Ciencias Medicas y Nutricion Salvador Zubiran
2018-02-01 PHASE2
NCT00629798 COMPLETED
Acute Myeloid Leukemia; Advanced Myelodysplastic Syndromes
Memorial Sloan Kettering Cancer Center
2008-02-12 PHASE2
NCT00258427 COMPLETED
Fanconi Anemia
Masonic Cancer Center, University of Minnesota
2002-03-26 PHASE2
NCT02441803 COMPLETED
Leukemia
M.D. Anderson Cancer Center
2015-09-14 PHASE2
NCT04127721 WITHDRAWN
Allogeneic Stem Cell Transplant Recipient; Hematologic and Lymphocytic Disorder; Hematopoietic and Lymphoid Cell Neoplasm
M.D. Anderson Cancer Center
2020-09-22 PHASE2
NCT03339700 UNKNOWN
Acute Lymphoblastic Leukemia, Adult
Instituto Nacional de Ciencias Medicas y Nutricion Salvador Zubiran
2018-09-15 PHASE2
NCT01366612 TERMINATED
Myeloid Malignancies; Acute Myelogenous Leukemia; Chronic Myelogenous Leukemia; Myeloproliferative Disorders; Myelodysplastic Syndrome
Hackensack Meridian Health
2010-06-16 PHASE3
NCT03128359 COMPLETED
Acute Leukemia; Chronic Lymphocytic Leukemia/Small Lymphocytic Lymphoma; Chronic Myelogenous Leukemia, BCR-ABL1 Positive; Diffuse Large B-Cell Lymphoma; Follicular Lymphoma; Graft Versus Host Disease; Hodgkin Lymphoma; Mantle Cell Lymphoma; Marginal Zone Lymphoma; Myelodysplastic Syndrome; Myeloproliferative Neoplasm; Recurrent Acute Myeloid Leukemia With Myelodysplasia-Related Changes; Recurrent Plasma Cell Myeloma; Refractory Plasma Cell Myeloma; Secondary Myelodysplastic Syndrome
City of Hope Medical Center
2017-05-30 PHASE2
NCT00950846 COMPLETED
Congenital Pediatric Disorders
Baylor College of Medicine
2009-09
NCT03674411 ACTIVE_NOT_RECRUITING
Acute Myeloid Leukemia; Acute Lymphocytic Leukemia; Biphenotypic/Undifferentiated Leukemia; Chronic Myelogenous Leukemia; Myelodysplasia; Relapsed Large Cell Lymphoma; Mantle Cell Lymphoma; Hodgkin Lymphoma; Burkitt Lymphoma; Relapsed T-Cell Lymphoma; Lymphoplasmacytic Lymphoma
Masonic Cancer Center, University of Minnesota
2019-01-02 PHASE2
NCT03229616 UNKNOWN
Autologous Hematopoietic Stem Cell Transplantation; Diffuse Large B-cell Lymphoma; Conditioning
Nanfang Hospital, Southern Medical University
2017-07-05 PHASE2; PHASE3
NCT01131169 COMPLETED
Multiple Myeloma
Memorial Sloan Kettering Cancer Center
2010-05 PHASE2
NCT02349906 COMPLETED
Primary Immunodeficiencies; Inborn Errors of Metabolism; Haemoglobinopathies; Bone Marrow Failure Syndromes
medac GmbH
2015-04 PHASE2
NCT03235973 UNKNOWN
Leukemia, Myeloid, Acute; Leukemia, Lymphoblastic, Acute
Institut Paoli-Calmettes
2018-04-28 PHASE1
NCT02793544 COMPLETED
Myelodysplastic Syndrome (MDS); Chronic Lymphocytic Leukemia (CLL); Chemotherapy-sensitive Lymphoma; Acute Lymphoblastic Leukemia (ALL)/T Lymphoblastic Lymphoma; Acute Myelogenous Leukemia (AML); Acute Biphenotypic Leukemia (ABL); Acute Undifferentiated Leukemia (AUL)
Center for International Blood and Marrow Transplant Research
2016-12 PHASE2
NCT01685411 TERMINATED
Acute Lymphoblastic Leukemia; Acute Myeloid Leukemia; Myelodysplastic Syndrome
Masonic Cancer Center, University of Minnesota
2013-01
NCT01625351 COMPLETED
Ewing Sarcoma; Gastrointestinal Tumor; Germ Cell Tumor; Hepatic Tumor; Lymphoma; Wilms Tumor; Rhabdoid Tumor; Clear Cell Carcinoma; Renal Cell Carcinoma; Melanoma; Neuroblastoma; Rhabdomyosarcoma; Non-rhabdomyosarcoma
St. Jude Children's Research Hospital
2012-08-20 PHASE1
NCT01380990 COMPLETED
Adenosine Deaminase Deficiency; Severe Combined Immunodeficiencies (SCID)
Great Ormond Street Hospital for Children NHS Foundation Trust
2012-11-15 PHASE1; PHASE2
NCT02836639 UNKNOWN
Lymphoma, Non-Hodgkin
Pusan National University Hospital
2016-02 PHASE2
NCT00176930 TERMINATED
Leukemia, Myeloid, Chronic; AML; Leukemia, Lymphocytic, Acute; MDS; Leukemia, Lymphocytic, Chronic; JMML; Hodgkin's Disease; Non-hodgkin's Lymphoma; Multiple Myeloma
Masonic Cancer Center, University of Minnesota
2001-10
NCT00612716 COMPLETED
Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm
Masonic Cancer Center, University of Minnesota
1999-10-06 PHASE2
NCT00426517 COMPLETED
Inherited Immune Deficiencies
National Institute of Allergy and Infectious Diseases (NIAID)
2007-01-19 EARLY_PHASE1
NCT01247701 COMPLETED
Myeloid Hematological Malignancies
Baylor College of Medicine
2010-11
NCT02744742 COMPLETED
Myelodysplastic Syndrome; Allogeneic Hematopoietic Stem Cell Transplantation; Conditioning
Nanfang Hospital, Southern Medical University
2016-04-18 PHASE2; PHASE3
NCT02784561 UNKNOWN
Leukemia
Chinese PLA General Hospital
2016-07 PHASE4
NCT02916979 COMPLETED
Leukemia, Lymphoid; Leukemia, Myeloid; Myelodysplastic Syndromes; Myelofibrosis; Lymphoma, Malignant; Multiple Myeloma; Waldenstrom Macroglobulinemia
Dartmouth-Hitchcock Medical Center
2016-09-06 PHASE1
NCT01596699 TERMINATED
Myeloid Malignancy; Bone Marrow Failure Syndrome; Transfusion-dependent Red Blood Cell (RBC) Defect; Congenital Immunodeficiency; Metabolic Disease; Severe Immune Dysregulation
University of California, San Francisco
2012-05-24 PHASE2
NCT02701673 WITHDRAWN
Lymphoma
M.D. Anderson Cancer Center
2016-06 PHASE1; PHASE2
NCT03303950 TERMINATED
Anemia; ASXL1 Gene Mutation; EZH2 Gene Mutation; IDH1 Gene Mutation; IDH2 Gene Mutation; Plasma Cell Myeloma; Primary Myelofibrosis; Recurrent Plasma Cell Myeloma; Secondary Myelofibrosis; Thrombocytopenia
University of Utah
2018-03-30 PHASE2
NCT02282904 TERMINATED
Chronic Granulomatous Disease
National Institute of Allergy and Infectious Diseases (NIAID)
2014-10-23 PHASE1; PHASE2
NCT02589145 TERMINATED
Lymphoma
M.D. Anderson Cancer Center
2016-06-22 PHASE1; PHASE2
NCT02627573 TERMINATED
Leukemia, Chronic Myeloid; Myelodysplastic Syndromes; Leukemia, Myeloid, Chronic, Atypical, BCR-ABL Negative
St. Petersburg State Pavlov Medical University
2015-07 PHASE2
NCT01413178 COMPLETED
Myeloma
M.D. Anderson Cancer Center
2011-09-30 PHASE3
NCT00857389 COMPLETED
Stem Cell Transplantation; Leukemia; Lymphoma
M.D. Anderson Cancer Center
2009-03-02 PHASE2
NCT02671708 COMPLETED
Autologous Hematopoietic Stem Cell Transplantation; Acute Myeloid Leukemia; Conditioning
Nanfang Hospital, Southern Medical University
2016-01 PHASE2; PHASE3
NCT03018223 COMPLETED
Non-Hodgkin's Lymphoma; Acute Leukemia in Remission; Chronic Myeloid Leukemia; Primary Myelofibrosis; Chronic Myelomonocytic Leukemia; Myelodysplastic Syndromes; Hodgkin Lymphoma; Multiple Myeloma
H. Lee Moffitt Cancer Center and Research Institute
2017-01-31 PHASE1
NCT01200329 COMPLETED
Lymphoma
M.D. Anderson Cancer Center
2011-06 PHASE2
NCT03601286 Recruiting
Severe Combined Immunodeficiency X-Linked
Great Ormond Street Hospital for Children NHS Foundation Trust
2018-12-21 Phase 1
NCT02999984 COMPLETED
Severe Combined Immunodeficiency Due to ADA Deficiency
University of California, Los Angeles
2016-12-16 PHASE1; PHASE2
NCT02114502 WITHDRAWN
Myeloma
M.D. Anderson Cancer Center
2014-09 PHASE2
NCT00943800 COMPLETED
Leukemia; Myelodysplastic Syndrome; Multiple Myeloma; Lymphoma
University of Chicago
2006-10-09
NCT01852071 COMPLETED
ADA-SCID
University of California, Los Angeles
2013-08-02 PHASE1; PHASE2
NCT00536601 COMPLETED
Adult Acute Lymphoblastic Leukemia in Remission; Adult Acute Myeloid Leukemia in Remission; Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities; Adult Acute Myeloid Leukemia With Del(5q); Adult Acute Myeloid Leukemia With Inv(16)(p13;q22); Adult Acute Myeloid Leukemia With t(15;17)(q22;q12); Adult Acute Myeloid Leukemia With t(16;16)(p13;q22); Adult Acute Myeloid Leukemia With t(8;21)(q22;q22); Adult Nasal Type Extranodal NK/T-cell Lymphoma; Childhood Acute Lymphoblastic Leukemia in Remission; Childhood Acute Myeloid Leukemia in Remission; Childhood Burkitt Lymphoma; Childhood Diffuse Large Cell Lymphoma; Childhood Immunoblastic Large Cell Lymphoma; Childhood Nasal Type Extranodal NK/T-cell Lymphoma; Ewing Sarcoma/Peripheral Primitive Neuroectodermal Tumor (PNET); Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue; Hepatosplenic T-cell Lymphoma; Intraocular Lymphoma; Nodal Marginal Zone B-cell Lymphoma; Peripheral T-cell Lymphoma; Plasma Cell Neoplasm; Primary Systemic Amyloidosis; Recurrent Adult Acute Lymphoblastic Leukemia; Recurrent Adult Acute Myeloid Leukemia; Recurrent Adult Burkitt Lymphoma; Recurrent Adult Diffuse Large Cell Lymphoma; Recurrent Adult Diffuse Mixed Cell Lymphoma; Recurrent Adult Diffuse Small Cleaved Cell Lymphoma; Recurrent Adult Grade III Lymphomatoid Granulomatosis; Recurrent Adult Hodgkin Lymphoma; Recurrent Adult Immunoblastic Large Cell Lymphoma; Recurrent Adult Lymphoblastic Lymphoma; Recurrent Childhood Acute Lymphoblastic Leukemia; Recurrent Childhood Acute Myeloid Leukemia; Recurrent Childhood Anaplastic Large Cell Lymphoma; Recurrent Childhood Grade III Lymphomatoid Granulomatosis; Recurrent Childhood Large Cell Lymphoma; Recurrent Childhood Lymphoblastic Lymphoma; Recurrent Childhood Small Noncleaved Cell Lymphoma; Recurrent Cutaneous T-cell Non-Hodgkin Lymphoma; Recurrent Ewing Sarcoma/Peripheral Primitive Neuroectodermal Tumor; Recurrent Grade 1 Follicular Lymphoma; Recurrent Grade 2 Follicular Lymphoma; Recurrent Grade 3 Follicular Lymphoma; Recurrent Malignant Testicular Germ Cell Tumor; Recurrent Mantle Cell Lymphoma; Recurrent Marginal Zone Lymphoma; Recurrent Neuroblastoma; Recurrent Small Lymphocytic Lymphoma; Recurrent/Refractory Childhood Hodgkin Lymphoma; Refractory Chronic Lymphocytic Leukemia; Refractory Multiple Myeloma; Regional Neuroblastoma; Splenic Marginal Zone Lymphoma; Testicular Lymphoma; Unspecified Adult Solid Tumor, Protocol Specific; Unspecified Childhood Solid Tumor, Protocol Specific; Waldenström Macroglobulinemia
Roswell Park Cancer Institute
2006-06-29
NCT01435447 COMPLETED
Lymphoid Malignancies
Shanghai Jiao Tong University School of Medicine
2011-04 PHASE2
NCT02120157 COMPLETED
Myeloablative Conditioning; HLA-mismatched Bone Marrow Transplantation; Graft Survival; Transplantation, Bone Marrow
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
2015-07-02 PHASE2
NCT02333838 UNKNOWN
Leukemia, Myeloid
Assistance Publique - Hôpitaux de Paris
2015-05 PHASE2
NCT01629511 TERMINATED
Allogeneic Hematopoietic Stem Cell Transplantation Recipient; Chronic Lymphocytic Leukemia; Prolymphocytic Leukemia; Richter Syndrome
M.D. Anderson Cancer Center
2012-11-21 PHASE1; PHASE2
NCT03235973 Unknown status
Leukemia Myeloid Acute|Leukemia Lymphoblastic Acute
Institut Paoli-Calmettes
2018-04-28 Phase 1
NCT02483325 COMPLETED
Hematological Diseases
Institut Paoli-Calmettes
2014-09 PHASE2
NCT01605032 COMPLETED
DS Stage I Plasma Cell Myeloma; DS Stage II Plasma Cell Myeloma; DS Stage III Plasma Cell Myeloma; Refractory Plasma Cell Myeloma
Albert Einstein College of Medicine
2012-02 PHASE2
NCT01795430 WITHDRAWN
Adult Supratentorial Primitive Neuroectodermal Tumor (PNET); Ewing Sarcoma of Bone; Extraosseous Ewing Sarcoma; Metastatic Ewing Sarcoma/Peripheral Primitive Neuroectodermal Tumor; Recurrent Childhood Supratentorial Primitive Neuroectodermal Tumor; Recurrent Ewing Sarcoma/Peripheral Primitive Neuroectodermal Tumor; Untreated Childhood Supratentorial Primitive Neuroectodermal Tumor
City of Hope Medical Center
2013-07
NCT00822393 COMPLETED
Acute Myeloid Leukemia; Myelodysplastic Syndrome
medac GmbH
2008-11-24 PHASE3
NCT02057770 TERMINATED
Leukemia, Myeloid, Acute
Washington University School of Medicine
2014-02-28 PHASE1
NCT00004088 COMPLETED
Multiple Myeloma and Plasma Cell Neoplasm
City of Hope Medical Center
1999-04-13 PHASE2
NCT01779882 COMPLETED
Myeloid Leukemia; Precursor Myeloid Neoplasms; Lymphoid Neoplasms
University Hospital, Basel, Switzerland
2013-01
NCT01824693 COMPLETED
Juvenile Myelomonocytic Leukemia
Children's Oncology Group
2013-06-24 PHASE2
NCT02130869 COMPLETED
Neuroblastoma; Lymphoma; High-risk Tumor
St. Jude Children's Research Hospital
2014-10-10 PHASE1
NCT01338987 COMPLETED
Myelodysplastic Syndrome; Acute Lymphocytic Leukemia; Acute Myelogenous Leukemia; Chronic Myelogenous Leukemia; Chronic Myelomonocytic Leukemia
National Cancer Institute (NCI)
2011-04-19 PHASE2
NCT00943319 COMPLETED
Leukemia; Lymphoma; Myeloma
University of Chicago
2012-03 PHASE1; PHASE2
NCT01983969 COMPLETED
Advanced Cancers; Lymphoma
M.D. Anderson Cancer Center
2013-11-07 PHASE1; PHASE2
NCT01572181 COMPLETED
Hematologic Malignancy
Nantes University Hospital
2012-04 PHASE2
NCT00003270 COMPLETED
Graft Versus Host Disease; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes
Roswell Park Cancer Institute
1997-09-04 PHASE2
NCT00475020 COMPLETED
Myelofibrosis
M.D. Anderson Cancer Center
2006-01-04 PHASE2
NCT01237951 COMPLETED
Myeloma
M.D. Anderson Cancer Center
2010-11-08 PHASE2
NCT01734850 COMPLETED
Human Immunodeficiency Virus
Calimmune, Inc.
2013-04 PHASE1; PHASE2
NCT01707004 COMPLETED
Acute Myeloid Leukemia With Multilineage Dysplasia Following Myelodysplastic Syndrome; Adult Acute Myeloid Leukemia in Remission; Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities; Adult Acute Myeloid Leukemia With Del(5q); Adult Acute Myeloid Leukemia With Inv(16)(p13;q22); Adult Acute Myeloid Leukemia With t(15;17)(q22;q12); Adult Acute Myeloid Leukemia With t(16;16)(p13;q22); Adult Acute Myeloid Leukemia With t(8;21)(q22;q22); de Novo Myelodysplastic Syndromes; Previously Treated Myelodysplastic Syndromes; Recurrent Adult Acute Myeloid Leukemia; Secondary Acute Myeloid Leukemia
University of Wisconsin, Madison
2013-05-16 PHASE2
NCT00987480 COMPLETED
Aplastic Anemia; Leukemia; Myelodysplastic Syndrome
Memorial Sloan Kettering Cancer Center
2009-09-25 PHASE2
NCT03794167 COMPLETED
Non-hodgkin Lymphoma
Soonchunhyang University Hospital
2012-06-01 PHASE2
NCT02750254 TERMINATED
Acute Myeloid Leukemia; Myelodysplastic Syndrome; Acute Lymphocytic Leukemia
Washington University School of Medicine
2016-06-27 PHASE1
NCT01471067 COMPLETED
Blood And Marrow Transplantation; Leukemia; Lymphoma; Transplantation Infection; Transplantation, Bone Marrow
M.D. Anderson Cancer Center
2012-07-13 PHASE1
NCT02410551 TERMINATED
Myeloproliferative Diseases
M.D. Anderson Cancer Center
2015-06-15 PHASE2
NCT02577094 WITHDRAWN
Lymphocyte B CD22 Positive Acute Lymphoblastic Leukemia
Nantes University Hospital
PHASE1; PHASE2
NCT01814475 COMPLETED
Myelofibrosis
Gruppo Italiano Trapianto di Midollo Osseo
2011-07 PHASE2
NCT02354443 TERMINATED
Metabolic Disorders
Fate Therapeutics
2015-06 PHASE1
NCT02294552 COMPLETED
Acute Myeloid Leukemia; Acute Lymphoid Leukemia; Lymphoma; Myelodysplastic Syndromes; Chronic Lymphocytic Leukemia; Immune System Diseases
Ivan S Moiseev
2014-10 PHASE2
NCT01410344 COMPLETED
Leukemia; Lymphoma; HIV
Medical College of Wisconsin
2011-09 PHASE2
NCT00498316 COMPLETED
Myelodysplastic Syndrome; Leukemia
M.D. Anderson Cancer Center
2007-07-03 PHASE1
NCT01969942 WITHDRAWN
Ewing Sarcoma
University of Louisville
2013-04 PHASE1
NCT01175356 COMPLETED
Ganglioneuroblastoma; Localized Resectable Neuroblastoma; Localized Unresectable Neuroblastoma; Regional Neuroblastoma; Stage 4 Neuroblastoma; Stage 4S Neuroblastoma
Children's Oncology Group
2011-12-21 PHASE1
NCT01071239 COMPLETED
Fanconi Anemia
Medical College of Wisconsin
2009-04 PHASE2
NCT02469974 WITHDRAWN
Myelofibrosis; MF
Marina Kremyanskaya
2015-05
NCT01643668 COMPLETED
Acute Myeloid Leukemia; Acute Lymphoblastic Leukemia; Myelodysplastic Syndrome
Massachusetts General Hospital
2012-07 PHASE2
NCT00553202 COMPLETED
Leukemia
Children's Oncology Group
2008-01 PHASE2
NCT00990249 COMPLETED
Leukemia; Lymphoma; Allogeneic Haematopoietic Stem Cell Transplantation; Acute Lymphoblastic Leukemia
M.D. Anderson Cancer Center
2009-10 PHASE2
NCT00578292 TERMINATED
Thalassemia
Baylor College of Medicine
2004-02
NCT00988013 COMPLETED
Acute Myeloid Leukemia; Lymphoblastic Leukemia; Acute Leukemia; Non Hodgkins Lymphoma; Chronic Myeloid Leukemia
University of Illinois at Chicago
2009-09
NCT01027000 COMPLETED
Leukemia; Lymphoma
Alliance for Clinical Trials in Oncology
2010-02 PHASE2
NCT01766375 UNKNOWN
Acute Myeloid Leukemia
Guangxi Medical University
2012-08 PHASE3
NCT01621477 TERMINATED
Acute Lymphoblastic Leukemia; Acute Myelocytic Leukemia; Chronic Myelocytic Leukemia; Juvenile Myelomonocytic Leukemia; Myelodysplastic Syndrome; Hodgkin or Non-Hodgkin Lymphoma; Sarcoma, Myeloid
St. Jude Children's Research Hospital
2012-08 PHASE2
NCT01093586 COMPLETED
Acute Myeloid Leukemia With Multilineage Dysplasia Following Myelodysplastic Syndrome; Adult Acute Lymphoblastic Leukemia in Remission; Adult Acute Megakaryoblastic Leukemia (M7); Adult Acute Minimally Differentiated Myeloid Leukemia (M0); Adult Acute Monoblastic Leukemia (M5a); Adult Acute Monocytic Leukemia (M5b); Adult Acute Myeloid Leukemia in Remission; Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities; Adult Acute Myeloid Leukemia With t(16;16)(p13;q22); Adult Erythroleukemia (M6a); Adult Nasal Type Extranodal NK/T-cell Lymphoma; Adult Pure Erythroid Leukemia (M6b); B-cell Adult Acute Lymphoblastic Leukemia; B-cell Childhood Acute Lymphoblastic Leukemia; Blastic Phase Chronic Myelogenous Leukemia; Burkitt Lymphoma; Childhood Acute Erythroleukemia (M6); Childhood Acute Lymphoblastic Leukemia in Remission; Childhood Acute Megakaryocytic Leukemia (M7); Childhood Acute Minimally Differentiated Myeloid Leukemia (M0); Childhood Acute Monoblastic Leukemia (M5a); Childhood Acute Monocytic Leukemia (M5b); Childhood Acute Myeloid Leukemia in Remission; Childhood Chronic Myelogenous Leukemia; Childhood Diffuse Large Cell Lymphoma; Childhood Immunoblastic Large Cell Lymphoma; Childhood Myelodysplastic Syndromes; Childhood Nasal Type Extranodal NK/T-cell Lymphoma; Chronic Myelomonocytic Leukemia; Chronic Phase Chronic Myelogenous Leukemia; Cutaneous B-cell Non-Hodgkin Lymphoma; de Novo Myelodysplastic Syndromes; Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue; Juvenile Myelomonocytic Leukemia; Myelodysplastic/Myeloproliferative Neoplasm, Unclassifiable; Nodal Marginal Zone B-cell Lymphoma; Previously Treated Myelodysplastic Syndromes; Prolymphocytic Leukemia; Recurrent Adult Acute Lymphoblastic Leukemia; Recurrent Adult Acute Myeloid Leukemia; Recurrent Adult Burkitt Lymphoma; Recurrent Adult Diffuse Large Cell Lymphoma; Recurrent Adult Diffuse Mixed Cell Lymphoma; Recurrent Adult Diffuse Small Cleaved Cell Lymphoma; Recurrent Adult Grade III Lymphomatoid Granulomatosis; Recurrent Adult Immunoblastic Large Cell Lymphoma; Recurrent Adult Lymphoblastic Lymphoma; Recurrent Childhood Acute Lymphoblastic Leukemia; Recurrent Childhood Acute Myeloid Leukemia; Recurrent Childhood Anaplastic Large Cell Lymphoma; Recurrent Childhood Grade III Lymphomatoid Granulomatosis; Recurrent Childhood Large Cell Lymphoma; Recurrent Childhood Lymphoblastic Lymphoma; Recurrent Childhood Small Noncleaved Cell Lymphoma; Recurrent Cutaneous T-cell Non-Hodgkin Lymphoma; Recurrent Grade 1 Follicular Lymphoma; Recurrent Grade 2 Follicular Lymphoma; Recurrent Grade 3 Follicular Lymphoma; Recurrent Mantle Cell Lymphoma; Recurrent Marginal Zone Lymphoma; Recurrent Mycosis Fungoides/Sezary Syndrome; Recurrent Small Lymphocytic Lymphoma; Refractory Chronic Lymphocytic Leukemia; Relapsing Chronic Myelogenous Leukemia; Secondary Acute Myeloid Leukemia; Secondary Myelodysplastic Syndromes; Secondary Myelofibrosis; Splenic Marginal Zone Lymphoma; Stage I Chronic Lymphocytic Leukemia; Stage II Chronic Lymphocytic Leukemia; Stage III Chronic Lymphocytic Leukemia; Stage IV Chronic Lymphocytic Leukemia; T-cell Adult Acute Lymphoblastic Leukemia; T-cell Childhood Acute Lymphoblastic Leukemia; T-cell Large Granular Lymphocyte Leukemia; Waldenstrom Macroglobulinemia
Case Comprehensive Cancer Center
2007-09 PHASE2
NCT01168219 COMPLETED
Acute Myeloid Leukemia; Adult Acute Megakaryoblastic Leukemia; Adult Acute Monoblastic Leukemia; Adult Acute Monocytic Leukemia; Adult Acute Myeloid Leukemia With Inv(16)(p13.1q22); CBFB-MYH11; Adult Acute Myeloid Leukemia With Maturation; Adult Acute Myeloid Leukemia With Minimal Differentiation; Adult Acute Myeloid Leukemia With t(16;16)(p13.1;q22); CBFB-MYH11; Adult Acute Myeloid Leukemia With t(8;21); (q22; q22.1); RUNX1-RUNX1T1; Adult Acute Myeloid Leukemia With t(9;11)(p21.3;q23.3); MLLT3-MLL; Adult Acute Myeloid Leukemia Without Maturation; Adult Acute Myelomonocytic Leukemia; Adult Erythroleukemia; Adult Pure Erythroid Leukemia; Alkylating Agent-Related Acute Myeloid Leukemia; de Novo Myelodysplastic Syndrome; Myelodysplastic Syndrome; Myelodysplastic Syndrome With Excess Blasts; Recurrent Adult Acute Myeloid Leukemia; Secondary Myelodysplastic Syndrome
National Cancer Institute (NCI)
2010-07-15 PHASE2
NCT00448357 COMPLETED
Chronic Myeloproliferative Disorders; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes
UNC Lineberger Comprehensive Cancer Center
2005-10 PHASE1; PHASE2
NCT00881556 TERMINATED
Epidermolysis Bullosa
Columbia University
2009-08-20 EARLY_PHASE1
NCT01421173 COMPLETED
Lymphoma
M.D. Anderson Cancer Center
2011-08 PHASE1
NCT00238433 COMPLETED
Lymphoma
OHSU Knight Cancer Institute
2005-03 PHASE2
NCT00245037 COMPLETED
Chronic Myeloproliferative Disorders; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Neoplasms; Precancerous Condition
OHSU Knight Cancer Institute
2005-06 PHASE1; PHASE2
NCT01798004 COMPLETED
Ganglioneuroblastoma; Stage 1 Neuroblastoma; Stage 2 Neuroblastoma; Stage 2A Neuroblastoma; Stage 2B Neuroblastoma; Stage 3 Neuroblastoma; Stage 4 Neuroblastoma; Stage 4S Neuroblastoma
Children's Oncology Group
2013-04-09 PHASE1
NCT01020734 COMPLETED
Leukemia
Asan Medical Center
2011-05 PHASE2
NCT00800839 COMPLETED
Hematologic Diseases; Leukemia; Lymphoma; Myeloma
M.D. Anderson Cancer Center
2008-09 PHASE2
NCT00003875 COMPLETED
Adult Acute Myeloid Leukemia in Remission; Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities; Adult Acute Myeloid Leukemia With Del(5q); Adult Acute Myeloid Leukemia With t(15;17)(q22;q12); Adult Acute Myeloid Leukemia With t(16;16)(p13;q22); Childhood Acute Myeloid Leukemia in Remission; Recurrent Adult Acute Myeloid Leukemia; Recurrent Childhood Acute Myeloid Leukemia
Fred Hutchinson Cancer Center
1998-10-13 PHASE2
NCT01043640 COMPLETED
Mucopolysaccharidosis; Hurler Syndrome; Hunter Syndrome; Maroteaux-Lamy Syndrome; Sly Syndrome; Alpha Mannosidosis; Fucosidosis; Aspartylglucosaminuria; Adrenoleukodystrophy (ALD); Krabbe Disease; Metachromatic Leukodystrophy (MLD); Sphingolipidoses; Peroxisomal Disorders
Masonic Cancer Center, University of Minnesota
2009-12 PHASE2
NCT00679536 UNKNOWN
Leukemia
Ann & Robert H Lurie Children's Hospital of Chicago
2008-05 PHASE1; PHASE2
NCT01279616 TERMINATED
Sickle Cell Disease
Nationwide Children's Hospital
2010-09 PHASE2
NCT01959477 COMPLETED
Adult Grade III Lymphomatoid Granulomatosis; Adult Nasal Type Extranodal NK/T-cell Lymphoma; Anaplastic Large Cell Lymphoma; Angioimmunoblastic T-cell Lymphoma; Childhood Burkitt Lymphoma; Childhood Diffuse Large Cell Lymphoma; Childhood Grade III Lymphomatoid Granulomatosis; Childhood Immunoblastic Large Cell Lymphoma; Childhood Nasal Type Extranodal NK/T-cell Lymphoma; Contiguous Stage II Adult Burkitt Lymphoma; Contiguous Stage II Adult Diffuse Large Cell Lymphoma; Contiguous Stage II Adult Diffuse Mixed Cell Lymphoma; Contiguous Stage II Adult Diffuse Small Cleaved Cell Lymphoma; Contiguous Stage II Adult Immunoblastic Large Cell Lymphoma; Contiguous Stage II Adult Lymphoblastic Lymphoma; Contiguous Stage II Grade 1 Follicular Lymphoma; Contiguous Stage II Grade 2 Follicular Lymphoma; Contiguous Stage II Grade 3 Follicular Lymphoma; Contiguous Stage II Mantle Cell Lymphoma; Contiguous Stage II Marginal Zone Lymphoma; Contiguous Stage II Small Lymphocytic Lymphoma; Cutaneous B-cell Non-Hodgkin Lymphoma; Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue; Hepatosplenic T-cell Lymphoma; Intraocular Lymphoma; Nodal Marginal Zone B-cell Lymphoma; Noncontiguous Stage II Adult Burkitt Lymphoma; Noncontiguous Stage II Adult Diffuse Large Cell Lymphoma; Noncontiguous Stage II Adult Diffuse Mixed Cell Lymphoma; Noncontiguous Stage II Adult Diffuse Small Cleaved Cell Lymphoma; Noncontiguous Stage II Adult Immunoblastic Large Cell Lymphoma; Noncontiguous Stage II Adult Lymphoblastic Lymphoma; Noncontiguous Stage II Grade 1 Follicular Lymphoma; Noncontiguous Stage II Grade 2 Follicular Lymphoma; Noncontiguous Stage II Grade 3 Follicular Lymphoma; Noncontiguous Stage II Mantle Cell Lymphoma; Noncontiguous Stage II Marginal Zone Lymphoma; Noncontiguous Stage II Small Lymphocytic Lymphoma; Noncutaneous Extranodal Lymphoma; Peripheral T-cell Lymphoma; Recurrent Adult Burkitt Lymphoma; Recurrent Adult Diffuse Large Cell Lymphoma; Recurrent Adult Diffuse Mixed Cell Lymphoma; Recurrent Adult Diffuse Small Cleaved Cell Lymphoma; Recurrent Adult Grade III Lymphomatoid Granulomatosis; Recurrent Adult Hodgkin Lymphoma; Recurrent Adult Immunoblastic Large Cell Lymphoma; Recurrent Adult Lymphoblastic Lymphoma; Recurrent Adult T-cell Leukemia/Lymphoma; Recurrent Childhood Anaplastic Large Cell Lymphoma; Recurrent Childhood Grade III Lymphomatoid Granulomatosis; Recurrent Childhood Large Cell Lymphoma; Recurrent Childhood Lymphoblastic Lymphoma; Recurrent Childhood Small Noncleaved Cell Lymphoma; Recurrent Cutaneous T-cell Non-Hodgkin Lymphoma; Recurrent Grade 1 Follicular Lymphoma; Recurrent Grade 2 Follicular Lymphoma; Recurrent Grade 3 Follicular Lymphoma; Recurrent Mantle Cell Lymphoma; Recurrent Marginal Zone Lymphoma; Recurrent Mycosis Fungoides/Sezary Syndrome; Recurrent Small Lymphocytic Lymphoma; Recurrent/Refractory Childhood Hodgkin Lymphoma; Refractory Hairy Cell Leukemia; Small Intestine Lymphoma; Splenic Marginal Zone Lymphoma; Stage I Adult Burkitt Lymphoma; Stage I Adult Diffuse Large Cell Lymphoma; Stage I Adult Diffuse Mixed Cell Lymphoma; Stage I Adult Diffuse Small Cleaved Cell Lymphoma; Stage I Adult Hodgkin Lymphoma; Stage I Adult Immunoblastic Large Cell Lymphoma; Stage I Adult Lymphoblastic Lymphoma; Stage I Adult T-cell Leukemia/Lymphoma; Stage I Childhood Anaplastic Large Cell Lymphoma; Stage I Childhood Hodgkin Lymphoma; Stage I Childhood Large Cell Lymphoma; Stage I Childhood Lymphoblastic Lymphoma; Stage I Childhood Small Noncleaved Cell Lymphoma; Stage I Cutaneous T-cell Non-Hodgkin Lymphoma; Stage I Grade 1 Follicular Lymphoma; Stage I Grade 2 Follicular Lymphoma; Stage I Grade 3 Follicular Lymphoma; Stage I Mantle Cell Lymphoma; Stage I Marginal Zone Lymphoma; Stage I Small Lymphocytic Lymphoma; Stage IA Mycosis Fungoides/Sezary Syndrome; Stage IB Mycosis Fungoides/Sezary Syndrome; Stage II Adult Hodgkin Lymphoma; Stage II Adult T-cell Leukemia/Lymphoma; Stage II Childhood Anaplastic Large Cell Lymphoma; Stage II Childhood Hodgkin Lymphoma; Stage II Childhood Large Cell Lymphoma; Stage II Childhood Lymphoblastic Lymphoma; Stage II Childhood Small Noncleaved Cell Lymphoma; Stage II Cutaneous T-cell Non-Hodgkin Lymphoma; Stage IIA Mycosis Fungoides/Sezary Syndrome; Stage IIB Mycosis Fungoides/Sezary Syndrome; Stage III Adult Burkitt Lymphoma; Stage III Adult Diffuse Large Cell Lymphoma; Stage III Adult Diffuse Mixed Cell Lymphoma; Stage III Adult Diffuse Small Cleaved Cell Lymphoma; Stage III Adult Hodgkin Lymphoma; Stage III Adult Immunoblastic Large Cell Lymphoma; Stage III Adult Lymphoblastic Lymphoma; Stage III Adult T-cell Leukemia/Lymphoma; Stage III Childhood Anaplastic Large Cell Lymphoma; Stage III Childhood Hodgkin Lymphoma; Stage III Childhood Large Cell Lymphoma; Stage III Childhood Lymphoblastic Lymphoma; Stage III Childhood Small Noncleaved Cell Lymphoma; Stage III Cutaneous T-cell Non-Hodgkin Lymphoma; Stage III Grade 1 Follicular Lymphoma; Stage III Grade 2 Follicular Lymphoma; Stage III Grade 3 Follicular Lymphoma; Stage III Mantle Cell Lymphoma; Stage III Marginal Zone Lymphoma; Stage III Small Lymphocytic Lymphoma; Stage IIIA Mycosis Fungoides/Sezary Syndrome; Stage IIIB Mycosis Fungoides/Sezary Syndrome; Stage IV Adult Burkitt Lymphoma; Stage IV Adult Diffuse Large Cell Lymphoma; Stage IV Adult Diffuse Mixed Cell Lymphoma; Stage IV Adult Diffuse Small Cleaved Cell Lymphoma; Stage IV Adult Hodgkin Lymphoma; Stage IV Adult Immunoblastic Large Cell Lymphoma; Stage IV Adult Lymphoblastic Lymphoma; Stage IV Adult T-cell Leukemia/Lymphoma; Stage IV Childhood Anaplastic Large Cell Lymphoma; Stage IV Childhood Hodgkin Lymphoma; Stage IV Childhood Large Cell Lymphoma; Stage IV Childhood Lymphoblastic Lymphoma; Stage IV Childhood Small Noncleaved Cell Lymphoma; Stage IV Cutaneous T-cell Non-Hodgkin Lymphoma; Stage IV Grade 1 Follicular Lymphoma; Stage IV Grade 2 Follicular Lymphoma; Stage IV Grade 3 Follicular Lymphoma; Stage IV Mantle Cell Lymphoma; Stage IV Marginal Zone Lymphoma; Stage IV Small Lymphocytic Lymphoma; Stage IVA Mycosis Fungoides/Sezary Syndrome; Stage IVB Mycosis Fungoides/Sezary Syndrome; T-cell Large Granular Lymphocyte Leukemia; Testicular Lymphoma; Waldenström Macroglobulinemia
Case Comprehensive Cancer Center
2014-03 EARLY_PHASE1
NCT01178658 UNKNOWN
Non-Hodgkin Lymphoma
Seoul National University Hospital
2010-07 PHASE2
NCT01800643 UNKNOWN
Acute Leukemia; Chronic Leukemia; Lymphoproliferative Disease; Myeloproliferative Disease; Immunodeficiency
Hospital Israelita Albert Einstein
2010-03 PHASE2; PHASE3
NCT01255527 UNKNOWN
Multiple Myeloma Patients Who Candidate for Autologous Peripheral Blood Stem Cell Transplantation
Yonsei University
2010-10 PHASE1; PHASE2
NCT00469144 COMPLETED
Myelodysplastic Syndrome; Leukemia; Acute Myeloid Leukemia
M.D. Anderson Cancer Center
2005-06 PHASE3
NCT01390402 COMPLETED
Leukemia; Chronic Myelogenous Leukemia
M.D. Anderson Cancer Center
2012-01 PHASE2
NCT01457885 COMPLETED
Acute Myeloblastic Leukemia
University of Michigan Rogel Cancer Center
2011-11 PHASE2
NCT00802113 COMPLETED
Non-Hodgkin's Lymphoma; Hodgkins Disease
Columbia University
2003-06 PHASE1; PHASE2
NCT01746173 TERMINATED
T-cell Non-Hodgkin Lymphoma
Dana-Farber Cancer Institute
2013-07 PHASE2
NCT00813124 COMPLETED
Stem Cell Transplantation; Leukemia
M.D. Anderson Cancer Center
2008-12 PHASE2
NCT01063439 UNKNOWN
Non Hodgkin's Lymphoma
Inje University
2010-01 PHASE2
NCT00796562 COMPLETED
MDS; Leukemias; Lymphomas
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
2008-12 PHASE2
NCT02007863 COMPLETED
Leukemia; Myelodysplasia; Acute Lymphocytic Leukemia; Acute Myelogenous Leukemia
University of Miami
2008-08
NCT01427881 COMPLETED
Accelerated Phase Chronic Myelogenous Leukemia; Adult Acute Lymphoblastic Leukemia in Remission; Adult Acute Megakaryoblastic Leukemia (M7); Adult Acute Myeloid Leukemia in Remission; Adult Erythroleukemia (M6a); Adult Nasal Type Extranodal NK/T-cell Lymphoma; Adult Pure Erythroid Leukemia (M6b); Anaplastic Large Cell Lymphoma; Angioimmunoblastic T-cell Lymphoma; Blastic Phase Chronic Myelogenous Leukemia; Childhood Acute Erythroleukemia (M6); Childhood Acute Lymphoblastic Leukemia in Remission; Childhood Acute Megakaryocytic Leukemia (M7); Childhood Acute Myeloid Leukemia in Remission; Childhood Burkitt Lymphoma; Childhood Chronic Myelogenous Leukemia; Childhood Diffuse Large Cell Lymphoma; Childhood Immunoblastic Large Cell Lymphoma; Childhood Myelodysplastic Syndromes; Childhood Nasal Type Extranodal NK/T-cell Lymphoma; Chronic Myelomonocytic Leukemia; Chronic Phase Chronic Myelogenous Leukemia; Cutaneous B-cell Non-Hodgkin Lymphoma; de Novo Myelodysplastic Syndromes; Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue; Hepatosplenic T-cell Lymphoma; Intraocular Lymphoma; Nodal Marginal Zone B-cell Lymphoma; Noncutaneous Extranodal Lymphoma; Peripheral T-cell Lymphoma; Philadelphia Chromosome Negative Chronic Myelogenous Leukemia; Post-transplant Lymphoproliferative Disorder; Previously Treated Myelodysplastic Syndromes; Recurrent Adult Acute Lymphoblastic Leukemia; Recurrent Adult Acute Myeloid Leukemia; Recurrent Adult Burkitt Lymphoma; Recurrent Adult Diffuse Large Cell Lymphoma; Recurrent Adult Diffuse Mixed Cell Lymphoma; Recurrent Adult Diffuse Small Cleaved Cell Lymphoma; Recurrent Adult Grade III Lymphomatoid Granulomatosis; Recurrent Adult Hodgkin Lymphoma; Recurrent Adult Immunoblastic Large Cell Lymphoma; Recurrent Adult Lymphoblastic Lymphoma; Recurrent Adult T-cell Leukemia/Lymphoma; Recurrent Childhood Acute Lymphoblastic Leukemia; Recurrent Childhood Acute Myeloid Leukemia; Recurrent Childhood Anaplastic Large Cell Lymphoma; Recurrent Childhood Grade III Lymphomatoid Granulomatosis; Recurrent Childhood Large Cell Lymphoma; Recurrent Childhood Lymphoblastic Lymphoma; Recurrent Childhood Small Noncleaved Cell Lymphoma; Recurrent Cutaneous T-cell Non-Hodgkin Lymphoma; Recurrent Grade 1 Follicular Lymphoma; Recurrent Grade 2 Follicular Lymphoma; Recurrent Grade 3 Follicular Lymphoma; Recurrent Mantle Cell Lymphoma; Recurrent Marginal Zone Lymphoma; Recurrent Mycosis Fungoides/Sezary Syndrome; Recurrent Small Lymphocytic Lymphoma; Recurrent/Refractory Childhood Hodgkin Lymphoma; Relapsing Chronic Myelogenous Leukemia; Secondary Acute Myeloid Leukemia; Secondary Myelodysplastic Syndromes; Small Intestine Lymphoma; Splenic Marginal Zone Lymphoma; Stage III Multiple Myeloma; Testicular Lymphoma; Waldenström Macroglobulinemia
Fred Hutchinson Cancer Center
2011-09 PHASE2
NCT01339988 UNKNOWN
Acute Leukemias; Chronic Leukemias; Myelodysplastic Syndrome; Juvenile Myelomonocytic Leukemia
Tel-Aviv Sourasky Medical Center
2011-06 PHASE4
NCT01749293 TERMINATED
Hematologic Malignancies
University of Illinois at Chicago
2012-08-30 PHASE2
NCT00907582 TERMINATED
Acute Promyelocytic Leukemia; Relapse
Shanghai Jiao Tong University School of Medicine
2009-06 PHASE2
NCT00691015 COMPLETED
Chronic Myeloproliferative Disorders; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Neoplasms
Barbara Ann Karmanos Cancer Institute
2008-05 PHASE2
NCT00997386 COMPLETED
Hematologic Neoplasms; Multiple Myeloma; Anemia, Aplastic; Hemoglobinuria, Paroxysmal; Myelofibrosis
University of Arizona
2009-09 PHASE2
NCT00317408 UNKNOWN
Lymphoma
European Inter-group Cooperation on Childhood and Adolescent Non Hodgkin Lymphoma
2004-04
NCT01622556 TERMINATED
Hematologic Malignancies
University of Virginia
2012-01 PHASE2
NCT01181271 COMPLETED
Diffuse, Large B-Cell, Lymphoma; Lymphoma, Low-Grade; T-Cell Lymphoma; Mantle-Cell Lymphoma; Hodgkin's Lymphoma; Chronic Lymphocytic Leukemia; Lymphoma, Small Lymphocytic
Massachusetts General Hospital
2010-08 PHASE2
NCT00179764 COMPLETED
Tumors; Malignant Melanoma; Hematological Malignancies; Myelogenous Leukemia, Chronic; Leukemia, Lymphoblastic, Acute
Ann & Robert H Lurie Children's Hospital of Chicago
2000-03-10
NCT01923935 UNKNOWN
Multiple Myeloma
Chonnam National University Hospital
2013-01 PHASE2
NCT01048827 COMPLETED
Acute Myeloid Leukemia
University of California, San Francisco
2009-11 PHASE1
NCT01338675 UNKNOWN
Chronic Granulomatous Disease
Seoul National University Hospital
2011-01 PHASE1; PHASE2
NCT01455506 COMPLETED
Acute Myeloid Leukemia; Myelodysplastic Syndrome
Hackensack Meridian Health
2009-05 PHASE1
NCT00731328 COMPLETED
Leukemia; Myelodysplastic Syndromes; Nonmalignant Neoplasm; Paroxysmal Nocturnal Hemoglobinuria
Asan Medical Center
2008-04 PHASE2
NCT01274195 UNKNOWN
Hematopoietic Stem Cell Transplantation
Seoul National University Hospital
2011-01 PHASE2
NCT00843947 COMPLETED
Hematologic Malignancies
University of California, Davis
2007-06 PHASE2
NCT01500161 TERMINATED
Acute Myelogenous Leukemia; Acute Lymphocytic Leukemia; Chronic Lymphocytic Leukemia; Chronic Myelogenous Leukemia; Hodgkins Disease; Non-Hodgkins Lymphoma; Aplastic Anemia; Multiple Myeloma; Myelodysplastic Syndrome
Texas Oncology Cancer Center
2011-11 PHASE2
NCT01464359 TERMINATED
Acute Myelogenous Leukemia; Refractory Acute Myelogenous Leukemia
Masonic Cancer Center, University of Minnesota
2011-10 PHASE2
NCT00619645 COMPLETED
Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes
University of California, Davis
2007-06 PHASE2
NCT01156350 UNKNOWN
Neuroblastoma
University Hospital, Clermont-Ferrand
2011-09 PHASE2
NCT00623935 COMPLETED
Acute Myelogenous Leukemia
University of Michigan Rogel Cancer Center
2007-03 PHASE2
NCT00863148 COMPLETED
MDS; AML; ALL; BAL
Nantes University Hospital
2009-10 PHASE2
NCT00775931 COMPLETED
Severe Osteopetrosis
Masonic Cancer Center, University of Minnesota
2008-08 PHASE2; PHASE3
NCT00496340 COMPLETED
Hematologic Malignancies
H. Lee Moffitt Cancer Center and Research Institute
2007-07 PHASE2
NCT00513474 COMPLETED
Chronic Myeloproliferative Disorders; Graft Versus Host Disease; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Neoplasms
Massachusetts General Hospital
2008-01 PHASE1
NCT01044745 TERMINATED
Accelerated Phase Chronic Myelogenous Leukemia; Adult Acute Lymphoblastic Leukemia in Remission; Adult Acute Myeloid Leukemia in Remission; Adult Nasal Type Extranodal NK/T-cell Lymphoma; Blastic Phase Chronic Myelogenous Leukemia; Contiguous Stage II Adult Burkitt Lymphoma; Contiguous Stage II Adult Diffuse Large Cell Lymphoma; Contiguous Stage II Adult Diffuse Mixed Cell Lymphoma; Contiguous Stage II Adult Diffuse Small Cleaved Cell Lymphoma; Contiguous Stage II Adult Immunoblastic Large Cell Lymphoma; Contiguous Stage II Adult Lymphoblastic Lymphoma; Contiguous Stage II Grade 1 Follicular Lymphoma; Contiguous Stage II Grade 2 Follicular Lymphoma; Contiguous Stage II Grade 3 Follicular Lymphoma; Contiguous Stage II Mantle Cell Lymphoma; Contiguous Stage II Marginal Zone Lymphoma; Contiguous Stage II Small Lymphocytic Lymphoma; de Novo Myelodysplastic Syndromes; Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue; Graft Versus Host Disease; Nodal Marginal Zone B-cell Lymphoma; Noncontiguous Stage II Adult Burkitt Lymphoma; Noncontiguous Stage II Adult Diffuse Large Cell Lymphoma; Noncontiguous Stage II Adult Diffuse Mixed Cell Lymphoma; Noncontiguous Stage II Adult Diffuse Small Cleaved Cell Lymphoma; Noncontiguous Stage II Adult Immunoblastic Large Cell Lymphoma; Noncontiguous Stage II Adult Lymphoblastic Lymphoma; Noncontiguous Stage II Grade 1 Follicular Lymphoma; Noncontiguous Stage II Grade 2 Follicular Lymphoma; Noncontiguous Stage II Grade 3 Follicular Lymphoma; Noncontiguous Stage II Mantle Cell Lymphoma; Noncontiguous Stage II Marginal Zone Lymphoma; Noncontiguous Stage II Small Lymphocytic Lymphoma; Previously Treated Myelodysplastic Syndromes; Recurrent Adult Acute Lymphoblastic Leukemia; Recurrent Adult Acute Myeloid Leukemia; Recurrent Adult Burkitt Lymphoma; Recurrent Adult Diffuse Large Cell Lymphoma; Recurrent Adult Diffuse Mixed Cell Lymphoma; Recurrent Adult Diffuse Small Cleaved Cell Lymphoma; Recurrent Adult Grade III Lymphomatoid Granulomatosis; Recurrent Adult Immunoblastic Large Cell Lymphoma; Recurrent Adult Lymphoblastic Lymphoma; Recurrent Adult T-cell Leukemia/Lymphoma; Recurrent Cutaneous T-cell Non-Hodgkin Lymphoma; Recurrent Grade 1 Follicular Lymphoma; Recurrent Grade 2 Follicular Lymphoma; Recurrent Grade 3 Follicular Lymphoma; Recurrent Mantle Cell Lymphoma; Recurrent Marginal Zone Lymphoma; Recurrent Mycosis Fungoides/Sezary Syndrome; Recurrent Small Lymphocytic Lymphoma; Refractory Chronic Lymphocytic Leukemia; Relapsing Chronic Myelogenous Leukemia; Secondary Myelodysplastic Syndromes; Splenic Marginal Zone Lymphoma; Stage I Adult Burkitt Lymphoma; Stage I Adult Diffuse Large Cell Lymphoma; Stage I Adult Diffuse Mixed Cell Lymphoma; Stage I Adult Diffuse Small Cleaved Cell Lymphoma; Stage I Adult Immunoblastic Large Cell Lymphoma; Stage I Adult Lymphoblastic Lymphoma; Stage I Adult T-cell Leukemia/Lymphoma; Stage I Chronic Lymphocytic Leukemia; Stage I Cutaneous T-cell Non-Hodgkin Lymphoma; Stage I Grade 1 Follicular Lymphoma; Stage I Grade 2 Follicular Lymphoma; Stage I Grade 3 Follicular Lymphoma; Stage I Mantle Cell Lymphoma; Stage I Marginal Zone Lymphoma; Stage I Mycosis Fungoides/Sezary Syndrome; Stage I Small Lymphocytic Lymphoma; Stage II Adult T-cell Leukemia/Lymphoma; Stage II Chronic Lymphocytic Leukemia; Stage II Cutaneous T-cell Non-Hodgkin Lymphoma; Stage II Mycosis Fungoides/Sezary Syndrome; Stage III Adult Burkitt Lymphoma; Stage III Adult Diffuse Large Cell Lymphoma; Stage III Adult Diffuse Mixed Cell Lymphoma; Stage III Adult Diffuse Small Cleaved Cell Lymphoma; Stage III Adult Immunoblastic Large Cell Lymphoma; Stage III Adult Lymphoblastic Lymphoma; Stage III Adult T-cell Leukemia/Lymphoma; Stage III Chronic Lymphocytic Leukemia; Stage III Cutaneous T-cell Non-Hodgkin Lymphoma; Stage III Grade 1 Follicular Lymphoma; Stage III Grade 2 Follicular Lymphoma; Stage III Grade 3 Follicular Lymphoma; Stage III Mantle Cell Lymphoma; Stage III Marginal Zone Lymphoma; Stage III Mycosis Fungoides/Sezary Syndrome; Stage III Small Lymphocytic Lymphoma; Stage IV Adult Burkitt Lymphoma; Stage IV Adult Diffuse Large Cell Lymphoma; Stage IV Adult Diffuse Mixed Cell Lymphoma; Stage IV Adult Diffuse Small Cleaved Cell Lymphoma; Stage IV Adult Immunoblastic Large Cell Lymphoma; Stage IV Adult Lymphoblastic Lymphoma; Stage IV Adult T-cell Leukemia/Lymphoma; Stage IV Chronic Lymphocytic Leukemia; Stage IV Cutaneous T-cell Non-Hodgkin Lymphoma; Stage IV Grade 1 Follicular Lymphoma; Stage IV Grade 2 Follicular Lymphoma; Stage IV Grade 3 Follicular Lymphoma; Stage IV Mantle Cell Lymphoma; Stage IV Marginal Zone Lymphoma; Stage IV Mycosis Fungoides/Sezary Syndrome; Stage IV Small Lymphocytic Lymphoma; Untreated Adult Acute Lymphoblastic Leukemia; Untreated Adult Acute Myeloid Leukemia; Waldenström Macroglobulinemia
University of Nebraska
2009-12-10 PHASE2
NCT00669890 TERMINATED
Acute Myeloid Leukemia; Juvenile Myelomonocytic Leukemia; Myelodysplastic Syndrome
New York Medical College
2004-05 PHASE1
NCT00084695 UNKNOWN
Childhood Langerhans Cell Histiocytosis; Fanconi Anemia; Leukemia; Lymphoma; Myelodysplastic Syndromes; Neuroblastoma; Sarcoma; Unspecified Childhood Solid Tumor, Protocol Specific
Milton S. Hershey Medical Center
2003-09 PHASE2
NCT00615589 TERMINATED
Multiple Myeloma; Plasma Cell Leukemia
University of Michigan Rogel Cancer Center
2008-02 PHASE2
NCT00613561 UNKNOWN
Severe Immunodeficiency Diseases
Ann & Robert H Lurie Children's Hospital of Chicago
2007-12 PHASE2
NCT01191957 COMPLETED
Acute Myeloid Leukemia (AML)
Gruppo Italiano Trapianto di Midollo Osseo
2008-01 PHASE3
NCT01087398 UNKNOWN
Osteopetrosis
Tehran University of Medical Sciences
2009-09 PHASE2; PHASE3
NCT01071486 WITHDRAWN
Busulfan Pharmacokinetic Analysis; GST Genetic Polymorphism
Rambam Health Care Campus
2009-08 PHASE4
NCT00822770 COMPLETED
Stem Cell Transplantation; Leukemia
M.D. Anderson Cancer Center
2009-01 PHASE1; PHASE2
NCT00410982 COMPLETED
Leukemia; Lymphoma; Myeloma
M.D. Anderson Cancer Center
2006-12 PHASE1
NCT00454480 COMPLETED
Leukemia; Myelodysplastic Syndromes
The University of New South Wales
2006-08 PHASE2; PHASE3
NCT00578344 TERMINATED
Sickle Cell Disease; Hemoglobin SC
Tami D. John
2005-07
NCT00623077 TERMINATED
Brain and Central Nervous System Tumors; Kidney Cancer; Liver Cancer; Retinoblastoma; Sarcoma
Masonic Cancer Center, University of Minnesota
2005-08 PHASE1
NCT00874315 WITHDRAWN
Neuroblastoma
Nationwide Children's Hospital
2008-09 PHASE2
NCT01135329 TERMINATED
Lymphoma; Leukemia; Myelodysplastic Syndrome
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
2010-08 PHASE2
NCT00887042 UNKNOWN
Acute Myeloid Leukemia
The Korean Society of Pediatric Hematology Oncology
2006-06 PHASE1; PHASE2
NCT00322101 COMPLETED
Acute Myeloid Leukemia With Multilineage Dysplasia Following Myelodysplastic Syndrome; Acute Myeloid Leukemia/Transient Myeloproliferative Disorder; Adult Acute Myeloid Leukemia in Remission; Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities; Adult Acute Myeloid Leukemia With Del(5q); Adult Acute Myeloid Leukemia With Inv(16)(p13;q22); Adult Acute Myeloid Leukemia With t(15;17)(q22;q12); Adult Acute Myeloid Leukemia With t(16;16)(p13;q22); Adult Acute Myeloid Leukemia With t(8;21)(q22;q22); Childhood Acute Myeloid Leukemia in Remission; Childhood Myelodysplastic Syndromes; de Novo Myelodysplastic Syndromes; Myelodysplastic Syndrome With Isolated Del(5q); Myelodysplastic/Myeloproliferative Neoplasm, Unclassifiable; Previously Treated Myelodysplastic Syndromes; Recurrent Adult Acute Myeloid Leukemia; Recurrent Childhood Acute Myeloid Leukemia; Secondary Acute Myeloid Leukemia; Secondary Myelodysplastic Syndromes
Fred Hutchinson Cancer Center
2006-01 PHASE3
NCT01009840 COMPLETED
Multiple Myeloma
Otsuka Pharmaceutical Development & Commercialization, Inc.
2010-05-01 PHASE2
NCT01118013 TERMINATED
Leukemia; Lymphoma; Lymphoproliferative Disorder; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Neoplasms
Alliance for Clinical Trials in Oncology
2010-12 PHASE2
NCT00885833 COMPLETED
Wiskott-Aldrich Syndrome
The Korean Society of Pediatric Hematology Oncology
2007-02 PHASE1; PHASE2
NCT00934232 TERMINATED
Multiple Myeloma
Guido Tricot
2009-08 PHASE1
NCT00176839 TERMINATED
Leukemia, Lymphocytic, Acute; AML; MDS
Masonic Cancer Center, University of Minnesota
2000-06-07 PHASE2; PHASE3
NCT01018446 COMPLETED
Hematopoietic Stem Cell Transplantation
Seoul National University Hospital
2008-12 PHASE1
NCT00328029 UNKNOWN
Signs and Symptoms, Respiratory
University Hospital, Strasbourg, France
2006-07 PHASE2
NCT00841724 COMPLETED
Hematological Malignancies
Nantes University Hospital
2009-01 PHASE2
NCT00020566 UNKNOWN
Sarcoma
University of Leicester
2001-02 PHASE3
NCT00815568 UNKNOWN
AML; MDS; ALL; CML; Lymphoma
Samsung Medical Center
2008-08 PHASE2
NCT03792815 COMPLETED
Non-Hodgkin's Lymphoma
Soonchunhyang University Hospital
2009-10 PHASE2
NCT00054327 COMPLETED
Leukemia; Lymphoma; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Diseases
Case Comprehensive Cancer Center
2000-11 PHASE2
NCT01359254 TERMINATED
Hematological Disease
University of Chicago
2010-04 PHASE2
NCT00301834 COMPLETED
Congenital Amegakaryocytic Thrombocytopenia; Diamond-blackfan Anemia; Leukemia; Myelodysplastic Syndromes; Severe Congenital Neutropenia
University of California, San Francisco
2005-01 PHASE2
NCT00506857 COMPLETED
Hematologic Malignancies
M.D. Anderson Cancer Center
2003-11 PHASE1; PHASE2
NCT00478244 TERMINATED
Epidermolysis Bullosa
Masonic Cancer Center, University of Minnesota
2007-04
NCT00852163 COMPLETED
Leukemia; Myelodysplastic Syndrome
Baylor Research Institute
2007-03 PHASE2
NCT01020539 COMPLETED
Acute Myelogenous Leukemia; Myelodysplastic Syndrome; Juvenile Myelomonocytic Leukemia
Columbia University
2002-09-11 PHASE1
NCT00598481 COMPLETED
Immunologic Deficiency Syndromes
Fondazione Telethon
2002-10-02 PHASE2
NCT00445744 COMPLETED
Adult Acute Myeloid Leukemia in Remission; Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities; Adult Acute Myeloid Leukemia With Del(5q); Adult Acute Myeloid Leukemia With Inv(16)(p13;q22); Adult Acute Myeloid Leukemia With t(15;17)(q22;q12); Adult Acute Myeloid Leukemia With t(16;16)(p13;q22); Adult Acute Myeloid Leukemia With t(8;21)(q22;q22); Childhood Acute Myeloid Leukemia in Remission; Childhood Myelodysplastic Syndromes; de Novo Myelodysplastic Syndromes; Essential Thrombocythemia; Myelodysplastic Syndrome With Isolated Del(5q); Polycythemia Vera; Previously Treated Myelodysplastic Syndromes; Primary Myelofibrosis; Recurrent Adult Acute Myeloid Leukemia; Recurrent Childhood Acute Myeloid Leukemia; Secondary Acute Myeloid Leukemia; Secondary Myelodysplastic Syndromes; Secondary Myelofibrosis; Untreated Adult Acute Myeloid Leukemia; Untreated Childhood Acute Myeloid Leukemia and Other Myeloid Malignancies
Fred Hutchinson Cancer Center
2006-12
NCT00556452 COMPLETED
Leukemia; Hodgkin Lymphoma; Non-Hodgkin Lymphoma; Multiple Myeloma; Myelodysplastic Syndrome
University of Michigan Rogel Cancer Center
2007-10 PHASE1; PHASE2
NCT00540995 TERMINATED
Adult Acute Myeloid Leukemia in Remission; Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities; Adult Acute Myeloid Leukemia With Del(5q); Adult Acute Myeloid Leukemia With Inv(16)(p13;q22); Adult Acute Myeloid Leukemia With t(15;17)(q22;q12); Adult Acute Myeloid Leukemia With t(16;16)(p13;q22); Adult Acute Myeloid Leukemia With t(8;21)(q22;q22); Blastic Phase Chronic Myelogenous Leukemia; Childhood Acute Myeloid Leukemia in Remission; Childhood Chronic Myelogenous Leukemia; Childhood Myelodysplastic Syndromes; Previously Treated Myelodysplastic Syndromes; Recurrent Adult Acute Myeloid Leukemia; Recurrent Childhood Acute Myeloid Leukemia; Refractory Anemia With Excess Blasts
City of Hope Medical Center
2007-06-11 PHASE1; PHASE2
NCT00802568 COMPLETED
Multiple Myeloma and Plasma Cell Neoplasm
Institut Paoli-Calmettes
2007-04 PHASE2
NCT00840684 COMPLETED
Leukemia
Institut Paoli-Calmettes
2009-01 PHASE1; PHASE2
NCT00806767 COMPLETED
Chronic Myeloproliferative Disorders; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Neoplasms
Institut Paoli-Calmettes
2007-03 PHASE2
NCT00782379 COMPLETED
Leukemia; Lymphoma; Myelodysplastic Syndromes
Northside Hospital, Inc.
2008-10 PHASE2
NCT00818961 TERMINATED
Leukemia; Lymphoma; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Diseases
Northside Hospital, Inc.
2005-05 PHASE2
NCT00416598 COMPLETED
Acute Myeloid Leukemia; Acute Myeloid Leukemia With Myelodysplasia-Related Changes; Adult Acute Myeloid Leukemia With Inv(16)(p13.1q22); CBFB-MYH11; Adult Acute Myeloid Leukemia With t(16;16)(p13.1;q22); CBFB-MYH11; Adult Acute Myeloid Leukemia With t(8;21); (q22; q22.1); RUNX1-RUNX1T1; Adult Acute Myeloid Leukemia With t(9;11)(p22.3;q23.3); MLLT3-KMT2A; Untreated Adult Acute Myeloid Leukemia
National Cancer Institute (NCI)
2006-11-15 PHASE2
NCT00448201 COMPLETED
Chronic Myeloproliferative Disorders; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes
UNC Lineberger Comprehensive Cancer Center
2011-01-07 PHASE2
NCT00670410 TERMINATED
Neuroblastoma
Columbia University
2003-11 PHASE1
NCT00477542 COMPLETED
Hematologic Malignancies
Indiana University
2007-05 PHASE1
NCT00427765 COMPLETED
Multiple Myeloma; Lymphoma
M.D. Anderson Cancer Center
2004-12 PHASE2
NCT00334672 UNKNOWN
Nonneoplastic Condition
Children's Cancer and Leukaemia Group
2006-03 PHASE3
NCT00836628 WITHDRAWN
Refractory Brain Tumors
Ann & Robert H Lurie Children's Hospital of Chicago
2008-07 PHASE1
NCT00555048 TERMINATED
Graft Versus Host Disease; Leukemia; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Diseases
Fred Hutchinson Cancer Center
2007-09 PHASE1; PHASE2
NCT00787761 COMPLETED
Myeloproliferative Disorders; Kidney Cancer; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Diseases
Northside Hospital, Inc.
2007-04 PHASE2
NCT00176904 COMPLETED
Adrenoleukodystrophy; Metachromatic Leukodystrophy; Globoid Cell Leukodystrophy; Gaucher's Disease; Fucosidosis; Wolman Disease; Niemann-Pick Disease; Batten Disease; GM1 Gangliosidosis; Tay Sachs Disease; Sandhoff Disease
Masonic Cancer Center, University of Minnesota
1995-01 PHASE2; PHASE3
NCT00627666 COMPLETED
Leukemia; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Neoplasms
Asan Medical Center
2003-01 PHASE2
NCT00179790 COMPLETED
Leukemia; Cancer
Ann & Robert H Lurie Children's Hospital of Chicago
2005-07 PHASE1; PHASE2
NCT00534430 COMPLETED
Leukemia; Myelodysplastic Syndromes
City of Hope Medical Center
2000-02-29 PHASE2
NCT00265889 COMPLETED
Lymphoma
Case Comprehensive Cancer Center
2002-02 PHASE2
NCT00112645 COMPLETED
Neuroblastoma; Sarcoma; Unspecified Childhood Solid Tumor, Protocol Specific
Milton S. Hershey Medical Center
2005-04 PHASE1
NCT00804947 UNKNOWN
Multiple Myeloma
Fundacion Para La Investigacion Hospital La Fe
2005-09 PHASE2
NCT00134017 COMPLETED
Chronic Myeloproliferative Disorders; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
2004-06 PHASE2
NCT00668564 TERMINATED
Hurler's Syndrome; Maroteaux-Lamy Syndrome; Sly Syndrome; Alpha Mannosidosis; Fucosidosis; Aspartylglucosaminuria; Sphingolipidoses; Krabbe Disease; Wolman's Disease; Niemann-Pick Disease Type B; Niemann-Pick Disease, Type C
Masonic Cancer Center, University of Minnesota
2008-03 PHASE2
NCT00740467 UNKNOWN
Graft Versus Host Disease; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Precancerous Condition
Institut Paoli-Calmettes
2008-01 PHASE2
NCT00003199 COMPLETED
Estrogen Receptor-negative Breast Cancer; Estrogen Receptor-positive Breast Cancer; Inflammatory Breast Cancer; Male Breast Cancer; Progesterone Receptor-negative Breast Cancer; Progesterone Receptor-positive Breast Cancer; Stage IIIB Breast Cancer; Stage IV Breast Cancer
Fred Hutchinson Cancer Center
1997-11 PHASE2
NCT00732316 COMPLETED
Leukemia; Myelodysplastic Syndromes
Asan Medical Center
2008-04 PHASE2
NCT00547196 COMPLETED
Leukemia; Lymphoma; Myelodysplastic Syndromes
City of Hope Medical Center
2005-08-16
NCT00499889 TERMINATED
Leukemia
M.D. Anderson Cancer Center
2003-02 PHASE2
NCT00774280 COMPLETED
Leukemia; Myelodysplastic Syndrome
Cooperative Study Group A for Hematology
2002-05 PHASE3
NCT00357396 COMPLETED
Sarcoma
Memorial Sloan Kettering Cancer Center
2005-06 PHASE2
NCT00113919 TERMINATED
Multiple Myeloma
University of Arkansas
2004-06 PHASE1; PHASE2
NCT00795132 COMPLETED
Acute Leukaemia; Chronic Disease; Leukemia; Myelodysplasia; Lymphoma
University of Utah
2004-04 PHASE2
NCT00301951 COMPLETED
Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes
University of California, San Francisco
2004-09 PHASE1
NCT00801931 TERMINATED
Leukemia; Lymphoma; Neuroblastoma; Immunodeficiencies; Anemia
Columbia University
2007-09-06 PHASE1; PHASE2
NCT00363467 TERMINATED
Acute Myeloid Leukemia (AML)
H. Lee Moffitt Cancer Center and Research Institute
2006-05
NCT00750126 UNKNOWN
Solid Tumors; Hematologic Neoplasms
University Hospital, Clermont-Ferrand
2007-04 PHASE2
NCT00186966 COMPLETED
Acute Myeloid Leukemia
Dutch Childhood Oncology Group
2002-03 PHASE3
NCT00176878 COMPLETED
Diamond-Blackfan Anemia; Kostmann's Neutropenia; Shwachman-Diamond Syndrome
Masonic Cancer Center, University of Minnesota
2000-06 PHASE2; PHASE3
NCT00304018 COMPLETED
Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes
University of California, San Francisco
2002-10 PHASE1
NCT00049517 COMPLETED
Leukemia
Eastern Cooperative Oncology Group
2002-12-19 PHASE3
NCT00785330 COMPLETED
Non-Hodgkin's Lymphoma
Institut fuer anwendungsorientierte Forschung und klinische Studien GmbH
2004-04 PHASE2
NCT00579111 TERMINATED
Myelodysplastic and Myeloproliferative Disorders; Acute Myelogenous Leukemia; Acute Lymphoblastic Leukemia; Chronic Myelogenous Leukemia; Multiple Myeloma; Plasma Cell Dyscrasia; Lymphoproliferative Disorders; Hematologic Diseases
Baylor College of Medicine
2007-06 PHASE1; PHASE2
NCT00186342 COMPLETED
Acute Disease; Myelodysplastic Syndromes; Leukemia, Myeloid, Chronic; Myeloproliferative Disorders; Blood and Marrow Transplant (BMT); Myelodysplastic Syndromes (MDS); Leukemia
Stanford University
1992-09
NCT00502905 COMPLETED
Leukemia
M.D. Anderson Cancer Center
2003-10 PHASE2
NCT00578435 COMPLETED
Genetic Disorders; Sickle Cell Anemia
Memorial Sloan Kettering Cancer Center
1994-01 PHASE2
NCT00684255 TERMINATED
Systemic Lupus Erythematosus; Systemic Sclerosis
New York Medical College
2007-08 PHASE1
NCT00521430 COMPLETED
Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes; Nonmalignant Neoplasm; Unspecified Adult Solid Tumor, Protocol Specific
Asan Medical Center
2004-04
NCT00176917 COMPLETED
Mucopolysaccharidosis I; Mucopolysaccharidosis VI; Mannosidosis; Mucolipidosis Type II (I-cell Disease)
Masonic Cancer Center, University of Minnesota
1999-05 PHASE2
NCT00611351 COMPLETED
Graft Versus Host Disease; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Diseases; Secondary Myelofibrosis
University of Nebraska
2005-06-07 PHASE2
NCT00281879 TERMINATED
Chronic Myeloproliferative Disorders; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Neoplasms; Unusual Cancers of Childhood
OHSU Knight Cancer Institute
2006-02 PHASE2
NCT00004128 UNKNOWN
Leukemia
European Organisation for Research and Treatment of Cancer - EORTC
1999-09 PHASE3
NCT00245115 TERMINATED
Leukemia
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
2005-10 PHASE1
NCT00531310 TERMINATED
Chronic Myeloid Leukemia
Columbia University
2003-01 PHASE2
NCT00003335 COMPLETED
Graft Versus Host Disease; Leukemia; Lymphoma; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Diseases
Case Comprehensive Cancer Center
1998-01 PHASE2
NCT00301912 WITHDRAWN
Anemia; Chronic Myeloproliferative Disorders; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Diseases
University of California, San Francisco
2002-01 PHASE2
NCT00007995 COMPLETED
Multiple Myeloma and Plasma Cell Neoplasm
Herbert Irving Comprehensive Cancer Center
1999-07 PHASE2
NCT00208923 COMPLETED
Hematologic Malignancies
Emory University
1998-07 PHASE2
NCT00313625 COMPLETED
Multiple Myeloma and Plasma Cell Neoplasm
Fred Hutchinson Cancer Center
2005-09 PHASE2
NCT00005797 COMPLETED
Chronic Myeloproliferative Disorders; Leukemia; Multiple Myeloma and Malignant Plasma Cell Neoplasms; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Neoplasms
H. Lee Moffitt Cancer Center and Research Institute
1993-03 PHASE2
NCT00296023 COMPLETED
Chronic Myeloproliferative Disorders; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes
University of California, San Francisco
1999-01
NCT00014469 COMPLETED
Graft Versus Host Disease; Leukemia; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Neoplasms
Memorial Sloan Kettering Cancer Center
2000-12 PHASE2
NCT00290628 TERMINATED
Chronic Myeloproliferative Disorders; Diamond-blackfan Anemia; Fanconi Anemia; Graft Versus Host Disease; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Diseases
Masonic Cancer Center, University of Minnesota
1999-10
NCT00049634 COMPLETED
Chronic Myeloproliferative Disorders; Leukemia; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Diseases
Fred Hutchinson Cancer Center
2002-01 PHASE1; PHASE2
NCT00002761 WITHDRAWN
Leukemia
Columbia University
1996-02 PHASE1; PHASE2
NCT00077116 COMPLETED
Leukemia; Myelodysplastic Syndromes
European Organisation for Research and Treatment of Cancer - EORTC
2003-11 PHASE2
NCT00053196 COMPLETED
Leukemia; Lymphoma; Multiple Myeloma; Plasma Cell Neoplasm; Myelodysplastic Syndromes; Myeloproliferative Neoplasms
Alliance for Clinical Trials in Oncology
2002-12 PHASE2
NCT00070174 COMPLETED
Leukemia
Children's Oncology Group
2003-12 PHASE2
NCT00002798 COMPLETED
Childhood Acute Erythroleukemia (M6); Childhood Acute Megakaryocytic Leukemia (M7); Childhood Acute Monoblastic Leukemia (M5a); Childhood Acute Monocytic Leukemia (M5b); Childhood Acute Myeloblastic Leukemia With Maturation (M2); Childhood Acute Myeloblastic Leukemia Without Maturation (M1); Childhood Acute Myelomonocytic Leukemia (M4); Childhood Myelodysplastic Syndromes; Chronic Myelomonocytic Leukemia; de Novo Myelodysplastic Syndromes; Refractory Anemia; Refractory Anemia With Excess Blasts; Refractory Anemia With Excess Blasts in Transformation; Refractory Anemia With Ringed Sideroblasts; Secondary Myelodysplastic Syndromes; Untreated Childhood Acute Myeloid Leukemia and Other Myeloid Malignancies
National Cancer Institute (NCI)
1996-08 PHASE3
NCT00004231 COMPLETED
Lymphoma
Northwestern University
1999-10 PHASE2
NCT00060255 COMPLETED
Breast Cancer; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Testicular Germ Cell Tumor; Unspecified Adult Solid Tumor, Protocol Specific; Unspecified Childhood Solid Tumor, Protocol Specific
Roswell Park Cancer Institute
1991-12 PHASE2
NCT00029380 COMPLETED
Hematologic Diseases; Anemia, Sickle Cell; Beta-Thalassemia; Hematopoietic Stem Cell Transplantation
National Heart, Lung, and Blood Institute (NHLBI)
1999-01 PHASE2
NCT00003116 COMPLETED
Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Diseases
Case Comprehensive Cancer Center
1997-05 PHASE2
NCT00186810 COMPLETED
Sickle Cell Disease
St. Jude Children's Research Hospital
1992-12 PHASE2
NCT00005940 COMPLETED
Adult Acute Myeloid Leukemia in Remission; Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities; Adult Acute Myeloid Leukemia With Del(5q); Adult Acute Myeloid Leukemia With Inv(16)(p13;q22); Adult Acute Myeloid Leukemia With t(15;17)(q22;q12); Adult Acute Myeloid Leukemia With t(16;16)(p13;q22); Adult Acute Myeloid Leukemia With t(8;21)(q22;q22)
Fred Hutchinson Cancer Center
1999-10 PHASE2
NCT00003336 COMPLETED
Leukemia; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Diseases
Case Comprehensive Cancer Center
1998-01 PHASE2
NCT00008190 COMPLETED
Leukemia
Herbert Irving Comprehensive Cancer Center
1999-03 PHASE2
NCT00152126 COMPLETED
Neuroblastoma; Central Nervous System Tumors; Lymphomas; Wilms Tumor
St. Jude Children's Research Hospital
2003-08
NCT00003913 COMPLETED
Leukemia; Lymphoma; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Diseases
Fred Hutchinson Cancer Center
1998-12 PHASE2
NCT00006363 COMPLETED
Adult Acute Basophilic Leukemia; Adult Acute Eosinophilic Leukemia; Adult Acute Erythroid Leukemia (M6); Adult Acute Megakaryoblastic Leukemia (M7); Adult Acute Minimally Differentiated Myeloid Leukemia (M0); Adult Acute Monoblastic Leukemia (M5a); Adult Acute Monoblastic Leukemia and Acute Monocytic Leukemia (M5); Adult Acute Monocytic Leukemia (M5b); Adult Acute Myeloblastic Leukemia With Maturation (M2); Adult Acute Myeloblastic Leukemia Without Maturation (M1); Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities; Adult Acute Myeloid Leukemia With Del(5q); Adult Acute Myeloid Leukemia With Inv(16)(p13;q22); Adult Acute Myeloid Leukemia With t(16;16)(p13;q22); Adult Acute Myeloid Leukemia With t(8;21)(q22;q22); Adult Acute Myelomonocytic Leukemia (M4); Adult Erythroleukemia (M6a); Adult Pure Erythroid Leukemia (M6b); Childhood Acute Basophilic Leukemia; Childhood Acute Eosinophilic Leukemia; Childhood Acute Erythroleukemia (M6); Childhood Acute Megakaryocytic Leukemia (M7); Childhood Acute Minimally Differentiated Myeloid Leukemia (M0); Childhood Acute Monoblastic Leukemia (M5a); Childhood Acute Monoblastic Leukemia and Acute Monocytic Leukemia (M5); Childhood Acute Monocytic Leukemia (M5b); Childhood Acute Myeloblastic Leukemia With Maturation (M2); Childhood Acute Myeloblastic Leukemia Without Maturation (M1); Childhood Acute Myelomonocytic Leukemia (M4); Childhood Myelodysplastic Syndromes; de Novo Myelodysplastic Syndromes; Untreated Adult Acute Myeloid Leukemia; Untreated Childhood Acute Myeloid Leukemia and Other Myeloid Malignancies
National Cancer Institute (NCI)
2000-11 PHASE3
NCT00043810 TERMINATED
Acute Myelogenous Leukemia; Myelodysplastic Syndrome
M.D. Anderson Cancer Center
2002-07 PHASE1; PHASE2
NCT00005986 TERMINATED
Leukemia
Masonic Cancer Center, University of Minnesota
2000-08 PHASE2
NCT00004896 COMPLETED
Leukemia; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Diseases
Northwestern University
1999-10 PHASE2
NCT00004907 COMPLETED
Lymphoma
Northwestern University
1999-10 PHASE1; PHASE2
NCT00004181 COMPLETED
Chronic Myeloproliferative Disorders; Leukemia; Multiple Myeloma and Plasma Cell Neoplasm
Northwestern University
1999-10 PHASE2
NCT00305708 COMPLETED
Congenital Amegakaryocytic Thrombocytopenia; Diamond-blackfan Anemia; Fanconi Anemia; Leukemia; Severe Congenital Neutropenia; Thrombocytopenia
University of California, San Francisco
2000-08 PHASE1; PHASE2
NCT00005824 COMPLETED
Lymphoma
AIDS Malignancy Consortium
2000-11 PHASE2
NCT00003414 COMPLETED
Graft Versus Host Disease; Lymphoma
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
1997-10 PHASE3
NCT00005866 COMPLETED
Leukemia; Myelodysplastic Syndromes
SWOG Cancer Research Network
2000-02 PHASE3
NCT00002868 COMPLETED
Leukemia
Eastern Cooperative Oncology Group
1997-11-20 PHASE3
NCT00040469 TERMINATED
Sickle Cell Anemia; Hemoglobinopathy; Thalassemia
Baylor College of Medicine
2000-08 PHASE2
NCT00034528 TERMINATED
Hemoglobinopathies; Anemia, Sickle Cell; Hemoglobin SC Disease; Thalassemia; Thalassemia Major
National Institute of Allergy and Infectious Diseases (NIAID)
2001-09 PHASE2
NCT00002547 COMPLETED
Leukemia; Myelodysplastic Syndromes
Barbara Ann Karmanos Cancer Institute
1987-08 PHASE2
NCT00055653 COMPLETED
Leukemia; Lymphoma; Myelodysplastic Syndromes; Myelodysplastic-Myeloproliferative Diseases
Roswell Park Cancer Institute
2003-01 PHASE2
NCT00006246 COMPLETED
Brain and Central Nervous System Tumors; Childhood Germ Cell Tumor; Leukemia; Lymphoma; Metastatic Cancer; Retinoblastoma; Sarcoma
Pediatric Brain Tumor Consortium
2000-11 PHASE1
NCT00002792 COMPLETED
Chronic Myeloproliferative Disorders; Leukemia; Myelodysplastic/Myeloproliferative Diseases
Fred Hutchinson Cancer Center
1996-06 PHASE2
NCT00003972 COMPLETED
Breast Cancer
Fred Hutchinson Cancer Center
1998-07 PHASE3
NCT00002768 COMPLETED
Leukemia
Alliance for Clinical Trials in Oncology
1996-06 PHASE2
NCT00002831 COMPLETED
Leukemia
M.D. Anderson Cancer Center
1995-08-01 PHASE1; PHASE2
NCT00006054 TERMINATED
Immunologic Deficiency Syndromes; Chediak-Higashi Syndrome; Common Variable Immunodeficiency; Graft Versus Host Disease; X-Linked Lymphoproliferative Syndrome; Familial Erythrophagocytic Lymphohistiocytosis; Hemophagocytic Lymphohistiocytosis; X-linked Agammaglobulinemia; Wiskott-Aldrich Syndrome; Chronic Granulomatous Disease; X-linked Hyper IgM Syndrome; Severe Combined Immunodeficiency; Leukocyte Adhesion Deficiency Syndrome; Virus-Associated Hemophagocytic Syndrome
Fairview University Medical Center
2000-03
NCT00002592 COMPLETED
Leukemia
Abramson Cancer Center at Penn Medicine
1993-06 PHASE2
NCT00003926 TERMINATED
Brain and Central Nervous System Tumors; Childhood Germ Cell Tumor; Chordoma; Kidney Cancer; Liver Cancer; Neuroblastoma; Ovarian Cancer; Retinoblastoma; Sarcoma
Masonic Cancer Center, University of Minnesota
1998-11 PHASE1
NCT00003081 COMPLETED
Sarcoma
Fred Hutchinson Cancer Center
1998-03 PHASE1
NCT00005948 COMPLETED
Leukemia
Fred Hutchinson Cancer Center
2000-01 PHASE2
NCT00003960 COMPLETED
Leukemia; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
1998-04 PHASE2
NCT00003146 COMPLETED
Multiple Myeloma and Plasma Cell Neoplasm
Fred Hutchinson Cancer Center
1997-11 PHASE2
NCT00006126 WITHDRAWN
Breast Cancer; Kidney Cancer; Lung Cancer; Melanoma (Skin); Testicular Germ Cell Tumor
Northwestern University
1999-09 PHASE1
NCT00002961 TERMINATED
Leukemia
Children's Hospital of Philadelphia
1995-10 PHASE3
NCT00003462 COMPLETED
Brain and Central Nervous System Tumors
Duke University
1998-04 PHASE1
NCT00005641 TERMINATED
Chronic Myeloproliferative Disorders; Graft Versus Host Disease; Leukemia; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes
H. Lee Moffitt Cancer Center and Research Institute
1997-09 PHASE2
NCT00705120 COMPLETED
Osteogenesis Imperfecta
St. Jude Children's Research Hospital
1995-11 PHASE1
NCT00002502 COMPLETED
Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes
Memorial Sloan Kettering Cancer Center
1992-07 PHASE2
NCT01177371 COMPLETED
Accelerated Phase Chronic Myelogenous Leukemia; Adult Acute Lymphoblastic Leukemia in Remission; Adult Acute Megakaryoblastic Leukemia (M7); Adult Acute Monoblastic Leukemia (M5a); Adult Acute Monocytic Leukemia (M5b); Adult Acute Myeloblastic Leukemia With Maturation (M2); Adult Acute Myeloblastic Leukemia Without Maturation (M1); Adult Acute Myeloid Leukemia in Remission; Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities; Adult Acute Myeloid Leukemia With Del(5q); Adult Acute Myeloid Leukemia With Inv(16)(p13;q22); Adult Acute Myeloid Leukemia With T(15;17)(q22;q12); Adult Acute Myeloid Leukemia With T(16;16)(p13;q22); Adult Acute Myeloid Leukemia With T(8;21)(q22;q22); Adult Acute Myelomonocytic Leukemia (M4); Adult Acute Promyelocytic Leukemia (M3); Adult Erythroleukemia (M6a); Adult Nasal Type Extranodal NK/T-cell Lymphoma; Adult Pure Erythroid Leukemia (M6b); Anaplastic Large Cell Lymphoma; Angioimmunoblastic T-cell Lymphoma; Burkitt Lymphoma; Childhood Acute Erythroleukemia (M6); Childhood Acute Lymphoblastic Leukemia in Remission; Childhood Acute Megakaryocytic Leukemia (M7); Childhood Acute Monoblastic Leukemia (M5a); Childhood Acute Monocytic Leukemia (M5b); Childhood Acute Myeloblastic Leukemia With Maturation (M2); Childhood Acute Myeloblastic Leukemia Without Maturation (M1); Childhood Acute Myeloid Leukemia in Remission; Childhood Acute Myelomonocytic Leukemia (M4); Childhood Acute Promyelocytic Leukemia (M3); Childhood Chronic Myelogenous Leukemia; Childhood Myelodysplastic Syndromes; Chronic Phase Chronic Myelogenous Leukemia; Cutaneous B-cell Non-Hodgkin Lymphoma; De Novo Myelodysplastic Syndromes; Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue; Hepatosplenic T-cell Lymphoma; Intraocular Lymphoma; Nodal Marginal Zone B-cell Lymphoma; Peripheral T-Cell Lymphoma; Post-transplant Lymphoproliferative Disorder; Previously Treated Myelodysplastic Syndromes; Recurrent Adult Acute Lymphoblastic Leukemia; Recurrent Adult Acute Myeloid Leukemia; Recurrent Adult Burkitt Lymphoma; Recurrent Adult Diffuse Large Cell Lymphoma; Recurrent Adult Diffuse Mixed Cell Lymphoma; Recurrent Adult Diffuse Small Cleaved Cell Lymphoma; Recurrent Adult Grade III Lymphomatoid Granulomatosis; Recurrent Adult Hodgkin Lymphoma; Recurrent Adult Immunoblastic Large Cell Lymphoma; Recurrent Adult Lymphoblastic Lymphoma; Recurrent Adult Non-Hodgkin Lymphoma; Recurrent Adult T-cell Leukemia/Lymphoma; Recurrent Childhood Acute Lymphoblastic Leukemia; Recurrent Childhood Acute Myeloid Leukemia; Recurrent Cutaneous T-cell Non-Hodgkin Lymphoma; Recurrent Grade 1 Follicular Lymphoma; Recurrent Grade 2 Follicular Lymphoma; Recurrent Grade 3 Follicular Lymphoma; Recurrent Mantle Cell Lymphoma; Recurrent Marginal Zone Lymphoma; Recurrent Mycosis Fungoides/Sezary Syndrome; Recurrent Small Lymphocytic Lymphoma; Refractory Multiple Myeloma; Relapsing Chronic Myelogenous Leukemia; Secondary Myelodysplastic Syndromes; Small Intestine Lymphoma; Splenic Marginal Zone Lymphoma; Testicular Lymphoma; Waldenstrom Macroglobulinemia
Case Comprehensive Cancer Center
1988-03 PHASE2
NCT00002554 COMPLETED
Leukemia
Fred Hutchinson Cancer Center
1993-11 PHASE2
NCT00003661 COMPLETED
Graft Versus Host Disease; Leukemia; Lymphoma; Myelodysplastic Syndromes; Neuroblastoma
Roswell Park Cancer Institute
1998-06 PHASE2
NCT00667927 COMPLETED
Acute Myeloid Leukemia
St. Jude Children's Research Hospital
1991-03 PHASE1
NCT00030719 UNKNOWN
Neuroblastoma
University of Leicester
2001-12 PHASE3
NCT00226512 WITHDRAWN
Acute Myeloid Leukemia; Myelodysplastic Syndrome
Hadassah Medical Organization
2004-07 PHASE3
NCT00156858 UNKNOWN
Hematologic Malignancy
Alberta Health services
1998-01
NCT00006056 UNKNOWN
Chediak-Higashi Syndrome; Graft Versus Host Disease; X-Linked Lymphoproliferative Syndrome; Familial Erythrophagocytic Lymphohistiocytosis; Hemophagocytic Lymphohistiocytosis; Virus-Associated Hemophagocytic Syndrome
Fairview University Medical Center
2000-03
NCT00006367 COMPLETED
Chronic Myeloproliferative Disorders
Fred Hutchinson Cancer Center
2000-05 PHASE2
NCT00025649 COMPLETED
Neuroblastoma
European Infant Neuroblastoma Study Group - 1999
1999-07 PHASE2
NCT00005893 COMPLETED
Neutropenia; Sickle Cell Anemia; Thalassemia Major; Red-Cell Aplasia, Pure
Fairview University Medical Center
2000-06
NCT00024050 COMPLETED
Leukemia; Myelodysplastic Syndromes
Fred Hutchinson Cancer Center
2001-02 PHASE2
NCT00003195 COMPLETED
Multiple Myeloma and Plasma Cell Neoplasm
Fred Hutchinson Cancer Center
1997-12 PHASE2
NCT00081055 WITHDRAWN
Graft Versus Host Disease; Leukemia; Myelodysplastic Syndromes
Mesoblast International Sàrl
PHASE2
NCT00002771 UNKNOWN
Leukemia
German CML Study Group
1995-01 PHASE3
NCT00027937 COMPLETED
Lymphoma; Unspecified Adult Solid Tumor, Protocol Specific; Unspecified Childhood Solid Tumor, Protocol Specific
Fred Hutchinson Cancer Center
2001-08 PHASE2
NCT00025402 UNKNOWN
Leukemia
III. Medizinische Klinik Mannheim
1997-07 PHASE3
NCT00024193 UNKNOWN
Neuroblastoma
Children's Cancer and Leukaemia Group
1999-04 PHASE2
NCT00228852 COMPLETED
T-Cell Immune Deficiency Diseases; Severe Combined Immunodeficiency
Emory University
PHASE1; PHASE2
NCT00436761 UNKNOWN
Unspecified Childhood Solid Tumor, Protocol Specific
Milton S. Hershey Medical Center
2004-05 PHASE1
NCT00516152 COMPLETED
Chronic Myeloid Leukemia; Acute Myelogenous Leukemia; Myelodysplasia; Acute Lymphocytic Leukemia; Severe Aplastic Anemia; Non-Hodgkin's Lymphoma; Lymphoproliferative Disease; Multiple Myeloma; Advanced Myeloproliferative Disease
University of California, San Francisco
2002-11 PHASE2
NCT00281983 COMPLETED
Chronic Lymphocytic Leukemia
German CLL Study Group
2000-06 PHASE1; PHASE2
NCT00003619 COMPLETED
Chronic Myeloproliferative Disorders; Leukemia; Myelodysplastic Syndromes; Thrombocytopenia
Drexel University College of Medicine
1998-02 PHASE1; PHASE2
NCT00054340 COMPLETED
Chronic Myeloproliferative Disorders; Graft Versus Host Disease; Leukemia; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Diseases
Fred Hutchinson Cancer Center
2002-10 PHASE1; PHASE2
NCT00295997 UNKNOWN
Chronic Myeloproliferative Disorders; Kidney Cancer; Leukemia; Lymphoma; Multiple Myeloma and Plasma Cell Neoplasm; Myelodysplastic Syndromes; Myelodysplastic/Myeloproliferative Neoplasms
University of California, San Francisco
2005-05
NCT00417053 UNKNOWN
Neuroblastoma
Children's Cancer and Leukaemia Group
PHASE3
NCT00002701 UNKNOWN
Leukemia
European Organisation for Research and Treatment of Cancer - EORTC
1995-10 PHASE3

(data from https://clinicaltrials.gov, updated on 2026-02-13)

Check the Busulfan product page for in-depth specifications, including solubility, stock solutions, MOA, and working concentrations.

Compliance for Clinical Use

Mechanism and Biochemical Profile

Busulfan functions as a cell cycle non-specific bifunctional alkylating agent that covalently cross-links DNA strands and DNA-protein complexes, thereby impairing DNA replication and inhibiting thioredoxin reductase activity. The resulting DNA damage triggers apoptotic cell death and severe myeloablation, effectively reducing tumor burden and facilitating host marrow conditioning prior to hematopoietic stem cell transplantation for acute leukemia and myelodysplastic syndromes.

Appendix RUO and cGMP Quality Standards

Quality Dimension RUO (Research Use Only) cGMP (Current Good Manufacturing Practice)
Clinical Applicability Prohibited in human clinical trials or medical diagnostics. Mandatory for human clinical trials (Phase I–III) and therapies.
Regulatory Status Non-regulated grade; exempt from drug manufacturing laws. Legally enforced by health authorities (e.g., FDA, EMA, NMPA).
Facility Environment Unclassified analytical or research laboratories. Validated Cleanrooms (ISO Class 5–8) with continuous monitoring.
Quality Control Basic purity and activity testing. Rigorous safety release testing (Sterility, Endotoxin, Mycoplasma).
Process Validation Basic equipment calibration; no process validation required. Full qualification (IQ/OQ/PQ) and complete batch records.
Quality Assurance Vendor self-declared without required formal QMS. Mandatory QA/QC unit, Change Control, CAPA, and vendor audits.
Regulatory Impact High risk of IND rejection if used as a critical raw material. Required for IND/NDA filings, supported by Drug Master Files (DMF).

Footnotes

Regulatory Note: Governed by FDA (21 CFR Parts 210/211/312), EMA (EudraLex Vol 4), ICH Guidelines (E6/Q7/Q9/Q10), and compendial standards (USP <71>/<85>/<1043>).

Note: Technical data last updated: Sep 1, 2026.